Plocabulin, a novel tubulin inhibitor, has potent antitumor activity in patient-derived xenograft models of gastrointestinal stromal tumors.

Gastrointestinal stromal tumor PM060184 Patient-derived xenograft Plocabulin Tubulin inhibitor

Journal

Translational oncology
ISSN: 1936-5233
Titre abrégé: Transl Oncol
Pays: United States
ID NLM: 101472619

Informations de publication

Date de publication:
Nov 2020
Historique:
received: 14 04 2020
accepted: 16 06 2020
pubmed: 28 7 2020
medline: 28 7 2020
entrez: 26 7 2020
Statut: ppublish

Résumé

The majority of patients with gastrointestinal stromal tumors (GIST) eventually become resistant with time due to secondary mutations in the driver receptor tyrosine kinase. Novel treatments that do not target these receptors may therefore be preferable. For the first time, we evaluated a tubulin inhibitor, plocabulin, in patient-derived xenograft (PDX) models of GIST, a disease generally considered to be resistant to cytotoxic agents. Three PDX models of GIST with different KIT genotype were generated by implanting tumor fragments from patients directly into nude mice. We then used these well characterized models with distinct sensitivity to imatinib to evaluate the efficacy of the novel tubulin inhibitor. The efficacy of the drug was assessed by volumetric analysis of the tumors, histopathology, immunohistochemistry and Western blotting. Plocabulin treatment led to extensive necrosis in all three models and significant tumor shrinkage in two models. This histological response can be explained by the drug's vascular-disruptive properties, which resulted in a shutdown of tumor vasculature, reflected by a decreased total vascular area in the tumor tissue. Our results demonstrated the in vivo efficacy of the novel tubulin inhibitor plocabulin in PDX models of GIST and challenge the established view that GIST are resistant to cytotoxic agents in general and to tubulin inhibitors in particular. Our findings provide a convincing rationale for early clinical exploration of plocabulin in GIST and warrant further exploration of this class of drugs in the management of this common sarcoma subtype.

Identifiants

pubmed: 32711367
pii: S1936-5233(20)30324-7
doi: 10.1016/j.tranon.2020.100832
pmc: PMC7381700
pii:
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100832

Informations de copyright

Copyright © 2020. Published by Elsevier Inc.

Déclaration de conflit d'intérêts

Declaration of competing interest Yannick Wang received travel support from PharmaMar. Maria Jose Guillén and Pablo M. Avilés are employees of PharmaMar. Patrick Schöffski received institutional support from PharmaMar for research funding. Other authors declare no potential conflicts of interest.

Références

N Engl J Med. 1991 Jan 3;324(1):1-8
pubmed: 1701519
Histopathology. 2006 Sep;49(3):309-11
pubmed: 16918979
Clin Cancer Res. 2013 Feb 1;19(3):620-30
pubmed: 23231951
J Clin Oncol. 2000 Sep 15;18(18):3211-20
pubmed: 10986053
Br J Cancer. 2019 Mar;120(6):612-620
pubmed: 30792533
Mol Cancer Ther. 2016 Dec;15(12):2845-2852
pubmed: 27777285
Ann Surg. 2000 Jan;231(1):51-8
pubmed: 10636102
Lancet. 2013 Sep 14;382(9896):973-83
pubmed: 23623056
N Engl J Med. 2001 Apr 5;344(14):1052-6
pubmed: 11287975
Acta Oncol. 2017 Oct;56(10):1317-1323
pubmed: 28557540
Cancer Res. 2014 Feb 15;74(4):1200-13
pubmed: 24385214
Transl Oncol. 2015 Apr;8(2):112-8
pubmed: 25926077
Science. 1998 Jan 23;279(5350):577-80
pubmed: 9438854
Ann Oncol. 2018 Oct 1;29(Suppl 4):iv267
pubmed: 30188977
Lancet. 2004 Sep 25-Oct 1;364(9440):1127-34
pubmed: 15451219
Cancer Discov. 2014 Sep;4(9):998-1013
pubmed: 25185190
Ther Adv Med Oncol. 2018 Aug 29;10:1758835918794623
pubmed: 30181783
Clin Cancer Res. 2009 Jun 15;15(12):4066-76
pubmed: 19509176
Lancet Oncol. 2013 Nov;14(12):1175-82
pubmed: 24140183
Pharmacol Ther. 2019 Oct;202:18-31
pubmed: 31173840
Mod Pathol. 1998 Aug;11(8):728-34
pubmed: 9720500
Clin Cancer Res. 2019 Jan 15;25(2):609-618
pubmed: 30274985
Cancer Invest. 2002;20(5-6):605-12
pubmed: 12197215
Mol Cancer Ther. 2019 Jun;18(6):1168-1178
pubmed: 30962320
J Cancer Res Clin Oncol. 2010 Jul;136(7):1065-71
pubmed: 20043176
ACS Chem Biol. 2013 Sep 20;8(9):2084-94
pubmed: 23859655
Proc Natl Acad Sci U S A. 2014 Sep 23;111(38):13817-21
pubmed: 25114240
Clin Sarcoma Res. 2014 Aug 10;4:10
pubmed: 25132955
Lancet. 2013 Jan 26;381(9863):295-302
pubmed: 23177515
Clin Cancer Res. 2005 Jun 1;11(11):4182-90
pubmed: 15930355
Biochem Pharmacol. 2014 Apr 1;88(3):291-302
pubmed: 24486569
J Cell Sci. 2003 Sep 15;116(Pt 18):3677-85
pubmed: 12917355
Nat Rev Cancer. 2011 Nov 17;11(12):865-78
pubmed: 22089421
Clin Cancer Res. 2014 Dec 1;20(23):6105-16
pubmed: 25294914
Mol Cytogenet. 2016 Nov 25;9:86
pubmed: 27924151
Ann Surg. 1992 Jan;215(1):68-77
pubmed: 1731651
BMC Cancer. 2018 Feb 7;18(1):164
pubmed: 29415678
World J Gastrointest Oncol. 2013 Jun 15;5(6):102-12
pubmed: 23847717
J Am Chem Soc. 2013 Jul 10;135(27):10164-71
pubmed: 23750450
Clin Cancer Res. 2012 Jun 1;18(11):3170-9
pubmed: 22661587
N Engl J Med. 2002 Aug 15;347(7):472-80
pubmed: 12181401

Auteurs

Yannick Wang (Y)

Laboratory of Experimental Oncology, Department of Oncology, KU Leuven, Leuven, Belgium. Electronic address: yannick.wang@kuleuven.be.

Agnieszka Wozniak (A)

Laboratory of Experimental Oncology, Department of Oncology, KU Leuven, Leuven, Belgium.

Jasmien Wellens (J)

Laboratory of Experimental Oncology, Department of Oncology, KU Leuven, Leuven, Belgium.

Yemarshet K Gebreyohannes (YK)

Laboratory of Experimental Oncology, Department of Oncology, KU Leuven, Leuven, Belgium.

Maria Jose Guillén (MJ)

PharmaMar S.A., Madrid, Spain.

Pablo M Avilés (PM)

PharmaMar S.A., Madrid, Spain.

Maria Debiec-Rychter (M)

Department of Human Genetics, KU Leuven and University Hospitals Leuven, Leuven, Belgium.

Raf Sciot (R)

Department of Pathology, KU Leuven and University Hospitals Leuven, Leuven, Belgium.

Patrick Schöffski (P)

Laboratory of Experimental Oncology, Department of Oncology, KU Leuven, Leuven, Belgium; Department of General Medical Oncology, University Hospitals Leuven, Leuven, Belgium.

Classifications MeSH