[Challenges and potential solutions in first-line treatments for immune thrombocytopenia in adults].

Traitements de première ligne au cours du purpura thrombopénique immunologique de l'adulte : état des lieux et perspectives.
Dexamethasone Dexaméthasone Immune thrombocytopenic purpura Immunoglobulines intraveineuses Intravenous immunoglobulins Prednisone Purpura thrombopénique immunologique

Journal

La Revue de medecine interne
ISSN: 1768-3122
Titre abrégé: Rev Med Interne
Pays: France
ID NLM: 8101383

Informations de publication

Date de publication:
Jan 2021
Historique:
received: 05 03 2020
revised: 04 06 2020
accepted: 20 06 2020
pubmed: 28 7 2020
medline: 25 11 2021
entrez: 28 7 2020
Statut: ppublish

Résumé

The first line treatment of immune thrombocytopenic purpura (ITP) is well established and based on short course of corticosteroids associated with intravenous immunoglobulins (IVIg) for the most severe forms. Predniso(lo)ne is the corticosteroid agent usually given but dexamethasone appears as an alternative. Some guidelines recommend to use dexamethasone as first line when a rapid increase of platelet count is required. Dexamethasone could be used rather than IVIg for moderate to severe but non life-threatening bleeding manifestations. Other therapeutic options such as anti FcRn monoclonal antibodies or recombinant FcγR currently in development for ITP could be an option in the future. In newly diagnosed ITP, we unfortunately lack robust predictive risk factors of severity and chronic outcome. Identifying such factors could be helpful for considering the early use of some treatments which are commonly used as second or third line.

Identifiants

pubmed: 32713675
pii: S0248-8663(20)30244-7
doi: 10.1016/j.revmed.2020.06.018
pii:
doi:

Substances chimiques

Adrenal Cortex Hormones 0
Immunoglobulins, Intravenous 0

Types de publication

Journal Article

Langues

fre

Sous-ensembles de citation

IM

Pagination

25-31

Informations de copyright

Copyright © 2020. Published by Elsevier Masson SAS.

Auteurs

B Godeau (B)

Service de médecine interne, Centre de références sur les cytopénies auto-immunes de l'adulte, CHU Henri Mondor, APHP, UPEC, 94010 Créteil, France. Electronic address: bertrand.godeau@aphp.fr.

B Bonnotte (B)

Service de médecine interne et immunologie clinique, CHU Dijon Bourgogne, Université Bourgogne-Franche Comté, Inserm, EFS UMR1098, 21000 Dijon, France.

M Michel (M)

Service de médecine interne, Centre de références sur les cytopénies auto-immunes de l'adulte, CHU Henri Mondor, APHP, UPEC, 94010 Créteil, France.

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Classifications MeSH