Induced Liver Regeneration Enhances CRISPR/Cas9-Mediated Gene Repair in Tyrosinemia Type 1.
AAV
CRISPR/Cas9
Fanconi anemia
gene therapy
Journal
Human gene therapy
ISSN: 1557-7422
Titre abrégé: Hum Gene Ther
Pays: United States
ID NLM: 9008950
Informations de publication
Date de publication:
03 2021
03 2021
Historique:
pubmed:
31
7
2020
medline:
1
2
2022
entrez:
31
7
2020
Statut:
ppublish
Résumé
The efficiency of gene repair by homologous recombination in the liver is enhanced by CRISP/Cas9 incision near the mutation. In this study, we explored interventions designed to further enhance
Identifiants
pubmed: 32729326
doi: 10.1089/hum.2020.042
pmc: PMC7987361
doi:
Types de publication
Journal Article
Research Support, N.I.H., Extramural
Langues
eng
Sous-ensembles de citation
IM
Pagination
294-301Références
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