Temporospatial genomic profiling in glioblastoma identifies commonly altered core pathways underlying tumor progression.

PI3K signaling clonal evolution contrast enhancement glioblastoma temporospatial heterogeneity

Journal

Neuro-oncology advances
ISSN: 2632-2498
Titre abrégé: Neurooncol Adv
Pays: England
ID NLM: 101755003

Informations de publication

Date de publication:
Historique:
entrez: 4 8 2020
pubmed: 4 8 2020
medline: 4 8 2020
Statut: epublish

Résumé

Tumor heterogeneity underlies resistance and disease progression in glioblastoma (GBM), and tumors most commonly recur adjacent to the surgical resection margins in contrast non-enhancing (NE) regions. To date, no targeted therapies have meaningfully altered overall patient survival in the up-front setting. The aim of this study was to characterize intratumoral heterogeneity in recurrent GBM using bulk samples from primary resection and recurrent samples taken from contrast-enhancing (EN) and contrast NE regions. Whole exome and RNA sequencing were performed on matched bulk primary and multiple recurrent EN and NE tumor samples from 16 GBM patients who received standard of care treatment alone or in combination with investigational clinical trial regimens. Private mutations emerge across multi-region sampling in recurrent tumors. Genomic clonal analysis revealed increased enrichment in gene alterations regulating the G2M checkpoint, Kras signaling, Wnt signaling, and DNA repair in recurrent disease. Subsequent functional studies identified augmented PI3K/AKT transcriptional and protein activity throughout progression, validated by phospho-protein levels. Moreover, a mesenchymal transcriptional signature was observed in recurrent EN regions, which differed from the proneural signature in recurrent NE regions. Subclonal populations observed within bulk resected primary GBMs transcriptionally evolve across tumor recurrence (EN and NE regions) and exhibit aberrant gene expression of common signaling pathways that persist despite standard or targeted therapy. Our findings provide evidence that there are both adaptive and clonally mediated dependencies of GBM on key pathways, such as the PI3K/AKT axis, for survival across recurrences.

Sections du résumé

BACKGROUND BACKGROUND
Tumor heterogeneity underlies resistance and disease progression in glioblastoma (GBM), and tumors most commonly recur adjacent to the surgical resection margins in contrast non-enhancing (NE) regions. To date, no targeted therapies have meaningfully altered overall patient survival in the up-front setting. The aim of this study was to characterize intratumoral heterogeneity in recurrent GBM using bulk samples from primary resection and recurrent samples taken from contrast-enhancing (EN) and contrast NE regions.
METHODS METHODS
Whole exome and RNA sequencing were performed on matched bulk primary and multiple recurrent EN and NE tumor samples from 16 GBM patients who received standard of care treatment alone or in combination with investigational clinical trial regimens.
RESULTS RESULTS
Private mutations emerge across multi-region sampling in recurrent tumors. Genomic clonal analysis revealed increased enrichment in gene alterations regulating the G2M checkpoint, Kras signaling, Wnt signaling, and DNA repair in recurrent disease. Subsequent functional studies identified augmented PI3K/AKT transcriptional and protein activity throughout progression, validated by phospho-protein levels. Moreover, a mesenchymal transcriptional signature was observed in recurrent EN regions, which differed from the proneural signature in recurrent NE regions.
CONCLUSIONS CONCLUSIONS
Subclonal populations observed within bulk resected primary GBMs transcriptionally evolve across tumor recurrence (EN and NE regions) and exhibit aberrant gene expression of common signaling pathways that persist despite standard or targeted therapy. Our findings provide evidence that there are both adaptive and clonally mediated dependencies of GBM on key pathways, such as the PI3K/AKT axis, for survival across recurrences.

Identifiants

pubmed: 32743548
doi: 10.1093/noajnl/vdaa078
pii: vdaa078
pmc: PMC7388612
doi:

Types de publication

Journal Article

Langues

eng

Pagination

vdaa078

Informations de copyright

© The Author(s) 2020. Published by Oxford University Press, the Society for Neuro-Oncology and the European Association of Neuro-Oncology.

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Auteurs

Mylan R Blomquist (MR)

Department of Cancer Biology, Mayo Clinic Arizona, Scottsdale, Arizona, USA.
Department of Neurosurgery, Mayo Clinic Arizona, Scottsdale, Arizona, USA.

Shannon Fortin Ensign (SF)

Department of Hematology and Oncology, Mayo Clinic Arizona, Phoenix, Arizona, USA.

Fulvio D'Angelo (F)

Institute for Cancer Genetics, Columbia University Medical Center, New York, New York, USA.

Joanna J Phillips (JJ)

Department of Pathology, University of California, San Francisco, San Francisco, California, USA.

Michele Ceccarelli (M)

BIOGEM, Ariano Irpino, Italy.

Sen Peng (S)

Cancer and Cell Biology Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Rebecca F Halperin (RF)

Integrated Cancer Genomics Division, The Translational Genomics Research Institute, Phoenix, Arizona, USA.

Francesca P Caruso (FP)

Department of Science and Technology, Università degli Studi del Sannio, Benevento, Italy.

Luciano Garofano (L)

Institute for Cancer Genetics, Columbia University Medical Center, New York, New York, USA.
Department of Science and Technology, Università degli Studi del Sannio, Benevento, Italy.

Sara A Byron (SA)

Integrated Cancer Genomics Division, The Translational Genomics Research Institute, Phoenix, Arizona, USA.

Winnie S Liang (WS)

Integrated Cancer Genomics Division, The Translational Genomics Research Institute, Phoenix, Arizona, USA.

David W Craig (DW)

Department of Translational Genomics, University of Southern California Keck School of Medicine, Los Angeles, California, USA.

John D Carpten (JD)

Department of Translational Genomics, University of Southern California Keck School of Medicine, Los Angeles, California, USA.

Michael D Prados (MD)

Department of Neurological Surgery, University of California, San Francisco, San Francisco, California, USA.

Jeffrey M Trent (JM)

Integrated Cancer Genomics Division, The Translational Genomics Research Institute, Phoenix, Arizona, USA.

Michael E Berens (ME)

Cancer and Cell Biology Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Antonio Iavarone (A)

Institute for Cancer Genetics, Columbia University Medical Center, New York, New York, USA.

Harshil Dhruv (H)

Cancer and Cell Biology Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Nhan L Tran (NL)

Department of Cancer Biology, Mayo Clinic Arizona, Scottsdale, Arizona, USA.
Department of Neurosurgery, Mayo Clinic Arizona, Scottsdale, Arizona, USA.

Classifications MeSH