Impairment of adenosinergic system in Rett syndrome: Novel therapeutic target to boost BDNF signalling.


Journal

Neurobiology of disease
ISSN: 1095-953X
Titre abrégé: Neurobiol Dis
Pays: United States
ID NLM: 9500169

Informations de publication

Date de publication:
11 2020
Historique:
received: 21 04 2020
revised: 23 07 2020
accepted: 08 08 2020
pubmed: 18 8 2020
medline: 13 10 2021
entrez: 18 8 2020
Statut: ppublish

Résumé

Rett syndrome (RTT; OMIM#312750) is mainly caused by mutations in the X-linked MECP2 gene (methyl-CpG-binding protein 2 gene; OMIM*300005), which leads to impairments in the brain-derived neurotrophic factor (BDNF) signalling. The boost of BDNF mediated effects would be a significant breakthrough but it has been hampered by the difficulty to administer BDNF to the central nervous system. Adenosine, an endogenous neuromodulator, may accomplish that role since through A

Identifiants

pubmed: 32798727
pii: S0969-9961(20)30318-1
doi: 10.1016/j.nbd.2020.105043
pii:
doi:

Substances chimiques

Brain-Derived Neurotrophic Factor 0
Mecp2 protein, mouse 0
Methyl-CpG-Binding Protein 2 0
Receptor, Adenosine A1 0
Receptor, Adenosine A2A 0
Receptor, trkB EC 2.7.10.1

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

105043

Informations de copyright

Copyright © 2020 The Authors. Published by Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest The authors declare that they have no competing interests.

Auteurs

Catarina Miranda-Lourenço (C)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: catarinalourenco@medicina.ulisboa.pt.

Sofia T Duarte (ST)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal; Child Neurology Department, Hospital Dona Estefânia - Centro Hospitalar Universitário de Lisboa Central, Portugal. Electronic address: Sofia.duarte22@hotmail.com.

Cátia Palminha (C)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: catiapalminha@gmail.com.

Cláudia Gaspar (C)

Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: cscgaspar@gmail.com.

Tiago M Rodrigues (TM)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal; Institute of Molecular and Clinical Ophtalmology, Mittlere Strasse 91, CH-4031 Basel, Switzerland. Electronic address: tiago.fm.rod@gmail.com.

Teresa Magalhães-Cardoso (T)

Laboratório de Farmacologia e Neurobiologia / MedInUP, Instituto de Ciências Biomédicas Abel Salazar - Universidade do Porto (ICBAS-UP), Porto, Portugal. Electronic address: tmcardoso@icbas.up.pt.

Nádia Rei (N)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: nadia.rei@gmail.com.

Mariana Colino-Oliveira (M)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: Mcolino.oliveira@gmail.com.

Rui Gomes (R)

Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: ragomes@medicina.ulisboa.pt.

Sara Ferreira (S)

Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: ssgferreira@gmail.com.

Jéssica Rosa (J)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: jessicarosa@campus.ul.pt.

Sara Xapelli (S)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: sxapelli@medicina.ulisboa.pt.

Judith Armstrong (J)

Genetics Department, Hospital Sant Joan de Deu. Institut Pediàtric de Recerca and CIBERER. (ISCIII), Barcelona, Spain. Electronic address: jarmstrong@sjdhospitalbarcelona.org.

Àngels García-Cazorla (À)

Synaptic Metabolism Laboratory, Neurology Department; Institut Pediàtric de Recerca and CIBERER. (ISCIII), Barcelona, Spain. Electronic address: agarcia@sjdhospitalbarcelona.org.

Paulo Correia-de-Sá (P)

Laboratório de Farmacologia e Neurobiologia / MedInUP, Instituto de Ciências Biomédicas Abel Salazar - Universidade do Porto (ICBAS-UP), Porto, Portugal. Electronic address: farmacol@icbas.up.pt.

Ana M Sebastião (AM)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: anaseb@medicina.ulisboa.pt.

Maria José Diógenes (MJ)

Instituto de Farmacologia e Neurociências, Faculdade de Medicina e Instituto de Medicina Molecular - João Lobo Antunes, Universidade de Lisboa, Lisboa, Portugal. Electronic address: diogenes@medicina.ulisboa.pt.

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Classifications MeSH