Structural Basis for α-Helix Mimicry and Inhibition of Protein-Protein Interactions with Oligourea Foldamers.

foldamers helical structures oligoureas protein-protein interactions structure-activity relationships

Journal

Angewandte Chemie (International ed. in English)
ISSN: 1521-3773
Titre abrégé: Angew Chem Int Ed Engl
Pays: Germany
ID NLM: 0370543

Informations de publication

Date de publication:
01 02 2021
Historique:
received: 29 06 2020
revised: 19 08 2020
pubmed: 17 9 2020
medline: 2 4 2021
entrez: 16 9 2020
Statut: ppublish

Résumé

Efficient optimization of a peptide lead into a drug candidate frequently needs further transformation to augment properties such as bioavailability. Among the different options, foldamers, which are sequence-based oligomers with precise folded conformation, have emerged as a promising technology. We introduce oligourea foldamers to reduce the peptide character of inhibitors of protein-protein interactions (PPI). However, the precise design of such mimics is currently limited by the lack of structural information on how these foldamers adapt to protein surfaces. We report a collection of X-ray structures of peptide-oligourea hybrids in complex with ubiquitin ligase MDM2 and vitamin D receptor and show how such hybrid oligomers can be designed to bind with high affinity to protein targets. This work should enable the generation of more effective foldamer-based disruptors of PPIs in the context of peptide lead optimization.

Identifiants

pubmed: 32935897
doi: 10.1002/anie.202008992
doi:

Substances chimiques

Urea 8W8T17847W

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

2296-2303

Informations de copyright

© 2020 Wiley-VCH GmbH.

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Auteurs

Léonie Cussol (L)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.

Laura Mauran-Ambrosino (L)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.
Ureka Pharma SAS, 2 rue Robert Escarpit, F-33607, Pessac, France.

Jérémie Buratto (J)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.

Anna Y Belorusova (AY)

Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), INSERM, U1258/CNRS, UMR 7104/, Univ. Strasbourg, 67404, Illkirch, France.

Maxime Neuville (M)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.
Ureka Pharma SAS, 2 rue Robert Escarpit, F-33607, Pessac, France.

Judit Osz (J)

Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), INSERM, U1258/CNRS, UMR 7104/, Univ. Strasbourg, 67404, Illkirch, France.

Sébastien Fribourg (S)

ARNA Laboratory, INSERM U1212, UMR CNRS 5320, Univ. Bordeaux, Bordeaux, France.

Juliette Fremaux (J)

Ureka Pharma SAS, 2 rue Robert Escarpit, F-33607, Pessac, France.

Christel Dolain (C)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.

Sébastien R Goudreau (SR)

Ureka Pharma SAS, 2 rue Robert Escarpit, F-33607, Pessac, France.

Natacha Rochel (N)

Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), INSERM, U1258/CNRS, UMR 7104/, Univ. Strasbourg, 67404, Illkirch, France.

Gilles Guichard (G)

Univ. Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Institut Européen de Chimie et Biologie, 2 rue Robert Escarpit, F-33607, Pessac, France.

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