Liver transplant for inherited metabolic disease among siblings.

clinical decision-making genetics liver disease metabolic recipient selection

Journal

Clinical transplantation
ISSN: 1399-0012
Titre abrégé: Clin Transplant
Pays: Denmark
ID NLM: 8710240

Informations de publication

Date de publication:
11 2020
Historique:
received: 01 06 2020
revised: 26 08 2020
accepted: 30 08 2020
pubmed: 22 9 2020
medline: 24 6 2021
entrez: 21 9 2020
Statut: ppublish

Résumé

Liver transplantation is a successful option for inherited metabolic disease yet little is published on the outcome among siblings. We report outcomes of siblings who have undergone liver transplantation for metabolic disease in a single program. Seventy-one siblings (35 males) from 33 individual families underwent liver transplantation since 1982. Outcomes were compared over three consecutive eras. Twenty-eight families had two siblings, four had three siblings, and one had four siblings. In half of families where dates of listing were known, siblings were listed simultaneously. Mean (SD) age at listing for the oldest and second sibling was 13.2 (7.1) and 9.8 (5.7) years, respectively (p < .01). In 18/33 families, the oldest sibling underwent transplantation first. Mean (SD) age at transplant fell from the oldest to second sibling from 12.9 (7.2) to 9.5 (6.3) years, respectively (p < .001). Ten-year patient survival was 83.5% which improved over the eras: era 1 (1982-1994) 65.0%, era 2 (1995-2007) 87.5%, and era 3 (2008-2019) 93.8%: p < .03. Sex, age at transplant, order of transplant, and presence of structural liver disease did not significantly impact survival. When siblings undergo liver transplant for inherited metabolic disease, later siblings are listed and transplanted at a significantly younger age.

Identifiants

pubmed: 32955727
doi: 10.1111/ctr.14090
pmc: PMC10064292
mid: NIHMS1880294
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

e14090

Subventions

Organisme : NIDDK NIH HHS
ID : P30 DK120531
Pays : United States

Informations de copyright

© 2020 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.

Références

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Auteurs

Patrick J McKiernan (PJ)

Division of pediatric gastroenterology, hepatology and nutrition, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

James E Squires (JE)

Division of pediatric gastroenterology, hepatology and nutrition, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Robert H Squires (RH)

Division of pediatric gastroenterology, hepatology and nutrition, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Jerry Vockley (J)

Division of medical genetics, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

George V Mazariegos (GV)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Kyle Soltys (K)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Armando Ganoza (A)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Kevin Strauss (K)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.
Clinic for Special Children, Strasburg, PA, USA.

Ajai Khanna (A)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Rakesh Sindhi (R)

Hillman Center for Pediatric Transplantation, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

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