Topical Propranolol Improves Epistaxis Control in Hereditary Hemorrhagic Telangiectasia (HHT): A Randomized Double-Blind Placebo-Controlled Trial.

antiangiogenic properties epistaxis epistaxis severity score hereditary hemorrhagic telangiectasia nasal endoscopy propranolol gel

Journal

Journal of clinical medicine
ISSN: 2077-0383
Titre abrégé: J Clin Med
Pays: Switzerland
ID NLM: 101606588

Informations de publication

Date de publication:
28 Sep 2020
Historique:
received: 31 08 2020
revised: 18 09 2020
accepted: 26 09 2020
entrez: 1 10 2020
pubmed: 2 10 2020
medline: 2 10 2020
Statut: epublish

Résumé

Epistaxis is a common debilitating manifestation in hereditary hemorrhagic telangiectasia (HHT), due to mucocutaneous telangiectases. The epistaxis can be difficult to control despite available treatments. Dysregulated angiogenesis has been shown to be associated with telangiectases formation. Topical propranolol has demonstrated antiangiogenic properties. We performed a two-phase study, i.e., a double-blind placebo-controlled phase, followed by an open-label phase. The aim of the study was assessment of safety and efficacy of nasal propranolol gel in HHT-related epistaxis. Twenty participants with moderate-severe HHT-related epistaxis were randomized to eight weeks of propranolol gel 1.5%, or placebo 0.5 cc, applied to each nostril twice daily; and continued propranolol for eight weeks in an open-label study. For the propranolol group, the epistaxis severity score (ESS) improved significantly (-2.03 ± 1.7 as compared with -0.35 ± 0.68 for the placebo group,

Identifiants

pubmed: 32998220
pii: jcm9103130
doi: 10.3390/jcm9103130
pmc: PMC7601781
pii:
doi:

Types de publication

Journal Article

Langues

eng

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Auteurs

Meir Mei-Zahav (M)

Pulmonary Institute, Schneider Children's Medical Center of Israel, Petah Tikva 49202, Israel.
Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.
The National HHT Center, Pulmonary Institute, Schneider CMCI, 14 Kaplan St., Petach Tikva 49202, Israel.

Yulia Gendler (Y)

Pulmonary Institute, Schneider Children's Medical Center of Israel, Petah Tikva 49202, Israel.
The Department of Nursing, Ariel University, Ariel 40700, Israel.

Elchanan Bruckheimer (E)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.
Cardiology Department, Schneider Children's Medical Center of Israel, Petah Tikva 49202, Israel.

Dario Prais (D)

Pulmonary Institute, Schneider Children's Medical Center of Israel, Petah Tikva 49202, Israel.
Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.
The National HHT Center, Pulmonary Institute, Schneider CMCI, 14 Kaplan St., Petach Tikva 49202, Israel.

Einat Birk (E)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.
Cardiology Department, Schneider Children's Medical Center of Israel, Petah Tikva 49202, Israel.

Muhamad Watad (M)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.

Neta Goldschmidt (N)

Department of Hematology, Hadassah-Hebrew University Medical Center, Jerusalem 91120, Israel.

Ethan Soudry (E)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 69978, Israel.
Department of Otolaryngology Head and Neck Surgery, Rabin Medical Center, Petah Tikva 49202, Israel.

Classifications MeSH