Compound heterozygous variants in the

Disease genetics Dyslipidaemias

Journal

Human genome variation
ISSN: 2054-345X
Titre abrégé: Hum Genome Var
Pays: England
ID NLM: 101652445

Informations de publication

Date de publication:
2020
Historique:
received: 11 04 2020
revised: 03 08 2020
accepted: 15 08 2020
entrez: 5 10 2020
pubmed: 6 10 2020
medline: 6 10 2020
Statut: epublish

Résumé

Sitosterolemia is an autosomal recessive disorder that affects lipid metabolism and is characterized by elevated serum plant sterol levels, xanthomas, and accelerated atherosclerosis. In this study, we report a novel nonsense single-nucleotide variant, c.225G > A (p.Trp75*), and an East Asian population-specific missense multiple-nucleotide variant, c.1256_1257delTCinsAA (p.Ile419Lys), in the

Identifiants

pubmed: 33014402
doi: 10.1038/s41439-020-00112-y
pii: 112
pmc: PMC7490419
doi:

Types de publication

Journal Article

Langues

eng

Pagination

25

Informations de copyright

© The Author(s) 2020.

Déclaration de conflit d'intérêts

Conflict of interestThe authors declare that they have no conflict of interest.

Références

Nat Protoc. 2016 Jan;11(1):1-9
pubmed: 26633127
Am J Hum Genet. 2001 Aug;69(2):278-90
pubmed: 11452359
Genet Med. 2015 May;17(5):405-24
pubmed: 25741868
J Clin Lipidol. 2018 Nov - Dec;12(6):1436-1444
pubmed: 30241732
Nucleic Acids Res. 2019 Jan 8;47(D1):D886-D894
pubmed: 30371827
Science. 2000 Dec 1;290(5497):1771-5
pubmed: 11099417
Nat Methods. 2010 Apr;7(4):248-9
pubmed: 20354512
Ann Pediatr Endocrinol Metab. 2016 Mar;21(1):7-14
pubmed: 27104173
Nat Commun. 2020 May 27;11(1):2539
pubmed: 32461613
Nature. 2016 Aug 17;536(7616):285-91
pubmed: 27535533
J Clin Lipidol. 2017 Nov - Dec;11(6):1432-1440.e4
pubmed: 29066094
Circ J. 2019 Aug 23;83(9):1917-1924
pubmed: 31327807
Nat Methods. 2014 Apr;11(4):361-2
pubmed: 24681721
J Clin Lipidol. 2020 Mar - Apr;14(2):207-217.e7
pubmed: 32088153
Atherosclerosis. 2018 Feb;269:106-116
pubmed: 29353225

Auteurs

Nobuhiro Hashimoto (N)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Sumito Dateki (S)

Department of Pediatrics, Nagasaki University Graduate School of Biomedical Sciences, Nagasaki, Japan.

Eri Suzuki (E)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Takatoshi Tsuchihashi (T)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.
Department of Pediatrics, Kawasaki Municipal Hospital, Kanagawa, Japan.

Aiko Isobe (A)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Sari Banno (S)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Tomoka Kageyama (T)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Naonori Maeda (N)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Naomi Hatabu (N)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Rieko Sato (R)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Masashi Miharu (M)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Hisayo Fujita (H)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Osamu Komiyama (O)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Hitomi Shimizu (H)

Department of Pediatrics, Nagasaki University Graduate School of Biomedical Sciences, Nagasaki, Japan.

Tomonobu Hasegawa (T)

Department of Pediatrics, Keio University School of Medicine, Tokyo, Japan.

Kazuki Yamazawa (K)

Department of Pediatrics, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.
Medical Genetics Center, National Hospital Organization Tokyo Medical Center, Tokyo, Japan.

Classifications MeSH