Optimizing the Therapeutic Window of Targeted Drugs in Oncology: Potency-Guided First-in-Human Studies.


Journal

Clinical and translational science
ISSN: 1752-8062
Titre abrégé: Clin Transl Sci
Pays: United States
ID NLM: 101474067

Informations de publication

Date de publication:
03 2021
Historique:
received: 21 05 2020
accepted: 07 09 2020
pubmed: 14 10 2020
medline: 15 12 2021
entrez: 13 10 2020
Statut: ppublish

Résumé

Many targeted therapies are administered at or near the maximum tolerated dose (MTD). With the advent of precision medicine, a larger therapeutic window is expected. Therefore, dose optimization will require a new approach to early clinical trial design. We analyzed publicly available data for 21 therapies targeting six kinases, and four poly (ADP-ribose) polymerase inhibitors, focusing on potency and exposure to gain insight into dose selection. The free average steady-state concentration (C

Identifiants

pubmed: 33048459
doi: 10.1111/cts.12902
pmc: PMC7993318
doi:

Substances chimiques

Antineoplastic Agents 0
Poly(ADP-ribose) Polymerase Inhibitors 0
Protein Kinase Inhibitors 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

536-543

Informations de copyright

© 2020 Tango Therapeutics. Clinical and Translational Science published by Wiley Periodicals LLC on behalf of the American Society for Clinical Pharmacology and Therapeutics.

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Auteurs

Matthew J Goldstein (MJ)

Tango Therapeutics, Cambridge, Massachusetts, USA.

Malte Peters (M)

MorphoSys AG, Planegg, Germany.

Barbara L Weber (BL)

Tango Therapeutics, Cambridge, Massachusetts, USA.

Charles B Davis (CB)

Tango Therapeutics, Cambridge, Massachusetts, USA.

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Classifications MeSH