Development of a Multiplex Real-Time PCR Assay for the Newborn Screening of SCID, SMA, and XLA.

DBS KREC Newborn Screening SCID SMA SMN1 TREC XLA real-time PCR

Journal

International journal of neonatal screening
ISSN: 2409-515X
Titre abrégé: Int J Neonatal Screen
Pays: Switzerland
ID NLM: 101665400

Informations de publication

Date de publication:
Dec 2019
Historique:
received: 01 09 2019
accepted: 31 10 2019
entrez: 19 10 2020
pubmed: 20 10 2020
medline: 20 10 2020
Statut: epublish

Résumé

Numerous studies have shown evidence supporting the benefits of universal newborn screening for primary immunodeficiencies (PID) and for Spinal Muscular Atrophy (SMA). We have developed a four-plex, real-time PCR assay to screen for Severe Combined Immune Deficiencies (SCID), X-linked agammaglobulinemia (XLA), and SMA in DNA extracted from a single 3.2 mm punch of a dried blood spot (DBS). A simple, high-throughput, semi-automated DNA extraction method was developed for a Janus liquid handler that can process 384 DBS punches in four 96-well plates in just over one hour with sample tracking capability. The PCR assay identifies the absence of exon 7 in the

Identifiants

pubmed: 33072998
doi: 10.3390/ijns5040039
pii: IJNS-05-00039
pmc: PMC7510252
doi:

Types de publication

Journal Article

Langues

eng

Pagination

39

Informations de copyright

© 2019 by the authors.

Déclaration de conflit d'intérêts

Conflicts of InterestC.G-M., A.T., K.V., M.J., G.F., S.D., D.G., D.S. and R.W. are PerkinElmer employees. Authors representing PerkinElmer had a role in designing the study, in collection, analyses, and interpretation of the data, in the writing of the manuscript, and in the decision to publish the results. The other authors declare no conflict of interest.

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Auteurs

Cristina Gutierrez-Mateo (C)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

Anne Timonen (A)

PerkinElmer, Wallac Oy, Mustionkatu 6, 20750 Turku, Finland; anne.timonen@perkinelmer.com (A.T.); katja.Vaahtera@perkinelmer.com (K.V.); Markku.Jaakkola@perkinelmer.com (M.J.).

Katja Vaahtera (K)

PerkinElmer, Wallac Oy, Mustionkatu 6, 20750 Turku, Finland; anne.timonen@perkinelmer.com (A.T.); katja.Vaahtera@perkinelmer.com (K.V.); Markku.Jaakkola@perkinelmer.com (M.J.).

Markku Jaakkola (M)

PerkinElmer, Wallac Oy, Mustionkatu 6, 20750 Turku, Finland; anne.timonen@perkinelmer.com (A.T.); katja.Vaahtera@perkinelmer.com (K.V.); Markku.Jaakkola@perkinelmer.com (M.J.).

David M Hougaard (DM)

Danish Center for Neonatal Screening, Statens Serum Institut, 2300 Copenhagen, Denmark; dh@ssi.dk (D.M.H.); jogr@ssi.dk (J.B.-G.); MABH@ssi.dk (M.B.-H.); DADN@ssi.dk (D.A.).

Jonas Bybjerg-Grauholm (J)

Danish Center for Neonatal Screening, Statens Serum Institut, 2300 Copenhagen, Denmark; dh@ssi.dk (D.M.H.); jogr@ssi.dk (J.B.-G.); MABH@ssi.dk (M.B.-H.); DADN@ssi.dk (D.A.).

Marie Baekvad-Hansen (M)

Danish Center for Neonatal Screening, Statens Serum Institut, 2300 Copenhagen, Denmark; dh@ssi.dk (D.M.H.); jogr@ssi.dk (J.B.-G.); MABH@ssi.dk (M.B.-H.); DADN@ssi.dk (D.A.).

Dea Adamsen (D)

Danish Center for Neonatal Screening, Statens Serum Institut, 2300 Copenhagen, Denmark; dh@ssi.dk (D.M.H.); jogr@ssi.dk (J.B.-G.); MABH@ssi.dk (M.B.-H.); DADN@ssi.dk (D.A.).

Galina Filippov (G)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

Stephanie Dallaire (S)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

David Goldfarb (D)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

Daniel Schoener (D)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

Rongcong Wu (R)

PerkinElmer, 940 Winter St, Waltham, MA 02451, USA; galina.Filippov@perkinelmer.com (G.F.); stephanie.dallaire@perkinelmer.com (S.D.); david.goldfarb@perkinelmer.com (D.G.); Daniel.Schoener@perkinelmer.com (D.S.); rongcong.wu@perkinelmer.com (R.W.).

Classifications MeSH