Activated Phosphoinositide 3-Kinase Delta Syndrome 1: Clinical and Immunological Data from an Italian Cohort of Patients.

PI3K PIK3CD activated phosphoinositide 3-kinase delta syndrome 1 lymphoproliferation p110δ primary combined immune deficiency

Journal

Journal of clinical medicine
ISSN: 2077-0383
Titre abrégé: J Clin Med
Pays: Switzerland
ID NLM: 101606588

Informations de publication

Date de publication:
17 Oct 2020
Historique:
received: 24 09 2020
revised: 14 10 2020
accepted: 15 10 2020
entrez: 21 10 2020
pubmed: 22 10 2020
medline: 22 10 2020
Statut: epublish

Résumé

Activated phosphoinositide 3-kinase delta syndrome 1 (APDS-1) is a recently described inborn error of immunity caused by monoallelic gain-of-function mutations in the

Identifiants

pubmed: 33080915
pii: jcm9103335
doi: 10.3390/jcm9103335
pmc: PMC7603210
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : European Community's Seventh Framework Programme
ID : EURO-PADnet HEALTH-F2-2008-201549
Organisme : Italian Ministerial Grant
ID : GR-2010-2315762

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Auteurs

Giulio Tessarin (G)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Stefano Rossi (S)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Manuela Baronio (M)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Luisa Gazzurelli (L)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Michael Colpani (M)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Alessio Benvenuto (A)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Fiammetta Zunica (F)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Fabio Cardinale (F)

Allergy, Immunology and Pediatric Pulmonology Unit, "Policlinico-Giovanni XXII" Hospital, University of Bari, 70126 Bari, Italy.

Baldassarre Martire (B)

Pediatrics Unit, Monsignor Dimiccoli Hospital, 70051 Barletta, Italy.

Letizia Brescia (L)

Pediatric Oncohematology Unit, Ospedale Santissima Annunziata, 74121 Taranto, Italy.

Giorgio Costagliola (G)

Division of Pediatrics, University of Pisa, 56126 Pisa, Italy.

Laura Luti (L)

Pediatric Oncology and Hematology, University of Pisa, 56126 Pisa, Italy.

Gabriella Casazza (G)

Pediatric Oncology and Hematology, University of Pisa, 56126 Pisa, Italy.

Maria Cristina Menconi (MC)

Pediatric Oncology and Hematology, University of Pisa, 56126 Pisa, Italy.

Francesco Saettini (F)

Pediatric Hematology Oncology Unit, Department of Pediatrics, University of Milano Bicocca, MBBM Foundation, 20900 Monza, Italy.

Laura Palumbo (L)

Pediatrics Clinic, ASST-Spedali Civili of Brescia, 25123 Brescia, Italy.

Maria Federica Girelli (MF)

Pediatrics Clinic, ASST-Spedali Civili of Brescia, 25123 Brescia, Italy.

Raffaele Badolato (R)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Gaetana Lanzi (G)

"Angelo Nocivelli" Institute for Molecular Medicine, ASST Spedali Civili, Department of Molecular and Translational Medicine, University of Brescia, 25123 Brescia, Italy.

Marco Chiarini (M)

Clinical Chemical Analysis Central Laboratory, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Daniele Moratto (D)

Clinical Chemical Analysis Central Laboratory, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Antonella Meini (A)

Pediatrics Clinic, ASST-Spedali Civili of Brescia, 25123 Brescia, Italy.

Silvia Giliani (S)

Cytogenetic and Medical Genetics Unit and "A. Nocivelli" Institute for Molecular Medicine, Department of Molecular and Translational Medicine, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Maria Pia Bondioni (MP)

Pediatric Radiology, University of Brescia, ASST Spedali Civili di Brescia, 25123 Brescia, Italy.

Alessandro Plebani (A)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Vassilios Lougaris (V)

Pediatrics Clinic and "A. Nocivelli" Institute for Molecular Medicine, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25123 Brescia, Italy.

Classifications MeSH