Inhibition of inflammatory signaling in Pax5 mutant cells mitigates B-cell leukemogenesis.


Journal

Scientific reports
ISSN: 2045-2322
Titre abrégé: Sci Rep
Pays: England
ID NLM: 101563288

Informations de publication

Date de publication:
05 11 2020
Historique:
received: 13 08 2020
accepted: 22 10 2020
entrez: 6 11 2020
pubmed: 7 11 2020
medline: 10 3 2021
Statut: epublish

Résumé

PAX5 is one of the most frequently mutated genes in B-cell acute lymphoblastic leukemia (B-ALL), and children with inherited preleukemic PAX5 mutations are at a higher risk of developing the disease. Abnormal profiles of inflammatory markers have been detected in neonatal blood spot samples of children who later developed B-ALL. However, how inflammatory signals contribute to B-ALL development is unclear. Here, we demonstrate that Pax5 heterozygosis, in the presence of infections, results in the enhanced production of the inflammatory cytokine interleukin-6 (IL-6), which appears to act in an autocrine fashion to promote leukemia growth. Furthermore, in vivo genetic downregulation of IL-6 in these Pax5 heterozygous mice retards B-cell leukemogenesis, and in vivo pharmacologic inhibition of IL-6 with a neutralizing antibody in Pax5 mutant mice with B-ALL clears leukemic cells. Additionally, this novel IL-6 signaling paradigm identified in mice was also substantiated in humans. Altogether, our studies establish aberrant IL6 expression caused by Pax5 loss as a hallmark of Pax5-dependent B-ALL and the IL6 as a therapeutic vulnerability for B-ALL characterized by PAX5 loss.

Identifiants

pubmed: 33154497
doi: 10.1038/s41598-020-76206-y
pii: 10.1038/s41598-020-76206-y
pmc: PMC7644722
doi:

Substances chimiques

Interleukin-6 0
PAX5 Transcription Factor 0
Pax5 protein, mouse 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

19189

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Auteurs

Marta Isidro-Hernández (M)

Experimental Therapeutics and Translational Oncology Program, Instituto de Biología Molecular y Celular del Cáncer, CSIC-USAL, Campus M. de Unamuno s/n, Salamanca, Spain.
Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.

Andrea Mayado (A)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Servicio de Citometría, Departamento de Medicina, Biomedical Research Networking Centre on Cancer CIBER- CIBERONC (CB16/12/00400), Institute of Health Carlos III, and Instituto de Biología Molecular y Celular del Cáncer, CSIC/Universidad de Salamanca, Salamanca, Spain.

Ana Casado-García (A)

Experimental Therapeutics and Translational Oncology Program, Instituto de Biología Molecular y Celular del Cáncer, CSIC-USAL, Campus M. de Unamuno s/n, Salamanca, Spain.
Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.

Jorge Martínez-Cano (J)

Immune system development and function Unit, Centro de Biología Molecular Severo Ochoa (Consejo Superior de Investigaciones Científicas -Universidad Autónoma de Madrid), Madrid, Spain.

Chiara Palmi (C)

Centro Ricerca Tettamanti, Dept of Medicine, University of Milan Bicocca, Monza, Italy.

Grazia Fazio (G)

Centro Ricerca Tettamanti, Dept of Medicine, University of Milan Bicocca, Monza, Italy.

Alberto Orfao (A)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Servicio de Citometría, Departamento de Medicina, Biomedical Research Networking Centre on Cancer CIBER- CIBERONC (CB16/12/00400), Institute of Health Carlos III, and Instituto de Biología Molecular y Celular del Cáncer, CSIC/Universidad de Salamanca, Salamanca, Spain.

Jordi Ribera (J)

Josep Carreras Leukaemia Research Institute (IJC), Badalona, Spain.

Josep Maria Ribera (JM)

Josep Carreras Leukaemia Research Institute (IJC), Badalona, Spain.
Catalan Institute of Oncology-Germans Trias i Pujol, Badalona, Spain.

Lurdes Zamora (L)

Josep Carreras Leukaemia Research Institute (IJC), Badalona, Spain.
Catalan Institute of Oncology-Germans Trias i Pujol, Badalona, Spain.

Javier Raboso-Gallego (J)

Experimental Therapeutics and Translational Oncology Program, Instituto de Biología Molecular y Celular del Cáncer, CSIC-USAL, Campus M. de Unamuno s/n, Salamanca, Spain.
Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.

Oscar Blanco (O)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Departamento de Anatomía Patológica, Universidad de Salamanca, Salamanca, Spain.

Diego Alonso-López (D)

Bioinformatics Unit, Cancer Research Center (CSIC-USAL), Salamanca, Spain.

Javier De Las Rivas (J)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Bioinformatics and Functional Genomics Research Group, Cancer Research Center (CSIC-USAL), Salamanca, Spain.

Rafael Jiménez (R)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Departamento de Fisiología y Farmacología, Universidad de Salamanca, Edificio Departamental, Campus M. de Unamuno s/n, 37007, Salamanca, Spain.

Francisco Javier García Criado (FJ)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Departamento de Cirugía, Universidad de Salamanca, Salamanca, Spain.

María Begoña García Cenador (MB)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain.
Departamento de Cirugía, Universidad de Salamanca, Salamanca, Spain.

Manuel Ramírez-Orellana (M)

Department of Pediatric Hematology and Oncology, Hospital Infantil Universitario Niño Jesús, Universidad Autónoma de Madrid, Madrid, Spain.

Giovanni Cazzaniga (G)

Centro Ricerca Tettamanti, Dept of Medicine, University of Milan Bicocca, Monza, Italy.

César Cobaleda (C)

Immune system development and function Unit, Centro de Biología Molecular Severo Ochoa (Consejo Superior de Investigaciones Científicas -Universidad Autónoma de Madrid), Madrid, Spain. cesar.cobaleda@csic.es.

Carolina Vicente-Dueñas (C)

Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain. cvd@usal.es.

Isidro Sánchez-García (I)

Experimental Therapeutics and Translational Oncology Program, Instituto de Biología Molecular y Celular del Cáncer, CSIC-USAL, Campus M. de Unamuno s/n, Salamanca, Spain. isg@usal.es.
Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain. isg@usal.es.

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Classifications MeSH