Arginine kinetics are altered in a pilot sample of adolescents and young adults with Barth syndrome.

Amino acid Barth syndrome Metabolism Mitochondria

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Dec 2020
Historique:
received: 25 09 2020
revised: 28 10 2020
accepted: 29 10 2020
entrez: 18 11 2020
pubmed: 19 11 2020
medline: 19 11 2020
Statut: epublish

Résumé

Barth syndrome (BTHS) is a rare, X-linked cardiomyopathy that is characterized by abnormalities in glucose and lipid metabolism, with less known regarding amino acid metabolism. This pilot study characterized whole-body arginine kinetics and found lower arginine rate of appearance into plasma (0.69 ± 0.09 vs. 0.88 ± 0.06 μmol/kgFFM/min,

Identifiants

pubmed: 33204638
doi: 10.1016/j.ymgmr.2020.100675
pii: S2214-4269(20)30121-X
pmc: PMC7649643
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100675

Subventions

Organisme : NIDDK NIH HHS
ID : P30 DK020579
Pays : United States
Organisme : NIDDK NIH HHS
ID : P30 DK056341
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL136759
Pays : United States

Informations de copyright

© 2020 The Authors. Published by Elsevier Inc.

Déclaration de conflit d'intérêts

W. Todd Cade, Kathryn L. Bohnert, Bruce W. Patterson, Adam J. Bittel, Shaji K. Chacko, Christina A. Pacak, Barry J. Byrne, Hilary J Vernon, and Dominic N. Reeds declare that they have no conflict of interest.

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Auteurs

W Todd Cade (WT)

Program in Physical Therapy, Washington University School of Medicine, St. Louis, MO, United States.
Department of Medicine, Washington University School of Medicine, St. Louis, MO, United States.
Doctor of Physical Therapy Division, Duke University School of Medicine, Durham, NC, United States.

Kathryn L Bohnert (KL)

Program in Physical Therapy, Washington University School of Medicine, St. Louis, MO, United States.

Adam J Bittel (AJ)

Program in Physical Therapy, Washington University School of Medicine, St. Louis, MO, United States.

Shaji J Chacko (SJ)

Department of Pediatrics, Children's Nutrition Research Center, U.S. Department of Agriculture/Agricultural Research Service, Baylor College of Medicine, Houston, TX, United States.

Bruce W Patterson (BW)

Department of Medicine, Washington University School of Medicine, St. Louis, MO, United States.

Christina A Pacak (CA)

Department of Pediatrics, University of Florida School of Medicine, Gainesville, FL, United States.

Barry J Byrne (BJ)

Department of Pediatrics, University of Florida School of Medicine, Gainesville, FL, United States.

Hilary J Vernon (HJ)

Department of Genetics, Johns Hopkins University School of Medicine, Baltimore, MD, United States.

Dominic N Reeds (DN)

Department of Medicine, Washington University School of Medicine, St. Louis, MO, United States.

Classifications MeSH