Gemogenovatucel-T (Vigil) immunotherapy as maintenance in frontline stage III/IV ovarian cancer (VITAL): a randomised, double-blind, placebo-controlled, phase 2b trial.


Journal

The Lancet. Oncology
ISSN: 1474-5488
Titre abrégé: Lancet Oncol
Pays: England
ID NLM: 100957246

Informations de publication

Date de publication:
12 2020
Historique:
received: 18 06 2020
revised: 21 08 2020
accepted: 24 08 2020
entrez: 3 12 2020
pubmed: 4 12 2020
medline: 5 1 2021
Statut: ppublish

Résumé

Gemogenovatucel-T is an autologous tumour cell vaccine manufactured from harvested tumour tissue, which specifically reduces expression of furin and downstream TGF-β1 and TGF-β2. The aim of this study was to determine the safety and efficacy of gemogenovatucel-T in front-line ovarian cancer maintenance. This randomised, double-blind, placebo-controlled, phase 2b trial involved 25 hospitals in the USA. Women aged 18 years and older with stage III/IV high-grade serous, endometrioid, or clear cell ovarian cancer in clinical complete response after a combination of surgery and five to eight cycles of chemotherapy involving carboplatin and paclitaxel, and an Eastern Cooperative Oncology Group status of 0 or 1 were eligible for inclusion in the study. Patients were randomly assigned (1:1) to gemogenovatucel-T or placebo by an independent third party interactive response system after successful screening using randomly permuted block sizes of two and four and stratified by extent of surgical cytoreduction and neoadjuvant versus adjuvant chemotherapy. Gemogenovatucel-T (1 × 10 Between Feb 11, 2015, and March 2, 2017, 310 patients consented to the study at 22 sites. 217 were excluded. 91 patients received gemogenovatucel-T (n=47) or placebo (n=44) and were analysed for safety and efficacy. The median follow-up from first dose of gemogenovatucel-T was 40·0 months (IQR 35·0-44·8) and from first dose of placebo was 39·8 months (35·5-44·6). Recurrence-free survival was 11·5 months (95% CI 7·5-not reached) for patients assigned to gemogenovatucel-T versus 8·4 months (7·9-15·5) for patients assigned to placebo (HR 0·69, 90% CI 0·44-1·07; one-sided p=0·078). Gemogenovatucel-T resulted in no grade 3 or 4 toxic effects. Two patients in the placebo group had five grade 3 toxic events, including arthralgia, bone pain, generalised muscle weakness, syncope, and dyspnea. Seven patients (four in the placebo group and three in the gemogenovatucel-T group) had 11 serious adverse events. No treatment-related deaths were reported in either of the groups. Front-line use of gemogenovatucel-T immunotherapy as maintenance was well tolerated but the primary endpoint was not met. Further investigation of gemogenovatucel-T in patients stratified by BRCA mutation status is warranted. Gradalis.

Sections du résumé

BACKGROUND
Gemogenovatucel-T is an autologous tumour cell vaccine manufactured from harvested tumour tissue, which specifically reduces expression of furin and downstream TGF-β1 and TGF-β2. The aim of this study was to determine the safety and efficacy of gemogenovatucel-T in front-line ovarian cancer maintenance.
METHODS
This randomised, double-blind, placebo-controlled, phase 2b trial involved 25 hospitals in the USA. Women aged 18 years and older with stage III/IV high-grade serous, endometrioid, or clear cell ovarian cancer in clinical complete response after a combination of surgery and five to eight cycles of chemotherapy involving carboplatin and paclitaxel, and an Eastern Cooperative Oncology Group status of 0 or 1 were eligible for inclusion in the study. Patients were randomly assigned (1:1) to gemogenovatucel-T or placebo by an independent third party interactive response system after successful screening using randomly permuted block sizes of two and four and stratified by extent of surgical cytoreduction and neoadjuvant versus adjuvant chemotherapy. Gemogenovatucel-T (1 × 10
FINDINGS
Between Feb 11, 2015, and March 2, 2017, 310 patients consented to the study at 22 sites. 217 were excluded. 91 patients received gemogenovatucel-T (n=47) or placebo (n=44) and were analysed for safety and efficacy. The median follow-up from first dose of gemogenovatucel-T was 40·0 months (IQR 35·0-44·8) and from first dose of placebo was 39·8 months (35·5-44·6). Recurrence-free survival was 11·5 months (95% CI 7·5-not reached) for patients assigned to gemogenovatucel-T versus 8·4 months (7·9-15·5) for patients assigned to placebo (HR 0·69, 90% CI 0·44-1·07; one-sided p=0·078). Gemogenovatucel-T resulted in no grade 3 or 4 toxic effects. Two patients in the placebo group had five grade 3 toxic events, including arthralgia, bone pain, generalised muscle weakness, syncope, and dyspnea. Seven patients (four in the placebo group and three in the gemogenovatucel-T group) had 11 serious adverse events. No treatment-related deaths were reported in either of the groups.
INTERPRETATION
Front-line use of gemogenovatucel-T immunotherapy as maintenance was well tolerated but the primary endpoint was not met. Further investigation of gemogenovatucel-T in patients stratified by BRCA mutation status is warranted.
FUNDING
Gradalis.

Identifiants

pubmed: 33271095
pii: S1470-2045(20)30533-7
doi: 10.1016/S1470-2045(20)30533-7
pii:
doi:

Substances chimiques

Cancer Vaccines 0
FANG vaccine 0

Banques de données

ClinicalTrials.gov
['NCT02346747']

Types de publication

Clinical Trial, Phase II Journal Article Multicenter Study Randomized Controlled Trial Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1661-1672

Informations de copyright

Copyright © 2020 Elsevier Ltd. All rights reserved.

Auteurs

Rodney P Rocconi (RP)

Division of Gynecologic Oncology, University of South Alabama-Mitchell Cancer Institute, Mobile, AL, USA.

Elizabeth A Grosen (EA)

Department of Obstetrics and Gynecology, Cancer Care Northwest, Spokane, WA, USA.

Sharad A Ghamande (SA)

Section of Gynecologic Oncology, Augusta University, Augusta, GA, USA.

John K Chan (JK)

Division of Gynecologic Oncology, California Pacific/Palo Alto Medical Foundation, Sutter Center Research Institute, San Francisco, CA, USA.

Minal A Barve (MA)

Department of Oncology, Mary Crowley Cancer Research Centers, Dallas, TX, USA; Department of Oncology, Texas Oncology, Dallas, TX, USA.

Jonathan Oh (J)

Department of Oncology, Texas Oncology, Dallas, TX, USA.

Devansu Tewari (D)

Department of Obstetrics and Gynecology, Kaiser Permanente, Irvine, CA, USA.

Peter C Morris (PC)

Division of Gynecologic Oncology, Nebraska Methodist Hospital, Omaha, NE, USA.

Erin E Stevens (EE)

Department of Gynecologic Oncology, Billings Clinic, Billings, MT, USA.

Justin N Bottsford-Miller (JN)

Department of Gynecologic Oncology, Billings Clinic, Billings, MT, USA.

Min Tang (M)

Stats Department, StatBeyond Consulting, Irvine, CA, USA.

Phylicia Aaron (P)

Department of Medical Affairs, Gradalis, Carollton, TX, USA.

Laura Stanbery (L)

Department of Medical Affairs, Gradalis, Carollton, TX, USA.

Staci Horvath (S)

Department of Site Research, Gradalis, Carollton, TX, USA.

Gladice Wallraven (G)

Department of Clinical and Regulatory Operations, Gradalis, Carollton, TX, USA.

Ernest Bognar (E)

Department of CMC Operations, Gradalis, Carollton, TX, USA; Department of CMC Operations, Gradalis, Carollton, TX, USA; Department of CMC Operations, Gradalis, Carollton, TX, USA.

Luisa Manning (L)

Department of Medical Affairs, Gradalis, Carollton, TX, USA.

John Nemunaitis (J)

Department of Medical Affairs, Gradalis, Carollton, TX, USA. Electronic address: jnemunaitis@gradalisinc.com.

David Shanahan (D)

Management Department, Gradalis, Carollton, TX, USA; Management Department, Gradalis, Carollton, TX, USA; Management Department, Gradalis, Carollton, TX, USA.

Brian M Slomovitz (BM)

Department of Obstetrics and Gynecology, Broward Health, Fort Lauderdale, FL, USA; Department of Obstetrics and Gynecology, Florida International University, Miami, FL, USA.

Thomas J Herzog (TJ)

Department of Obstetrics and Gynecology, University of Cincinnati Cancer Center, Cincinnati, OH, USA.

Bradley J Monk (BJ)

Department of Obstetrics and Gynecology, Arizona Oncology, Phoenix, AZ, USA.

Robert L Coleman (RL)

US Oncology Research, The Woodlands, TX, USA.

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Classifications MeSH