Measuring change in health-related quality of life: the impact of different analytical methods on the interpretation of treatment effects in glioma patients.

brain tumor patient-reported outcome quality of life questionnaire

Journal

Neuro-oncology practice
ISSN: 2054-2577
Titre abrégé: Neurooncol Pract
Pays: England
ID NLM: 101640528

Informations de publication

Date de publication:
Dec 2020
Historique:
entrez: 11 12 2020
pubmed: 12 12 2020
medline: 12 12 2020
Statut: epublish

Résumé

Different analytical methods may lead to different conclusions about the impact of treatment on health-related quality of life (HRQoL). This study aimed to examine 3 different methods to evaluate change in HRQoL and to study whether these methods result in different conclusions. HRQoL data from 15 randomized clinical trials were combined (CODAGLIO project). Change in HRQoL scores, measured with the European Organization for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 and BN20 questionnaires, was analyzed in 3 ways: (1) at the group level, comparing mean changes in scale/item scores between treatment arms, (2) at the patient level per scale/item, calculating the percentage of patients that deteriorated, improved, or remained stable per scale/item, and (3) at the individual patient level, combining all scales/items. Baseline and first follow-up HRQoL data were available for 3727 patients. At the group scale/item level, only the item "hair loss" showed a significant and clinically relevant change (ie, ≥10 points) over time, whereas change scores on the other scales/items were statistically significant only (all Different analytical methods of changes in HRQoL result in distinct conclusions of treatment effects, all of which may be relevant for informing clinical decision making.

Sections du résumé

BACKGROUND BACKGROUND
Different analytical methods may lead to different conclusions about the impact of treatment on health-related quality of life (HRQoL). This study aimed to examine 3 different methods to evaluate change in HRQoL and to study whether these methods result in different conclusions.
METHODS METHODS
HRQoL data from 15 randomized clinical trials were combined (CODAGLIO project). Change in HRQoL scores, measured with the European Organization for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 and BN20 questionnaires, was analyzed in 3 ways: (1) at the group level, comparing mean changes in scale/item scores between treatment arms, (2) at the patient level per scale/item, calculating the percentage of patients that deteriorated, improved, or remained stable per scale/item, and (3) at the individual patient level, combining all scales/items.
RESULTS RESULTS
Baseline and first follow-up HRQoL data were available for 3727 patients. At the group scale/item level, only the item "hair loss" showed a significant and clinically relevant change (ie, ≥10 points) over time, whereas change scores on the other scales/items were statistically significant only (all
CONCLUSIONS CONCLUSIONS
Different analytical methods of changes in HRQoL result in distinct conclusions of treatment effects, all of which may be relevant for informing clinical decision making.

Identifiants

pubmed: 33304601
doi: 10.1093/nop/npaa033
pii: npaa033
pmc: PMC7716184
doi:

Types de publication

Journal Article

Langues

eng

Pagination

668-675

Informations de copyright

© The Author(s) 2020. Published by Oxford University Press on behalf of the Society for Neuro-Oncology and the European Association of Neuro-Oncology.

Références

Chin J Cancer. 2014 Jan;33(1):40-5
pubmed: 24384239
J Clin Oncol. 2015 Jul 1;33(19):2166-75
pubmed: 26014298
J Neurooncol. 2018 Sep;139(2):359-368
pubmed: 29663172
BMJ Open. 2018 Jan 10;8(1):e019117
pubmed: 29326191
Bioinformatics. 2016 Sep 15;32(18):2847-9
pubmed: 27207943
Expert Rev Pharmacoecon Outcomes Res. 2011 Apr;11(2):171-84
pubmed: 21476819
Eur J Cancer. 2015 Jul;51(10):1321-30
pubmed: 25899986
J Clin Epidemiol. 2016 Jan;69:79-88
pubmed: 26327487
J Clin Oncol. 1998 Jan;16(1):139-44
pubmed: 9440735
JAMA Oncol. 2018 Apr 1;4(4):495-504
pubmed: 29392280
Health Qual Life Outcomes. 2016 Jun 07;14:87
pubmed: 27267486
Semin Oncol. 2014 Aug;41(4):541-552
pubmed: 25173146
Eur J Cancer. 2010 Apr;46(6):1033-40
pubmed: 20181476
Lancet Oncol. 2016 Nov;17(11):e510-e514
pubmed: 27769798

Auteurs

Marijke B Coomans (MB)

Department of Neurology, Leiden University Medical Center, Leiden, the Netherlands.

Martin J B Taphoorn (MJB)

Department of Neurology, Leiden University Medical Center, Leiden, the Netherlands.
Department of Neurology, Haaglanden Medical Center, Den Haag, the Netherlands.

Neil K Aaronson (NK)

Division of Psychosocial Research and Epidemiology, The Netherlands Cancer Institute, Amsterdam, the Netherlands.

Brigitta G Baumert (BG)

Institute of Radiation-Oncology, Kantonsspital Graubünden, Chur, Switzerland.
Department of Radiation Oncology (MAASTRO clinic), and GROW (School for Oncology and Developmental Biology), Maastricht University Medical Center, Maastricht, the Netherlands.

Martin van den Bent (M)

The Brain Tumor Center, Erasmus MC Cancer Institute, Rotterdam, the Netherlands.

Andrew Bottomley (A)

Quality of Life Department, European Organisation for Research and Treatment of Cancer, Brussels, Belgium.

Alba A Brandes (AA)

Department of Medical Oncology, Azienda USL-IRCCS Institute of Neurological Sciences, Bologna, Italy.

Olivier Chinot (O)

Aix-Marseille Université, APHM, CNRS, INP, Inst Neurophysiopathol, CHU Timone, Service de Neuro-Oncologie, Marseille, France.

Corneel Coens (C)

Quality of Life Department, European Organisation for Research and Treatment of Cancer, Brussels, Belgium.

Thierry Gorlia (T)

European Organization for Research and Treatment of Cancer Headquarters, Brussels, Belgium.

Ulrich Herrlinger (U)

Division of Clinical Neurooncology, Department of Neurology, University of Bonn Medical Center, Bonn, Germany.

Florence Keime-Guibert (F)

Groupe Hôpital Pitié-Salpetrière, Paris, France.

Annika Malmström (A)

Department of Advanced Home Care and Department of Clinical and Experimental Medicine, Linköping University, Linköping, Sweden.

Francesca Martinelli (F)

Quality of Life Department, European Organisation for Research and Treatment of Cancer, Brussels, Belgium.

Roger Stupp (R)

Northwestern University, Feinberg School of Medicine, Chicago, Illinois, US.

Andrea Talacchi (A)

Department of Neurosciences, Azienda Ospedaliera San Giovanni Addolorata, Roma, Italia.

Michael Weller (M)

Department of Neurology, University Hospital and University of Zurich, Zurich, Switzerland.

Wolfgang Wick (W)

Neurology Clinic and National Centre for Tumour Diseases, University Hospital Heidelberg, Heidelberg, Germany.
German Consortium of Translational Cancer Research (DKTK), Clinical Cooperation Unit Neurooncology, German Cancer Research Center, Heidelberg, Germany.

Jaap C Reijneveld (JC)

Department of Neurology and Brain Tumour Center Amsterdam, Amsterdam University Medical Center, Amsterdam, the Netherlands.
Stichting Epilepsie Instellingen Nederland (SEIN), Heemstede, the Netherlands.

Linda Dirven (L)

Department of Neurology, Leiden University Medical Center, Leiden, the Netherlands.
Department of Neurology, Haaglanden Medical Center, Den Haag, the Netherlands.

Classifications MeSH