Barriers and Considerations for Diagnosing Rare Diseases in Indigenous Populations.

Indigenous populations diagnosis equity genomics rare diseases

Journal

Frontiers in pediatrics
ISSN: 2296-2360
Titre abrégé: Front Pediatr
Pays: Switzerland
ID NLM: 101615492

Informations de publication

Date de publication:
2020
Historique:
received: 03 07 2020
accepted: 02 11 2020
entrez: 31 12 2020
pubmed: 1 1 2021
medline: 1 1 2021
Statut: epublish

Résumé

Advances in omics and specifically genomic technologies are increasingly transforming rare disease diagnosis. However, the benefits of these advances are disproportionately experienced within and between populations, with Indigenous populations frequently experiencing diagnostic and therapeutic inequities. The International Rare Disease Research Consortium (IRDiRC) multi-stakeholder partnership has been advancing toward the vision of all people living with a rare disease receiving an accurate diagnosis, care, and available therapy within 1 year of coming to medical attention. In order to further progress toward this vision, IRDiRC has created a taskforce to explore the access barriers to diagnosis of rare genetic diseases faced by Indigenous peoples, with a view of developing recommendations to overcome them. Herein, we provide an overview of the state of play of current barriers and considerations identified by the taskforce, to further stimulate awareness of these issues and the passage toward solutions. We focus on analyzing barriers to accessing genetic services, participating in genomic research, and other aspects such as concerns about data sharing, the handling of biospecimens, and the importance of capacity building.

Identifiants

pubmed: 33381478
doi: 10.3389/fped.2020.579924
pmc: PMC7767925
doi:

Types de publication

Journal Article Review

Langues

eng

Pagination

579924

Informations de copyright

Copyright © 2020 D'Angelo, Hermes, McMaster, Prichep, Richer, van der Westhuizen, Repetto, Mengchun, Malherbe, Reichardt, Arbour, Hudson, du Plessis, Haendel, Wilcox, Lynch, Rind, Easteal, Estivill, Thomas and Baynam.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

J Law Med Ethics. 2020 Mar;48(1):218-220
pubmed: 32342771
Hum Gene Ther. 2018 Feb;29(2):128-135
pubmed: 29284292
Genet Med. 2017 Mar;19(3):345-351
pubmed: 27632687
EMBO Mol Med. 2019 May;11(5):
pubmed: 30979709
J Genet Couns. 2020 Aug;29(4):562-573
pubmed: 32329955
Am J Med Genet A. 2015 Jul;167(7):1659-67
pubmed: 25851998
Sci Rep. 2017 Feb 09;7:42187
pubmed: 28181990
Adv Exp Med Biol. 2017;1031:511-520
pubmed: 29214589
Nature. 2016 Oct 12;538(7624):161-164
pubmed: 27734877
F1000Res. 2015 Sep 23;4:891
pubmed: 26594346
Soc Sci (Basel). 2019 Apr;8(4):
pubmed: 31463160
Ethn Dis. 2019 Dec 12;29(Suppl 3):659-668
pubmed: 31889771
Genet Med. 2019 Nov;21(11):2422-2430
pubmed: 31110330
Mol Genet Metab. 2016 Apr;117(4):393-400
pubmed: 26846157
Med J Aust. 2008 Nov 3;189(9):499-503
pubmed: 18976191
Nat Genet. 2020 Jan;52(1):21-26
pubmed: 31873296
J Genet Couns. 2020 Apr;29(2):202-205
pubmed: 32200573
Eur J Hum Genet. 2014 Mar;22(3):322-6
pubmed: 23860041
Nature. 2020 Jan;577(7788):11-12
pubmed: 31871327
J Empir Res Hum Res Ethics. 2015 Oct;10(4):347-59
pubmed: 26376752
Hum Genomics. 2017 Mar 16;11(1):5
pubmed: 28302154
Front Genet. 2019 Dec 20;10:1209
pubmed: 31921282
Cell. 2019 Mar 21;177(1):32-37
pubmed: 30901545
Nat Rev Genet. 2020 Jun;21(6):377-384
pubmed: 32251390
Pharmgenomics Pers Med. 2018 Apr 10;11:59-66
pubmed: 29692621
Sci Data. 2016 Mar 15;3:160018
pubmed: 26978244
Nature. 2017 Jun 21;546(7659):474
pubmed: 28640268
Hum Mutat. 2015 Nov;36(11):E2441-53
pubmed: 26173767
Genetics. 2005 Feb;169(2):517-21
pubmed: 15731516
J Community Genet. 2016 Apr;7(2):119-26
pubmed: 26536881
Front Public Health. 2020 Apr 24;8:111
pubmed: 32391301
Mol Genet Metab. 2020 Apr;129(4):243-254
pubmed: 32033911
Paediatr Child Health. 2011 Mar;16(3):e23-4
pubmed: 22379385
Front Public Health. 2017 Apr 10;5:31
pubmed: 28443272
Med J Aust. 2016 Oct 17;205(8):379
pubmed: 27736627
CMAJ. 2012 Mar 6;184(4):E211-2
pubmed: 22311952
BMC Health Serv Res. 2013 Mar 06;13:83
pubmed: 23497140
Nature. 2016 Jan 7;529(7584):9-10
pubmed: 26738574
Genet Med. 2008 Jul;10(7):545-50
pubmed: 18580685
Med J Aust. 2009 May 18;190(10):574-9
pubmed: 19450207
Hum Mutat. 2012 May;33(5):884-6
pubmed: 22457028
J Genet Couns. 2019 Apr;28(2):407-418
pubmed: 30629780
Commun Biol. 2019 Jan 7;2:9
pubmed: 30623105
Eur J Hum Genet. 2020 Feb;28(2):165-173
pubmed: 31527858
JCO Glob Oncol. 2020 Mar;6:83-91
pubmed: 32213083
Cell. 2019 Mar 21;177(1):26-31
pubmed: 30901543
Hum Mutat. 2012 May;33(5):803-8
pubmed: 22422702
Nat Commun. 2018 Jul 27;9(1):2957
pubmed: 30054469
Mol Genet Metab. 2010 Oct-Nov;101(2-3):178-82
pubmed: 20732827
Clin Transl Sci. 2018 Jan;11(1):21-27
pubmed: 28796445
Annu Rev Genomics Hum Genet. 2019 Aug 31;20:495-517
pubmed: 30892943
Nat Genet. 2020 Feb;52(2):135
pubmed: 32025002
Aust J Prim Health. 2016 Nov;22(5):377-382
pubmed: 28442021
N Engl J Med. 2019 Aug 15;381(7):668-676
pubmed: 31412182
J Med Genet. 2018 Apr;55(4):233-239
pubmed: 29358271
Nat Rev Genet. 2019 Sep;20(9):495
pubmed: 31420601

Auteurs

Carla S D'Angelo (CS)

IRDiRC Scientific Secretariat, National Institute for Health and Medical Research, Paris, France.

Azure Hermes (A)

National Centre for Indigenous Genomics, Australian National University, Canberra, ACT, Australia.

Christopher R McMaster (CR)

Department of Pharmacology, Dalhousie University, Halifax, NS, Canada.

Elissa Prichep (E)

Precision Medicine, Platform on Shaping the Future of Health and Healthcare, World Economic Forum, San Francisco, CA, United States.

Étienne Richer (É)

Institute of Genetics, Canadian Institutes of Health Research, Government of Canada, Ottawa, ON, Canada.

Francois H van der Westhuizen (FH)

Human Metabolomics, North-West University, Potchefstroom, South Africa.

Gabriela M Repetto (GM)

Facultad de Medicina, Center for Genetics and Genomics, Clinica Alemana Universidad del Desarrollo, Santiago, Chile.

Gong Mengchun (G)

Institute of Health Management, Southern Medical University, Guangdong, China.

Helen Malherbe (H)

KwaZulu-Natal Research Innovation and Sequencing Platform, University of KwaZulu-Natal, Durban, South Africa.
Rare Diseases South Africa, Johannesburg, South Africa.

Juergen K V Reichardt (JKV)

Australian Institute of Tropical Health and Medicine, James Cook University, Smithfield, QLD, Australia.

Laura Arbour (L)

Department of Medical Genetics, University of British Columbia, Victoria, BC, Canada.

Maui Hudson (M)

Faculty of Maori and Indigenous Studies, University of Waikato, Hamilton, New Zealand.

Kelly du Plessis (K)

Rare Diseases South Africa, Johannesburg, South Africa.

Melissa Haendel (M)

Oregon Clinical and Translational Research Institute, Oregon Health and Science University, Portland, OR, United States.

Phillip Wilcox (P)

Department of Mathematics and Statistics, University of Otago, Dunedin, New Zealand.

Sally Ann Lynch (SA)

National Rare Disease Office, Mater Misericordiae University Hospital, Dublin, Ireland.
Academic Centre on Rare Diseases, University College Dublin, Dublin, Ireland.

Shamir Rind (S)

Western Australian Register of Developmental Anomalies, Perth, WA, Australia.

Simon Easteal (S)

National Centre for Indigenous Genomics, Australian National University, Canberra, ACT, Australia.

Xavier Estivill (X)

Quantitative Genomics Laboratories (qgenomics), Esplugues de Llobregat, Barcelona, Spain.

Yarlalu Thomas (Y)

Western Australian Register of Developmental Anomalies, Perth, WA, Australia.

Gareth Baynam (G)

Western Australian Register of Developmental Anomalies, Perth, WA, Australia.
Genetic Services of Western Australia, Department of Health, Government of Western Australia, Perth, WA, Australia.
Faculty of Health and Medicine, Division of Pediatrics, University of Western Australia, Perth, WA, Australia.
Telethon Kids Institute, University of Western Australia, Perth, WA, Australia.
Faculty of Medicine, University of Notre Dame, Fremantle, WA, Australia.
Faculty of Science and Engineering, Spatial Sciences, Curtin University, Perth, WA, Australia.
Faculty of Medicine, Notre Dame University, Perth, WA, Australia.
School of Population and Global Health, University of Melbourne, Melbourne, VIC, Australia.

Classifications MeSH