Cell Therapy for Chronic TBI: Interim Analysis of the Randomized Controlled STEMTRA Trial.


Journal

Neurology
ISSN: 1526-632X
Titre abrégé: Neurology
Pays: United States
ID NLM: 0401060

Informations de publication

Date de publication:
04 Jan 2021
Historique:
received: 09 02 2020
accepted: 20 10 2020
entrez: 5 1 2021
pubmed: 6 1 2021
medline: 6 1 2021
Statut: aheadofprint

Résumé

To determine if chronic motor deficits secondary to traumatic brain injury (TBI) can be improved by implantation of allogeneic modified bone marrow-derived mesenchymal stromal/stem cells (SB623). This 6-month interim analysis of the 1-year double-blind, randomized, surgical sham-controlled, phase 2 STEMTRA trial (NCT02416492) evaluated safety and efficacy of the stereotactic intracranial implantation of SB623 in patients with stable chronic motor deficits secondary to TBI. Patients in this multi-center trial (N = 63) underwent randomization in a 1:1:1:1 ratio to 2.5 × 10 The primary efficacy endpoint of significant improvement from baseline of Fugl-Meyer Motor Scale score at 6 months for SB623-treated patients was achieved. SB623-treated patients improved by (LS mean [SE]) +8.3 (1.4) vs +2.3 (2.5) for control at 6 months, the LS mean difference was 6.0 (95% CI: 0.3-11.8); SB623 cell implantation appeared to be safe and well tolerated, and patients implanted with SB623 experienced significant improvement from baseline motor status at 6 months compared to controls. This study provides Class I evidence that implantation of SB623 was well tolerated and associated with improvement in motor status.

Identifiants

pubmed: 33397772
pii: WNL.0000000000011450
doi: 10.1212/WNL.0000000000011450
pmc: PMC8055341
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Commentaires et corrections

Type : CommentIn

Informations de copyright

Copyright © 2021 The Author(s). Published by Wolters Kluwer Health, Inc. on behalf of the American Academy of Neurology.

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Auteurs

Masahito Kawabori (M)

Department of Neurosurgery, Hokkaido University Hospital, Sapporo, Japan. masahitokawabori@yahoo.co.jp.

Alan H Weintraub (AH)

Rocky Mountain Regional Brain Injury System and University of Colorado School of Medicine, Englewood, CO, USA.

Hideaki Imai (H)

Department of Neurosurgery, Hokkaido University Hospital, Sapporo, Japan.

Laroslav Zinkevych (L)

Ukraine Presidential Hospital, Kiev, Ukraine.

Peter McAllister (P)

New England Institute for Neurology and Headache, Stamford, CT; New England Institute for Clinical Research, Stamford, CT; Department of Neurology, Yale University, New Haven, CT; Frank Netter School of Medicine, Quinnipiac University, Hamden, CT, USA.

Gary K Steinberg (GK)

Department of Neurosurgery and Stanford Stroke Center, Stanford University School of Medicine and Stanford Health Care, Stanford, CA, USA.

Benjamin M Frishberg (BM)

The Neurology Center of Southern California, Carlsbad, CA, USA.

Takao Yasuhara (T)

Department of Neurological Surgery, Okayama University Graduate School of Medicine, Okayama University Hospital, Okayama, Japan.

Jefferson W Chen (JW)

Department of Neurological Surgery, University of California, Irvine, School of Medicine, Irvine, CA, USA.

Steven C Cramer (SC)

Department of Neurology, University of California, Los Angeles; and California Rehabilitation Institute; Los Angeles, CA, USA.

Achal S Achrol (AS)

Department of Neurosurgery, Loma Linda University Medical Center, Loma Linda, CA, USA.

Neil E Schwartz (NE)

Department of Neurology and Neurological Sciences, and Stanford Stroke Center, Stanford University School of Medicine and Stanford Health Care, Stanford, CA, USA.

Jun Suenaga (J)

Department of Neurosurgery, Yokohama City University School of Medicine, Yokohama, Kanagawa, Japan.

Daniel C Lu (DC)

Department of Neurosurgery, Ronald Reagan UCLA Medical Center, Los Angeles, CA, USA.

Ihor Semeniv (I)

Clinical Hospital Feofaniya, Kiev, Ukraine.

Hajime Nakamura (H)

Department of Neurosurgery, Osaka University Graduate School of Medicine, Suita, Osaka, Japan.

Douglas Kondziolka (D)

Department of Neurosurgery, New York University and NYU Langone Medical Center, New York, NY, USA.

Dai Chida (D)

SanBio, Inc., Mountain View, CA, USA.

Takehiko Kaneko (T)

SanBio, Inc., Mountain View, CA, USA.

Yasuaki Karasawa (Y)

Department of Neurosurgery, The University of Tokyo Hospital, Tokyo, Japan.

Susan Paadre (S)

Biostatistical Consulting Inc., Lexington, MA, USA.

Bijan Nejadnik (B)

SanBio, Inc., Mountain View, CA, USA.

Damien Bates (D)

SanBio, Inc., Mountain View, CA, USA.

Anthony H Stonehouse (AH)

Watson & Stonehouse Enterprises LLC, Pacific Grove, CA, USA.

R Mark Richardson (RM)

Massachusetts General Hospital and Harvard Medical School, Boston, MA, USA.

David O Okonkwo (DO)

Department of Neurological Surgery, University of Pittsburgh Medical Center, Pittsburgh, PA, USA.

Classifications MeSH