Musculoskeletal Features without Ataxia Associated with a Novel de novo Mutation in

KCNA1 ataxia creatine kinase molecular modeling muscle hypertrophy myokymia neuromyotonia patch clamp

Journal

Biomedicines
ISSN: 2227-9059
Titre abrégé: Biomedicines
Pays: Switzerland
ID NLM: 101691304

Informations de publication

Date de publication:
14 Jan 2021
Historique:
received: 30 11 2020
revised: 02 01 2021
accepted: 06 01 2021
entrez: 20 1 2021
pubmed: 21 1 2021
medline: 21 1 2021
Statut: epublish

Résumé

The

Identifiants

pubmed: 33466780
pii: biomedicines9010075
doi: 10.3390/biomedicines9010075
pmc: PMC7829709
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : Ataxia UK
ID : grant 2018 to P.I.
Organisme : University of Bari
ID : (Fondi di Ateneo 2017-2018) to P.I. and J.-F.D
Organisme : Canadian Institutes for Health Research (CIHR)
ID : Grant PJT-169160 to R.B.
Organisme : Natural Sciences and Engineering Research Council (NSERC)
ID : Grant RGPIN-2017-06871 to R.B.
Organisme : AFM
ID : (grant 22431) to C.F.
Organisme : Telethon
ID : (grant GUP19002) to C.F.
Pays : Italy
Organisme : Malta Council for Science and Technology
ID : Grant BooKind E20LG42 to M.C.D.A.

Références

J Neurol. 2006 Jul;253(7):957-9
pubmed: 16511644
Int J Mol Sci. 2020 Oct 14;21(20):
pubmed: 33066705
Science. 2005 Aug 5;309(5736):897-903
pubmed: 16002581
J Mol Biol. 1993 Dec 5;234(3):779-815
pubmed: 8254673
Neurobiol Dis. 2012 Sep;47(3):310-21
pubmed: 22609489
Ann Neurol. 2000 Oct;48(4):647-56
pubmed: 11026449
Nature. 2006 Dec 7;444(7120):775-9
pubmed: 17136096
Int J Mol Sci. 2020 Apr 17;21(8):
pubmed: 32316562
Nat Commun. 2016 Jul 06;7:12102
pubmed: 27381274
Mol Cell Neurosci. 2017 Sep;83:6-12
pubmed: 28666963
Nephron. 2018;139(4):359-366
pubmed: 29791908
Nature. 2005 Aug 11;436(7052):852-6
pubmed: 16094369
Neurogenetics. 2016 Jan;17(1):11-6
pubmed: 26395884
Neuron. 2015 Jan 21;85(2):238-56
pubmed: 25611506
Neuron. 1998 Apr;20(4):809-19
pubmed: 9581771
Neuromuscul Disord. 2004 Oct;14(10):689-93
pubmed: 15351427
Curr Protoc Bioinformatics. 2016 Jun 20;54:5.6.1-5.6.37
pubmed: 27322406
J Neurosci. 1998 Sep 15;18(18):7200-15
pubmed: 9736643
Nat Neurosci. 2003 Apr;6(4):378-83
pubmed: 12612586
Nat Genet. 1994 Oct;8(2):136-40
pubmed: 7842011
Int J Mol Sci. 2020 Apr 22;21(8):
pubmed: 32331416
J Neurosci. 1999 Jul 15;19(14):5768-81
pubmed: 10407018
PLoS Comput Biol. 2016 Jan 11;12(1):e1004704
pubmed: 26751683
Hum Mol Genet. 2018 Feb 15;27(4):625-637
pubmed: 29294000
Bone. 2021 Jan;142:115645
pubmed: 32949783
Am J Physiol Cell Physiol. 2007 Feb;292(2):C778-87
pubmed: 16956965
J Chem Theory Comput. 2016 Jan 12;12(1):405-13
pubmed: 26631602
J Med Genet. 2020 Feb;57(2):132-137
pubmed: 31586945
Sci Adv. 2017 Oct 25;3(10):e1701099
pubmed: 29075666
J Chem Phys. 2020 Jul 28;153(4):044130
pubmed: 32752662
Neuron. 2005 Feb 3;45(3):379-88
pubmed: 15694325
Neuron. 2011 Dec 8;72(5):713-20
pubmed: 22153369
Front Physiol. 2015 Jan 15;5:525
pubmed: 25642194
Trends Neurosci. 2004 Apr;27(4):210-7
pubmed: 15046880
Elife. 2016 Oct 06;5:
pubmed: 27710769
Neurogenetics. 2007 Apr;8(2):131-5
pubmed: 17136396
Neurogenetics. 2016 Oct;17(4):245-249
pubmed: 27271339
J Comput Chem. 2009 Jul 30;30(10):1545-614
pubmed: 19444816
J Comput Chem. 2008 Aug;29(11):1859-65
pubmed: 18351591
Neuroscience. 2008 Dec 2;157(3):577-87
pubmed: 18926884
Front Pharmacol. 2016 May 10;7:121
pubmed: 27242528
J Biol Chem. 2014 Jun 6;289(23):16452-61
pubmed: 24742679
Proc Natl Acad Sci U S A. 2012 May 29;109(22):8552-7
pubmed: 22538811
J Gen Physiol. 2011 Jun;137(6):563-77
pubmed: 21624947
J Gen Physiol. 2001 Mar;117(3):205-18
pubmed: 11222625
J Biol Chem. 2012 Nov 16;287(47):40091-8
pubmed: 23019337
Brain. 2014 Apr;137(Pt 4):1009-18
pubmed: 24578548
J Phys Chem B. 2011 Jul 14;115(27):8732-8
pubmed: 21692541
Am J Med Genet A. 2018 Aug;176(8):1748-1752
pubmed: 30055040
Brain. 1999 May;122 ( Pt 5):817-25
pubmed: 10355668
Epilepsia. 2009 Sep;50(9):2027-34
pubmed: 19490051
Nature. 2004 Feb 5;427(6974):548-53
pubmed: 14765197
Nat Struct Mol Biol. 2014 Mar;21(3):244-52
pubmed: 24487958
Nature. 2007 Nov 15;450(7168):376-82
pubmed: 18004376

Auteurs

Paola Imbrici (P)

Department of Pharmacy-Drug Sciences, University of Bari Aldo Moro, 70121 Bari, Italy.

Andrea Accogli (A)

Medical Genetics Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Rikard Blunck (R)

Department of Physics, Université de Montréal, Montréal, QC H3C 3J7, Canada.

Concetta Altamura (C)

Department of Biomedical Sciences and Human Oncology, School of Medicine, University of Bari Aldo Moro, 70121 Bari, Italy.

Michele Iacomino (M)

Medical Genetics Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Maria Cristina D'adamo (MC)

Department of Physiology and Biochemistry, Faculty of Medicine and Surgery, University of Malta, MDS-2080 Msida, Malta.

Anna Allegri (A)

Paediatric Endocrinology Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Marina Pedemonte (M)

Paediatric Neurology and Neuromuscular Disorders Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Noemi Brolatti (N)

Paediatric Neurology and Neuromuscular Disorders Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Stella Vari (S)

Paediatric Neurology and Neuromuscular Disorders Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Matteo Cataldi (M)

Neuropsychiatric Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Valeria Capra (V)

Neurosurgery Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Stefano Gustincich (S)

Department of Neuroscience and Brain Technologies, Istituto Italiano di Tecnologia, 80131 Genoa, Italy.

Federico Zara (F)

Medical Genetics Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.

Jean-Francois Desaphy (JF)

Department of Biomedical Sciences and Human Oncology, School of Medicine, University of Bari Aldo Moro, 70121 Bari, Italy.

Chiara Fiorillo (C)

Paediatric Neurology and Neuromuscular Disorders Unit, IRCCS Institute "G. Gaslini", 80131 Genoa, Italy.
Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genoa, 16126 Genoa, Italy.

Classifications MeSH