Greater disease burden of variegate porphyria than hereditary coproporphyria: An Israeli nationwide study of neurocutaneous porphyrias.

Clinical HCP HCP, hereditary coproporphyria NCP, neurocutaneous porphyrias Neurocutaneous Porphyria Systemic VP VP, variegate porphyria

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Mar 2021
Historique:
received: 30 12 2020
accepted: 31 12 2020
entrez: 25 1 2021
pubmed: 26 1 2021
medline: 26 1 2021
Statut: epublish

Résumé

Hereditary coproporphyria (HCP) and variegate porphyria (VP) are referred to as neurocutaneous porphyrias (NCP). Data concerning their systemic presentation are limited and no direct attempt of comparison of the two has ever been made. Our aim was to describe the type and frequency of systemic manifestations of NCPs in Israeli patients. A cross-sectional survey was conducted. The study population included all patients with NCP diagnosed at the Israeli National Service for Biochemical Diagnoses of Porphyrias (INSP) between 1988 and 2019. Of the 83 patients with NCP who were alive in 2019, 61 (73%) completed the survey, 40 with VP and 21 with HCP. Systemic symptoms were reported by 63% of the VP group and 62% of the HCP group (

Identifiants

pubmed: 33489763
doi: 10.1016/j.ymgmr.2021.100707
pii: S2214-4269(21)00001-X
pmc: PMC7811049
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100707

Informations de copyright

© 2021 The Authors. Published by Elsevier Inc.

Déclaration de conflit d'intérêts

The authors declare they have no conflict of interest.

Références

Hepatol Commun. 2018 Dec 20;3(2):193-206
pubmed: 30766957
PLoS Med. 2019 Nov 19;16(11):e1002967
pubmed: 31743343
BMC Med Genet. 2008 Jun 20;9:54
pubmed: 18570668
Indian J Gastroenterol. 2016 Nov;35(6):405-418
pubmed: 27796941
Hautarzt. 2016 Mar;67(3):221-5
pubmed: 26743053
Hepatology. 2020 May;71(5):1546-1558
pubmed: 31512765
Gastroenterology. 2019 Aug;157(2):365-381.e4
pubmed: 31085196
J Inherit Metab Dis. 2013 Sep;36(5):849-57
pubmed: 23114748
Cell Mol Biol (Noisy-le-grand). 2009 Feb 16;55(1):72-83
pubmed: 19268005
Int J Biochem. 1980;12(5-6):837-53
pubmed: 7450140
Clin Biochem. 2000 Aug;33(6):465-73
pubmed: 11074238
J Emerg Med. 2015 Sep;49(3):305-12
pubmed: 26159905
Med Clin North Am. 2018 Jul;102(4):745-763
pubmed: 29933827
Lancet. 2010 Mar 13;375(9718):924-37
pubmed: 20226990
Rambam Maimonides Med J. 2018 Apr 19;9(2):
pubmed: 29553924
Br J Haematol. 2017 Feb;176(4):527-538
pubmed: 27982422
N Engl J Med. 2017 Nov 23;377(21):2101
pubmed: 29166231
Orphanet J Rare Dis. 2020 Feb 21;15(1):56
pubmed: 32085780
Am J Hum Genet. 1999 Oct;65(4):984-94
pubmed: 10486317
Mol Genet Metab. 2016 Nov;119(3):278-283
pubmed: 27595545
Cell Mol Biol (Noisy-le-grand). 2009 Jul 01;55(2):79-88
pubmed: 19656455
J Eur Acad Dermatol Venereol. 2020 Jan;34(1):184-187
pubmed: 31264284
Am J Med. 2014 Dec;127(12):1233-41
pubmed: 25016127
Clin Res Hepatol Gastroenterol. 2015 Sep;39(4):412-25
pubmed: 26142871
Eur J Med Genet. 2019 Dec;62(12):103589
pubmed: 30476629

Auteurs

Ran Kaftory (R)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.

Yonatan Edel (Y)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
National Service for the Biochemical Diagnoses of Porphyrias, Rabin Medical Center - Beilinson Hospital, Petah Tikva 4941492, Israel.
Department of Internal Medicine C, Rabin Medical Center - Beilinson Hospital, Petah Tikva 4941492, Israel.

Igor Snast (I)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
Photodermatosis Service, Division of Dermatology, Rabin Medical Center, Petah Tikva 4941492, Israel.

Moshe Lapidoth (M)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
Photodermatosis Service, Division of Dermatology, Rabin Medical Center, Petah Tikva 4941492, Israel.

Rivka Mamet (R)

National Service for the Biochemical Diagnoses of Porphyrias, Rabin Medical Center - Beilinson Hospital, Petah Tikva 4941492, Israel.

Avishay Elis (A)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
Department of Internal Medicine C, Rabin Medical Center - Beilinson Hospital, Petah Tikva 4941492, Israel.

Emmilia Hodak (E)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
Photodermatosis Service, Division of Dermatology, Rabin Medical Center, Petah Tikva 4941492, Israel.

Assi Levi (A)

Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv 6997801, Israel.
Photodermatosis Service, Division of Dermatology, Rabin Medical Center, Petah Tikva 4941492, Israel.

Classifications MeSH