Unraveling Molecular Pathways Altered in MeCP2-Related Syndromes, in the Search for New Potential Avenues for Therapy.

MECP2 duplication syndrome MeCP2 Rett syndrome miRNA biomarkers microcephaly

Journal

Biomedicines
ISSN: 2227-9059
Titre abrégé: Biomedicines
Pays: Switzerland
ID NLM: 101691304

Informations de publication

Date de publication:
03 Feb 2021
Historique:
received: 22 12 2020
revised: 25 01 2021
accepted: 30 01 2021
entrez: 6 2 2021
pubmed: 7 2 2021
medline: 7 2 2021
Statut: epublish

Résumé

Methyl-CpG-binding protein 2 (MeCP2) is an X-linked epigenetic modulator whose dosage is critical for neural development and function. Loss-of-function mutations in

Identifiants

pubmed: 33546327
pii: biomedicines9020148
doi: 10.3390/biomedicines9020148
pmc: PMC7913493
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : Instituto de Salud Carlos III
ID : PI15/01082

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Auteurs

Alba-Aina Castells (AA)

Neural Development Lab, Departament de Patologia i Terapèutica Experimental, Institut de Neurociències, Universitat de Barcelona, l'Hospitalet de Llobregat, 08907 Barcelona, Spain.
Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.
IDIBELL, l'Hospitalet de Llobregat, 08908 Barcelona, Spain.

Rafel Balada (R)

Neural Development Lab, Departament de Patologia i Terapèutica Experimental, Institut de Neurociències, Universitat de Barcelona, l'Hospitalet de Llobregat, 08907 Barcelona, Spain.
IDIBELL, l'Hospitalet de Llobregat, 08908 Barcelona, Spain.

Alba Tristán-Noguero (A)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Mar O'Callaghan (M)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Elisenda Cortès-Saladelafont (E)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Ainhoa Pascual-Alonso (A)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Àngels Garcia-Cazorla (À)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Judith Armstrong (J)

Departments of Neurology, Biochemistry and Genetics, Institut Pediàtric de Recerca, CIBERER and ISCIII, Hospital San Joan de Déu, Esplugues de Llobregat, 08950 Barcelona, Spain.

Soledad Alcántara (S)

Neural Development Lab, Departament de Patologia i Terapèutica Experimental, Institut de Neurociències, Universitat de Barcelona, l'Hospitalet de Llobregat, 08907 Barcelona, Spain.
IDIBELL, l'Hospitalet de Llobregat, 08908 Barcelona, Spain.

Classifications MeSH