CTNNB1 gene mutation associated with neurodevelopmental disorder, microcephaly, and persistence of bilateral hyperplastic primary vítreous: a case report and literature review.

Mutación del gen CTNNB1 asociada a alteración del neurodesarrollo, microcefalia y persistencia del vítreo primario hiperplásico bilateral: reporte de un caso y revisión de la literatura.
CTNNB1 gene Developmental disabilities Discapacidades del desarrollo Gen CTNNB1 Microcefalia Microcephaly Microftalmia Microphthalmia Persistence hyperplastic primary vítreous Persistent fetal vasculature Vasculatura fetal persistente Vítreo primario hiperplásico persistente

Journal

Archivos de la Sociedad Espanola de Oftalmologia
ISSN: 2173-5794
Titre abrégé: Arch Soc Esp Oftalmol (Engl Ed)
Pays: Spain
ID NLM: 101715860

Informations de publication

Date de publication:
06 Feb 2021
Historique:
received: 06 08 2020
revised: 24 11 2020
accepted: 25 11 2020
entrez: 10 2 2021
pubmed: 11 2 2021
medline: 11 2 2021
Statut: aheadofprint

Résumé

The most cases of persistence hyperplastic primary vítreous (PHPV) are unilateral and sporadic, however, bilateral presentation could be present in a small number of patients, in whom other genetic diseases must be ruled out. We describe a case of a 2 months child with bilateral persistence hyperplastic primary vítreous confirmed by ultrasound. In addition, with neurodevelopmental defects, microcephaly, facial dimorphism, axial hypotonia, and without brain abnormalities on MRI, in whom a de novo mutation of the CTNNB1 gene was found during the genetic study, which explains the findings.

Identifiants

pubmed: 33563475
pii: S0365-6691(21)00010-1
doi: 10.1016/j.oftal.2020.11.028
pii:
doi:

Types de publication

Case Reports

Langues

eng spa

Sous-ensembles de citation

IM

Informations de copyright

Copyright © 2021 Sociedad Española de Oftalmología. Publicado por Elsevier España, S.L.U. All rights reserved.

Auteurs

L M Zuluaga Gómez (LM)

Facultad de Medicina, Universidad de Antioquia , Medellín, Colombia.

S C Caballero Mojica (SC)

Facultad de Medicina, Universidad de Antioquia , Medellín, Colombia. Electronic address: silviaccm05@gmail.com.

G J Vélez Rengifo (GJ)

Centro especializado en Neurología y Psiquiatría Infantil (CENPI), Medellín, Colombia.

J D Bravo Acosta (JD)

Facultad de Medicina, Universidad de Antioquia , Medellín, Colombia.

J H Montoya Villada (JH)

Hospital universitario San Vicente Fundación, Medellín, Colombia.

Classifications MeSH