Prenatal mucopolysaccharidosis VII: A novel pathogenic variant identified in

Mucopolysaccharidosis VII Sly syndrome clinical exome sequencing glycosaminoglycans prenatal diagnosis β‐glucuronidase

Journal

Clinical case reports
ISSN: 2050-0904
Titre abrégé: Clin Case Rep
Pays: England
ID NLM: 101620385

Informations de publication

Date de publication:
Feb 2021
Historique:
received: 10 10 2020
revised: 17 11 2020
accepted: 25 11 2020
entrez: 18 2 2021
pubmed: 19 2 2021
medline: 19 2 2021
Statut: epublish

Résumé

Clinical exome sequencing is a powerful approach to overcome the wide clinical and genetic heterogeneity of mucopolysaccharidosis. These data could be useful for prenatal diagnosis of MPS VII, genetic counseling, and preimplantation genetic testing.

Identifiants

pubmed: 33598246
doi: 10.1002/ccr3.3644
pii: CCR33644
pmc: PMC7869334
doi:

Types de publication

Case Reports

Langues

eng

Pagination

790-795

Informations de copyright

© 2020 The Authors. Clinical Case Reports published by John Wiley & Sons Ltd.

Déclaration de conflit d'intérêts

There are no conflicts of interest to disclose. There is no funding or financial support to declare for this study. The manuscript complies with the ethical approval requirements. The data that support the findings of this study are available from the corresponding author upon reasonable request.

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Auteurs

Antonio Miguel Poyatos-Andújar (AM)

UGC de Laboratorios Laboratorio de Genética Hospital Universitario San Cecilio Granada Spain.

Susana García-Linares (S)

UGC de Laboratorios Laboratorio de Genética Hospital Universitario San Cecilio Granada Spain.

Pilar Carretero (P)

Department of Obstetrics and Gynecology Hospital Universitario San Cecilio Instituto de Investigación Biosanitaria IBS Granada Spain.

Olga Ocon (O)

Department of Obstetrics and Gynecology Hospital Universitario San Cecilio Instituto de Investigación Biosanitaria IBS Granada Spain.

Dolores Fresneda (D)

Department of Obstetrics and Gynecology Hospital Universitario San Cecilio Instituto de Investigación Biosanitaria IBS Granada Spain.

Laura Gort (L)

Secció d'Errors Congènits del Metabolisme -IBC Servei de Bioquímica i Genètica Molecular Hospital Clínic IDIBAPS, CIBERER Barcelona Spain.

Francisa Sonia Molina García (FS)

Department of Obstetrics and Gynecology Hospital Universitario San Cecilio Instituto de Investigación Biosanitaria IBS Granada Spain.

Classifications MeSH