Cerebrospinal fluid liquid biopsy for detecting somatic mosaicism in brain.

cell-free DNA cerebrospinal fluid focal epilepsy liquid biopsy somatic mutations

Journal

Brain communications
ISSN: 2632-1297
Titre abrégé: Brain Commun
Pays: England
ID NLM: 101755125

Informations de publication

Date de publication:
2021
Historique:
received: 16 11 2020
revised: 16 11 2020
accepted: 18 11 2020
entrez: 19 3 2021
pubmed: 20 3 2021
medline: 20 3 2021
Statut: epublish

Résumé

Brain somatic mutations are an increasingly recognized cause of epilepsy, brain malformations and autism spectrum disorders and may be a hidden cause of other neurodevelopmental and neurodegenerative disorders. At present, brain mosaicism can be detected only in the rare situations of autopsy or brain biopsy. Liquid biopsy using cell-free DNA derived from cerebrospinal fluid has detected somatic mutations in malignant brain tumours. Here, we asked if cerebrospinal fluid liquid biopsy can be used to detect somatic mosaicism in non-malignant brain diseases. First, we reliably quantified cerebrospinal fluid cell-free DNA in 28 patients with focal epilepsy and 28 controls using droplet digital PCR. Then, in three patients we identified somatic mutations in cerebrospinal fluid: in one patient with subcortical band heterotopia the

Identifiants

pubmed: 33738444
doi: 10.1093/braincomms/fcaa235
pii: fcaa235
pmc: PMC7954394
doi:

Types de publication

Journal Article

Langues

eng

Pagination

fcaa235

Commentaires et corrections

Type : ErratumIn

Informations de copyright

© The Author(s) (2021). Published by Oxford University Press on behalf of the Guarantors of Brain.

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Auteurs

Zimeng Ye (Z)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.

Zac Chatterton (Z)

Brain and Mind Centre, Sydney Medical School, The University of Sydney, Sydney, New South Wales 2050, Australia.

Jahnvi Pflueger (J)

Australian Research Council Centre of Excellence in Plant Energy Biology, School of Molecular Sciences, The University of Western Australia, Perth, Western Australia 6009, Australia.
Harry Perkins Institute of Medical Research, Perth, Western Australia 6150, Australia.

John A Damiano (JA)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.

Lara McQuillan (L)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.

Anthony Simon Harvey (AS)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.
Department of Neurology, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Stephen Malone (S)

Department of Neurosciences, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia.

Hongdo Do (H)

Department of Anatomical Pathology, St. Vincent's Hospital, Melbourne, Victoria 3065, Australia.
School of Cancer Medicine, La Trobe University, Melbourne, Victoria 3086, Australia.
Department of Clinical Pathology, University of Melbourne, Melbourne, Victoria 3010, Australia.

Wirginia Maixner (W)

Department of Neurosurgery, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Amy Schneider (A)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.

Bernadette Nolan (B)

Department of Neurosciences, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia.

Martin Wood (M)

Neurosurgical Department, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia.

Wei Shern Lee (WS)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Greta Gillies (G)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Kate Pope (K)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.

Michael Wilson (M)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Paul J Lockhart (PJ)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Alexander Dobrovic (A)

School of Cancer Medicine, La Trobe University, Melbourne, Victoria 3086, Australia.
Department of Clinical Pathology, University of Melbourne, Melbourne, Victoria 3010, Australia.
Translational Genomics and Epigenomics Laboratory, Olivia Newton-John Cancer Research Institute, Melbourne, Victoria 3084, Australia.

Ingrid E Scheffer (IE)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.
Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.
Department of Neurology, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Melanie Bahlo (M)

Population Health and Immunity Division, The Walter and Eliza Hall Institute of Medical Research, Melbourne, Victoria 3052, Australia.
Department of Medical Biology, University of Melbourne, Melbourne, Victoria 3010, Australia.

Richard J Leventer (RJ)

Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.
Department of Paediatrics, University of Melbourne, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.
Department of Neurology, Royal Children's Hospital, Melbourne, Victoria 3052, Australia.

Ryan Lister (R)

Australian Research Council Centre of Excellence in Plant Energy Biology, School of Molecular Sciences, The University of Western Australia, Perth, Western Australia 6009, Australia.
Harry Perkins Institute of Medical Research, Perth, Western Australia 6150, Australia.

Samuel F Berkovic (SF)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.

Michael S Hildebrand (MS)

Department of Medicine (Austin Health), University of Melbourne, Melbourne, Victoria 3084, Australia.
Murdoch Children's Research Institute, Melbourne, Victoria 3052, Australia.

Classifications MeSH