Expanding the β-III Spectrin-Associated Phenotypes toward Non-Progressive Congenital Ataxias with Neurodegeneration.


Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
02 Mar 2021
Historique:
received: 29 01 2021
revised: 19 02 2021
accepted: 25 02 2021
entrez: 3 4 2021
pubmed: 4 4 2021
medline: 13 5 2021
Statut: epublish

Résumé

(1) Background: A non-progressive congenital ataxia (NPCA) phenotype caused by β-III spectrin (

Identifiants

pubmed: 33801522
pii: ijms22052505
doi: 10.3390/ijms22052505
pmc: PMC7958857
pii:
doi:

Substances chimiques

SPTBN2 protein, human 0
Spectrin 12634-43-4

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Instituto de Salud Carlos III
ID : PI18/00147
Organisme : Conselleria de Cultura, Educación y Ciencia, Generalitat Valenciana
ID : PROMETEO/2018/135
Organisme : Ministerio de Educación, Cultura y Deporte
ID : FPU15/00964
Organisme : Spanish Foundation Per Amor a l'Art
ID : FPAA

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Auteurs

Paula Sancho (P)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.

Amparo Andrés-Bordería (A)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.
Department of Physiology, Faculty of Medicine and Dentistry, University of Valencia, 46010 Valencia, Spain.

Nerea Gorría-Redondo (N)

Pediatric Neurology Unit, Department of Pediatrics, Complejo Hospitalario de Navarra, 31008 Pamplona, Spain.

Katia Llano (K)

Clinical Psychology, Department of Psychiatry, Complejo Hospitalario de Navarra, 31008 Pamplona, Spain.

Dolores Martínez-Rubio (D)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.

María Eugenia Yoldi-Petri (ME)

Pediatric Neurology Unit, Department of Pediatrics, Complejo Hospitalario de Navarra, 31008 Pamplona, Spain.

Luba Blumkin (L)

Pediatric Neurology Unit, Wolfson Medical Center, Holon, Sackler School of Medicine, Tel-Aviv University, 69978 Tel-Aviv, Israel.

Pablo Rodríguez de la Fuente (P)

Pediatric Imaging Unit, Department of Radiology, Complejo Hospitalario de Navarra, 31008 Pamplona, Spain.

Fernando Gil-Ortiz (F)

CELLS-ALBA Synchrotron Light Source, 08290 Barcelona, Spain.

Leonor Fernández-Murga (L)

Molecular Oncology Laboratory, Hospital Arnau de Vilanova, 46015 Valencia, Spain.

Ana Sánchez-Monteagudo (A)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.

Vincenzo Lupo (V)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.

Belén Pérez-Dueñas (B)

Pediatric Neurology Research Group, Vall d'Hebron Research Institute (VHIR), Universitat Autònoma de Barcelona, 08035 Barcelona, Spain.

Carmen Espinós (C)

Unit of Rare Neurodegenerative Diseases, Centro de Investigación Príncipe Felipe (CIPF), 46012 Valencia, Spain.

Sergio Aguilera-Albesa (S)

Pediatric Neurology Unit, Department of Pediatrics, Complejo Hospitalario de Navarra, 31008 Pamplona, Spain.
Navarrabiomed-Fundación Miguel Servet, 31008 Pamplona, Spain.

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Classifications MeSH