Base editing strategy for insertion of the A673T mutation in the APP gene to prevent the development of AD
A673T
Alzheimer's disease
Base editing
CRISPR/Cas9
FAD
Islandic mutation
Journal
Molecular therapy. Nucleic acids
ISSN: 2162-2531
Titre abrégé: Mol Ther Nucleic Acids
Pays: United States
ID NLM: 101581621
Informations de publication
Date de publication:
04 Jun 2021
04 Jun 2021
Historique:
received:
03
09
2020
accepted:
24
02
2021
entrez:
5
4
2021
pubmed:
6
4
2021
medline:
6
4
2021
Statut:
epublish
Résumé
The amyloid precursor protein (
Identifiants
pubmed: 33815938
doi: 10.1016/j.omtn.2021.02.032
pii: S2162-2531(21)00067-6
pmc: PMC7985668
doi:
Types de publication
Journal Article
Langues
eng
Pagination
253-263Subventions
Organisme : NIA NIH HHS
ID : U24 AG021886
Pays : United States
Informations de copyright
© 2021 The Author(s).
Déclaration de conflit d'intérêts
The authors declare no competing interests.
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