Potent programmable antiviral against dengue virus in primary human cells by Cas13b RNP with short spacer and delivery by VLP.

CRISPR-Cas13 RNA virus VLP and virus-like particle delivery dengue flavivirus zika

Journal

Molecular therapy. Methods & clinical development
ISSN: 2329-0501
Titre abrégé: Mol Ther Methods Clin Dev
Pays: United States
ID NLM: 101624857

Informations de publication

Date de publication:
11 Jun 2021
Historique:
received: 25 03 2021
accepted: 22 04 2021
pubmed: 11 5 2021
medline: 11 5 2021
entrez: 10 5 2021
Statut: ppublish

Résumé

With sequencing as a standard frontline protocol to identify emerging viruses such Zika virus and severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2), direct utilization of sequence data to program antivirals against the viruses could accelerate drug development to treat their infections. CRISPR-Cas effectors are promising candidates that could be programmed to inactivate viral genetic material based on sequence data, but several challenges such as delivery and design of effective CRISPR RNA (crRNA) need to be addressed to realize practical use. Here, we showed that virus-like particle (VLP) could deliver PspCas13b-crRNA ribonucleoprotein (RNP) in nanomolar range to efficiently suppress dengue virus infection in primary human target cells. Shortening spacer length could significantly enhance RNA-targeting efficiency of PspCas13b in mammalian cells compared to the natural length of 30 nucleotides without compromising multiplex targeting by a crRNA array. Our results demonstrate the potentials of applying PspCas13b RNP to suppress RNA virus infection, with implications in targeting host RNA as well.

Identifiants

pubmed: 33969146
doi: 10.1016/j.omtm.2021.04.014
pii: S2329-0501(21)00080-2
pmc: PMC8087611
doi:

Types de publication

Journal Article

Langues

eng

Pagination

729-740

Informations de copyright

© 2021 The Author(s).

Déclaration de conflit d'intérêts

S.O., E.S., P.P., A.S., and B.S. are co-inventors on a patent application based on this work.

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Auteurs

Ekapot Singsuksawat (E)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Suppachoke Onnome (S)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Pratsaneeyaporn Posiri (P)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Amporn Suphatrakul (A)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Nittaya Srisuk (N)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Rapirat Nantachokchawapan (R)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Hansa Praneechit (H)

Division of Dengue Hemorrhagic Fever Research, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok 10700, Thailand.
Graduate Program in Immunology, Department of Immunology, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok 10700, Thailand.

Chutimon Sae-Kow (C)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Pala Chidpratum (P)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Khanit Sa-Ngiamsuntorn (K)

Department of Biochemistry, Faculty of Pharmacy, Mahidol University, Bangkok 10400, Thailand.

Suradej Hongeng (S)

Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok 10400, Thailand.

Panisadee Avirutnan (P)

Division of Dengue Hemorrhagic Fever Research, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok 10700, Thailand.
Siriraj Center of Research Excellence in Dengue and Emerging Pathogens, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok 10700, Thailand.

Thaneeya Duangchinda (T)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Bunpote Siridechadilok (B)

National Center for Genetic Engineering and Biotechnology, Klong Luang, Pathumthani 12120, Thailand.

Classifications MeSH