Immunoglobulin light chain amyloidosis diagnosis and treatment algorithm 2021.
Journal
Blood cancer journal
ISSN: 2044-5385
Titre abrégé: Blood Cancer J
Pays: United States
ID NLM: 101568469
Informations de publication
Date de publication:
15 05 2021
15 05 2021
Historique:
received:
30
01
2021
accepted:
28
04
2021
revised:
11
04
2021
entrez:
16
5
2021
pubmed:
17
5
2021
medline:
11
1
2022
Statut:
epublish
Résumé
Immunoglobulin light chain amyloidosis (AL) commonly presents with nephrotic range proteinuria, heart failure with preserved ejection fraction, nondiabetic peripheral neuropathy, unexplained hepatomegaly or diarrhea, and should be considered in patients presenting with these symptoms. More importantly, patients being monitored for smoldering multiple myeloma and a monoclonal gammopathy of undetermined significance (MGUS) are at risk for developing AL amyloidosis. MGUS and myeloma patients that have atypical features, including unexplained weight loss; lower extremity edema, early satiety, and dyspnea on exertion should be considered at risk for light chain amyloidosis. Overlooking the diagnosis of light chain amyloidosis leading to therapy delay is common, and it represents an error of diagnostic consideration. Herein we provide a review of established and investigational treatments for patients with AL amyloidosis and provide algorithms for workup and management of these patients.
Identifiants
pubmed: 33993188
doi: 10.1038/s41408-021-00483-7
pii: 10.1038/s41408-021-00483-7
pmc: PMC8124067
doi:
Substances chimiques
Amyloid
0
Antibodies, Monoclonal
0
Antineoplastic Agents
0
daratumumab
4Z63YK6E0E
Types de publication
Journal Article
Review
Langues
eng
Sous-ensembles de citation
IM
Pagination
90Subventions
Organisme : NCI NIH HHS
ID : P50 CA186781
Pays : United States
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