CERKL, a retinal dystrophy gene, regulates mitochondrial function and dynamics in the mammalian retina.


Journal

Neurobiology of disease
ISSN: 1095-953X
Titre abrégé: Neurobiol Dis
Pays: United States
ID NLM: 9500169

Informations de publication

Date de publication:
08 2021
Historique:
received: 17 03 2021
revised: 06 05 2021
accepted: 21 05 2021
pubmed: 29 5 2021
medline: 20 1 2022
entrez: 28 5 2021
Statut: ppublish

Résumé

The retina is a highly active metabolic organ that displays a particular vulnerability to genetic and environmental factors causing stress and homeostatic imbalance. Mitochondria constitute a bioenergetic hub that coordinates stress response and cellular homeostasis, therefore structural and functional regulation of the mitochondrial dynamic network is essential for the mammalian retina. CERKL (ceramide kinase like) is a retinal degeneration gene whose mutations cause Retinitis Pigmentosa in humans, a visual disorder characterized by photoreceptors neurodegeneration and progressive vision loss. CERKL produces multiple isoforms with a dynamic subcellular localization. Here we show that a pool of CERKL isoforms localizes at mitochondria in mouse retinal ganglion cells. The depletion of CERKL levels in Cerkl

Identifiants

pubmed: 34048907
pii: S0969-9961(21)00154-6
doi: 10.1016/j.nbd.2021.105405
pii:
doi:

Substances chimiques

Phosphotransferases (Alcohol Group Acceptor) EC 2.7.1.-
CerkL protein, mouse EC 2.7.1.138

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

105405

Informations de copyright

Copyright © 2021. Published by Elsevier Inc.

Auteurs

Serena Mirra (S)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain; Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Instituto de Salud Carlos III, Barcelona, Spain; Institut de Biomedicina de la Universitat de Barcelona- Institut de Recerca Hospital Sant Joan de Déu, IBUB-IRSJD, Barcelona, Spain. Electronic address: serena.mirra@ub.edu.

Rocío García-Arroyo (R)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain.

Elena B Domènech (E)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain; Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Instituto de Salud Carlos III, Barcelona, Spain.

Aleix Gavaldà-Navarro (A)

Institut de Biomedicina de la Universitat de Barcelona- Institut de Recerca Hospital Sant Joan de Déu, IBUB-IRSJD, Barcelona, Spain; Department of Biochemistry and Molecular Biomedicine, Barcelona, Spain; CIBEROBN, Instituto de Salud Carlos III, Spain.

Carlos Herrera-Úbeda (C)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain.

Clara Oliva (C)

Clinical Biochemistry Department, Hospital Sant Joan de Déu, Spain.

Jordi Garcia-Fernàndez (J)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain.

Rafael Artuch (R)

Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Instituto de Salud Carlos III, Barcelona, Spain; Clinical Biochemistry Department, Hospital Sant Joan de Déu, Spain.

Francesc Villarroya (F)

Institut de Biomedicina de la Universitat de Barcelona- Institut de Recerca Hospital Sant Joan de Déu, IBUB-IRSJD, Barcelona, Spain; Department of Biochemistry and Molecular Biomedicine, Barcelona, Spain; CIBEROBN, Instituto de Salud Carlos III, Spain.

Gemma Marfany (G)

Department of Genetics, Microbiology and Statistics and Institute of Biomedicine (IBUB), Faculty of Biology, University of Barcelona, Barcelona, Spain; Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Instituto de Salud Carlos III, Barcelona, Spain; Institut de Biomedicina de la Universitat de Barcelona- Institut de Recerca Hospital Sant Joan de Déu, IBUB-IRSJD, Barcelona, Spain. Electronic address: gmarfany@ub.edu.

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Classifications MeSH