Different Lipid Signature in Fibroblasts of Long-Chain Fatty Acid Oxidation Disorders.


Journal

Cells
ISSN: 2073-4409
Titre abrégé: Cells
Pays: Switzerland
ID NLM: 101600052

Informations de publication

Date de publication:
18 05 2021
Historique:
received: 13 04 2021
revised: 15 05 2021
accepted: 17 05 2021
entrez: 2 6 2021
pubmed: 3 6 2021
medline: 27 10 2021
Statut: epublish

Résumé

Long-chain fatty acid oxidation disorders (lc-FAOD) are a group of diseases affecting the degradation of long-chain fatty acids. In order to investigate the disease specific alterations of the cellular lipidome, we performed undirected lipidomics in fibroblasts from patients with carnitine palmitoyltransferase II, very long-chain acyl-CoA dehydrogenase, and long-chain 3-hydroxyacyl-CoA dehydrogenase. We demonstrate a deep remodeling of mitochondrial cardiolipins. The aberrant phosphatidylcholine/phosphatidylethanolamine ratio and the increased content of plasmalogens and of lysophospholipids support the theory of an inflammatory phenotype in lc-FAOD. Moreover, we describe increased ratios of sphingomyelin/ceramide and sphingomyelin/hexosylceramide in LCHAD deficiency which may contribute to the neuropathic phenotype of LCHADD/mitochondrial trifunctional protein deficiency.

Identifiants

pubmed: 34069977
pii: cells10051239
doi: 10.3390/cells10051239
pmc: PMC8157847
pii:
doi:

Substances chimiques

Cardiolipins 0
Ceramides 0
Fatty Acids 0
Sphingolipids 0
Long-Chain-3-Hydroxyacyl-CoA Dehydrogenase EC 1.1.1.211
Acyl-CoA Dehydrogenase, Long-Chain EC 1.3.8.8
Carnitine O-Palmitoyltransferase EC 2.3.1.21

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : NIDDK NIH HHS
ID : R01 DK078775
Pays : United States
Organisme : Ultragenix
ID : UX007-NCIST217
Organisme : Deutsche Forschungsgemeinschaft
ID : TU492/3-1

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Auteurs

Khaled I Alatibi (KI)

Department of General Pediatrics, Adolescent Medicine and Neonatology, Faculty of Medicine, Medical Centre-University of Freiburg, 79106 Freiburg, Germany.
Faculty of Biology, University of Freiburg, 79104 Freiburg, Germany.

Judith Hagenbuchner (J)

Department of Pediatrics II, Medical University Innsbruck, 6020 Innsbruck, Austria.

Zeinab Wehbe (Z)

Department of General Pediatrics, Adolescent Medicine and Neonatology, Faculty of Medicine, Medical Centre-University of Freiburg, 79106 Freiburg, Germany.
Department of Pediatric Hematology and Oncology, Faculty of Medicine, Center of Pediatric and Adolescent Medicine-Medical Center-University of Freiburg, 79106 Freiburg, Germany.

Daniela Karall (D)

Department of Pediatrics I, Medical University Innsbruck, 6020 Innsbruck, Austria.

Michael J Ausserlechner (MJ)

Department of Pediatrics I, Medical University Innsbruck, 6020 Innsbruck, Austria.

Jerry Vockley (J)

School of Medicine, University of Pittsburgh, Pittsburgh, PA 15260, USA.
Center for Rare Disease Therapy, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA 15224, USA.
Graduate School of Public Health, University of Pittsburgh, Pittsburgh, PA 15260, USA.

Ute Spiekerkoetter (U)

Department of General Pediatrics, Adolescent Medicine and Neonatology, Faculty of Medicine, Medical Centre-University of Freiburg, 79106 Freiburg, Germany.

Sarah C Grünert (SC)

Department of General Pediatrics, Adolescent Medicine and Neonatology, Faculty of Medicine, Medical Centre-University of Freiburg, 79106 Freiburg, Germany.

Sara Tucci (S)

Department of General Pediatrics, Adolescent Medicine and Neonatology, Faculty of Medicine, Medical Centre-University of Freiburg, 79106 Freiburg, Germany.

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Classifications MeSH