Health-related quality of life in patients with newly diagnosed multiple myeloma ineligible for stem cell transplantation: results from the randomized phase III ALCYONE trial.


Journal

BMC cancer
ISSN: 1471-2407
Titre abrégé: BMC Cancer
Pays: England
ID NLM: 100967800

Informations de publication

Date de publication:
02 Jun 2021
Historique:
received: 29 09 2020
accepted: 09 05 2021
entrez: 3 6 2021
pubmed: 4 6 2021
medline: 21 10 2021
Statut: epublish

Résumé

In the phase III ALCYONE trial, daratumumab plus bortezomib/melphalan/prednisone (D-VMP) significantly improved overall response rate and progression-free status compared with VMP alone in transplant-ineligible patients with newly diagnosed multiple myeloma (NDMM). Here, we present patient-reported outcomes (PROs) from ALCYONE. The European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30-item (EORTC QLQ-C30) and EuroQol 5-dimensional descriptive system (EQ-5D-5L) questionnaire were administered at baseline, every 3 months (year 1) and every 6 months (until progression). Treatment effects were assessed using a repeated-measures, mixed-effects model. Compliance with PRO assessments was comparable at baseline (> 90%) and throughout study (> 76%) for both treatment groups. Improvements from baseline were observed in both groups for EORTC QLQ-C30 Global Health Status (GHS), most functional scales, symptom scales and EQ-5D-5L visual analog scale (VAS). Between-group differences were significant for GHS (p = 0.0240) and VAS (p = 0.0160) at month 3. Improvements in pain were clinically meaningful in both groups at all assessment time points. Cognitive function declined in both groups, but the magnitude of the decline was not clinically meaningful. Patients with transplant-ineligible NDMM demonstrated early and continuous improvements in health-related quality of life, including improvements in functioning and symptoms, following treatment with D-VMP or VMP. ClinicalTrials.gov identifier NCT02195479 , registered September 21, 2014.

Sections du résumé

BACKGROUND BACKGROUND
In the phase III ALCYONE trial, daratumumab plus bortezomib/melphalan/prednisone (D-VMP) significantly improved overall response rate and progression-free status compared with VMP alone in transplant-ineligible patients with newly diagnosed multiple myeloma (NDMM). Here, we present patient-reported outcomes (PROs) from ALCYONE.
METHODS METHODS
The European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30-item (EORTC QLQ-C30) and EuroQol 5-dimensional descriptive system (EQ-5D-5L) questionnaire were administered at baseline, every 3 months (year 1) and every 6 months (until progression). Treatment effects were assessed using a repeated-measures, mixed-effects model.
RESULTS RESULTS
Compliance with PRO assessments was comparable at baseline (> 90%) and throughout study (> 76%) for both treatment groups. Improvements from baseline were observed in both groups for EORTC QLQ-C30 Global Health Status (GHS), most functional scales, symptom scales and EQ-5D-5L visual analog scale (VAS). Between-group differences were significant for GHS (p = 0.0240) and VAS (p = 0.0160) at month 3. Improvements in pain were clinically meaningful in both groups at all assessment time points. Cognitive function declined in both groups, but the magnitude of the decline was not clinically meaningful.
CONCLUSIONS CONCLUSIONS
Patients with transplant-ineligible NDMM demonstrated early and continuous improvements in health-related quality of life, including improvements in functioning and symptoms, following treatment with D-VMP or VMP.
TRIAL REGISTRATION BACKGROUND
ClinicalTrials.gov identifier NCT02195479 , registered September 21, 2014.

Identifiants

pubmed: 34078314
doi: 10.1186/s12885-021-08325-2
pii: 10.1186/s12885-021-08325-2
pmc: PMC8170980
doi:

Substances chimiques

Antibodies, Monoclonal 0
daratumumab 4Z63YK6E0E
Bortezomib 69G8BD63PP
Melphalan Q41OR9510P
Prednisone VB0R961HZT

Banques de données

ClinicalTrials.gov
['NCT02195479']

Types de publication

Clinical Trial, Phase III Journal Article Multicenter Study Randomized Controlled Trial

Langues

eng

Sous-ensembles de citation

IM

Pagination

659

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Auteurs

Stefan Knop (S)

Department of Haematology and Oncology, Würzburg University Medical Center, Oberdürrbacher Straße 6, 97080, Würzburg, Germany. knop_s@ukw.de.

Maria-Victoria Mateos (MV)

University Hospital of Salamanca-Instituto de Investigación Biomédica de Salamanca, Salamanca, Spain.

Meletios A Dimopoulos (MA)

National and Kapodistrian University of Athens, Athens, Greece.

Kenshi Suzuki (K)

Japanese Red Cross Medical Center, Tokyo, Japan.

Andrzej Jakubowiak (A)

University of Chicago Medical Center, Chicago, IL, USA.

Chantal Doyen (C)

Université Catholique of Louvain, CHU UCL Namur, Yvoir, Belgium.

Paulo Lucio (P)

Champalimaud Centre for the Unknown, Lisbon, Portugal.

Zsolt Nagy (Z)

Semmelweis University, Budapest, Hungary.

Ganna Usenko (G)

Dnipropetrovsk City Multidisciplinary Clinical Hospital No. 4, Dnipropetrovsk, Ukraine.

Ludek Pour (L)

University Hospital Brno, Brno, Czech Republic.

Mark Cook (M)

University Hospitals Birmingham NHS Trust, Birmingham, UK.

Sebastian Grosicki (S)

Silesian Medical University, Katowice, Poland.

Andre Crepaldi (A)

Clinica de Tratamento E, Cuiaba, Brazil.

Anna Marina Liberati (AM)

Azienda Ospedaliera "Santa Maria", Terni, Italy.

Philip Campbell (P)

Andrew Love Cancer Centre, Geelong, Australia.

Tatiana Shelekhova (T)

Clinic of Professional Pathology, Saratov, Russia.

Sung-Soo Yoon (SS)

Department of Internal Medicine, Seoul National University College of Medicine, Seoul, Republic of Korea.

Genadi Losava (G)

LTD "Medinvent" Institute of Health, Tbilisi, Georgia.

Tomoaki Fujisaki (T)

Matsuyama Red Cross Hospital, Matsuyama, Japan.

Mamta Garg (M)

Leicester Royal Infirmary, Leicester, UK.

Jianping Wang (J)

Janssen Research and Development, Raritan, NJ, USA.

Susan Wroblewski (S)

Janssen Research & Development, LLC, Spring House, PA, USA.

Anupa Kudva (A)

Janssen Research and Development, Raritan, NJ, USA.

Katharine S Gries (KS)

Janssen Research and Development, Raritan, NJ, USA.

John Fastenau (J)

Janssen Research and Development, Raritan, NJ, USA.

Jesus San-Miguel (J)

Clínica Universidad de Navarra-Centro de Investigación Médica Aplicada, Instituto de Investigación Sanitaria de Navarra, Centro de Investigación Biomédica en Red de Cáncer, Pamplona, Spain.

Michele Cavo (M)

Institute of Hematology, Department of Experimental, Diagnostic and Specialty Medicine, University of Bologna, Bologna, Italy.

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Classifications MeSH