Structural analysis of the full-length human LRRK2.


Journal

Cell
ISSN: 1097-4172
Titre abrégé: Cell
Pays: United States
ID NLM: 0413066

Informations de publication

Date de publication:
24 06 2021
Historique:
received: 05 01 2021
revised: 23 03 2021
accepted: 04 05 2021
pubmed: 10 6 2021
medline: 6 1 2022
entrez: 9 6 2021
Statut: ppublish

Résumé

Mutations in leucine-rich repeat kinase 2 (LRRK2) are commonly implicated in the pathogenesis of both familial and sporadic Parkinson's disease (PD). LRRK2 regulates critical cellular processes at membranous organelles and forms microtubule-based pathogenic filaments, yet the molecular basis underlying these biological roles of LRRK2 remains largely enigmatic. Here, we determined high-resolution structures of full-length human LRRK2, revealing its architecture and key interdomain scaffolding elements for rationalizing disease-causing mutations. The kinase domain of LRRK2 is captured in an inactive state, a conformation also adopted by the most common PD-associated mutation, LRRK2

Identifiants

pubmed: 34107286
pii: S0092-8674(21)00601-2
doi: 10.1016/j.cell.2021.05.004
pmc: PMC8887629
mid: NIHMS1775752
pii:
doi:

Substances chimiques

LRRK2 protein, human EC 2.7.11.1
Leucine-Rich Repeat Serine-Threonine Protein Kinase-2 EC 2.7.11.1

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

3519-3527.e10

Subventions

Organisme : NHLBI NIH HHS
ID : K99 HL143037
Pays : United States
Organisme : NINDS NIH HHS
ID : P30 NS055077
Pays : United States
Organisme : NHLBI NIH HHS
ID : R00 HL143037
Pays : United States
Organisme : NIA NIH HHS
ID : R01 AG053987
Pays : United States

Informations de copyright

Copyright © 2021 Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of interests The authors declare no competing interests.

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Auteurs

Alexander Myasnikov (A)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA; Cryo-EM and Tomography Center, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Hanwen Zhu (H)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Patricia Hixson (P)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Boer Xie (B)

Center for Proteomics and Metabolomics, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Kaiwen Yu (K)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA; Department of Developmental Neurobiology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Aaron Pitre (A)

Cell & Tissue Imaging Center, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Junmin Peng (J)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA; Center for Proteomics and Metabolomics, St. Jude Children's Research Hospital, Memphis, TN 38105, USA; Department of Developmental Neurobiology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA.

Ji Sun (J)

Department of Structural Biology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA. Electronic address: ji.sun@stjude.org.

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