Long-term effect of apomorphine infusion in advanced Parkinson's disease: a real-life study.


Journal

NPJ Parkinson's disease
ISSN: 2373-8057
Titre abrégé: NPJ Parkinsons Dis
Pays: United States
ID NLM: 101675390

Informations de publication

Date de publication:
11 Jun 2021
Historique:
received: 09 11 2020
accepted: 09 04 2021
entrez: 12 6 2021
pubmed: 13 6 2021
medline: 13 6 2021
Statut: epublish

Résumé

Long-term effects of continuous subcutaneous apomorphine infusion (CSAI) on health-related quality of life (HRQoL) and predictors of CSAI discontinuation are poorly known. Data from consecutive advanced Parkinson's disease patients treated in routine care were retrospectively collected over 24 months after CSAI initiation, with a focus on the 39-item Parkinson's disease questionnaire (PDQ-39). We determined predictors of CSAI discontinuation and HRQoL improvement using multiple regression analysis. Of the 110 subjects evaluated over a 2-year period, 35% discontinued CSAI. Of those who continued treatment, HRQoL remained stable with a sustained reduction in motor fluctuations. The observed effect on dyskinesias was mild and transient. Of note, patients with preexisting impulse control disorders showed an overall good tolerability. PDQ-39 was the only baseline predictor of HRQoL improvement after 2 years of treatment. The presence of dyskinesias, poorer psychological status, shorter disease duration, male sex, and worse OFF state were predictors of discontinuation. Best candidates for CSAI are patients with: (i) poor baseline HRQoL and (ii) marked motor fluctuations.

Identifiants

pubmed: 34117268
doi: 10.1038/s41531-021-00194-7
pii: 10.1038/s41531-021-00194-7
pmc: PMC8196159
doi:

Types de publication

Journal Article

Langues

eng

Pagination

50

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Auteurs

Bruna Meira (B)

Neurology Department, Centro Hospitalar Lisboa Ocidental, Lisbon, Portugal.

Bertrand Degos (B)

Neurology Department, Avicenne Hospital, AP-HP, Sorbonne Paris Nord University, Bobigny, France.

Elise Corsetti (E)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.

Mohamed Doulazmi (M)

Adaptation Biologique et Vieillissement, Institut de Biologie Paris Seine, Sorbonne University, CNRS, Paris, France.

Emeline Berthelot (E)

Neurology Department, Hôpital Zobda Quitman, Fort-de-France, French West Indies, France.

Clara Virbel-Fleischman (C)

Air Liquide SA, Explor Center (Healthcare), Fort-de-France, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Pauline Dodet (P)

Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.
Sleep Disorders (Department "R3S"), Pitié-Salpêtrière Hospital, Paris, France.

Aurélie Méneret (A)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Louise-Laure Mariani (LL)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Cécile Delorme (C)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Florence Cormier-Dequaire (F)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

David Bendetowicz (D)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Nicolas Villain (N)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.
Sorbonne Université, GRC no 21, Alzheimer Precision Medicine, Paris, France.

Clément Tarrano (C)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Lise Mantisi (L)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.

Hélène Letrillart (H)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.

Céline Louapre (C)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Eavan McGovern (E)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.

Yulia Worbe (Y)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Neurophysiology Department, Saint Antoine Hospital, AP-HP, Paris, France.

David Grabli (D)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Marie Vidailhet (M)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Elodie Hainque (E)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France.

Emmanuel Roze (E)

Neurology Department, Pitié-Salpêtrière Hospital, AP-HP, Paris, France. emmanuel.flamand-roze@aphp.fr.
Paris Brain Institute, Sorbonne University, UMR S 1127, Inserm U 1127, CNRS UMR 7225, Paris, France. emmanuel.flamand-roze@aphp.fr.

Classifications MeSH