Adverse events as potential predictive factors of activity in patients with advanced hepatocellular carcinoma treated with lenvatinib.


Journal

Liver international : official journal of the International Association for the Study of the Liver
ISSN: 1478-3231
Titre abrégé: Liver Int
Pays: United States
ID NLM: 101160857

Informations de publication

Date de publication:
12 2021
Historique:
revised: 02 07 2021
received: 25 05 2021
accepted: 08 07 2021
pubmed: 13 7 2021
medline: 4 3 2022
entrez: 12 7 2021
Statut: ppublish

Résumé

Lenvatinib is a standard of care option in first-line therapy of advanced hepatocellular carcinoma (HCC). In the present study, we aim to identify, in patients with HCC treated with lenvatinib, a possible association between occurrence and grading of adverse events (AEs) and outcome. We performed a retrospective analysis of 606 Japanese and Italian patients treated with lenvatinib in first-line setting and investigated the possible correlation between the onset of AEs, toxicity grade (G) and outcome measures such as overall survival (OS) and progression-free survival (PFS). The appearance of arterial hypertension G ≥ 2 independently predicted prolonged OS [hazard ratio (HR) 0.66, 95% confidence interval (CI) 0.46-0.93, P = .0188], whereas decreased appetite G ≥ 2 independently predicted decreased OS (HR 1.70, 95% CI 1.25-2.32, P = .0007) by multivariate analysis. Appearance of hand-foot skin reaction independently predicted prolonged PFS (HR 0.72, 95% CI 0.56-0.93, P = .0149), whereas decreased appetite G ≥ 2 predicted decreased PFS (HR 1.36, 95% CI 1.04-1.77, P = .0277). Our main findings are that the occurrence of arterial hypertension G ≥ 2 is a predictor of longer survival, whereas decreased appetite G ≥ 2 predicts for a poor prognosis. A careful management of AEs under lenvatinib treatment for HCC is required, to improve patients' quality of life, minimize the need for treatment discontinuation and achieve optimal outcome.

Sections du résumé

BACKGROUND AND AIM
Lenvatinib is a standard of care option in first-line therapy of advanced hepatocellular carcinoma (HCC). In the present study, we aim to identify, in patients with HCC treated with lenvatinib, a possible association between occurrence and grading of adverse events (AEs) and outcome.
METHODS
We performed a retrospective analysis of 606 Japanese and Italian patients treated with lenvatinib in first-line setting and investigated the possible correlation between the onset of AEs, toxicity grade (G) and outcome measures such as overall survival (OS) and progression-free survival (PFS).
RESULTS
The appearance of arterial hypertension G ≥ 2 independently predicted prolonged OS [hazard ratio (HR) 0.66, 95% confidence interval (CI) 0.46-0.93, P = .0188], whereas decreased appetite G ≥ 2 independently predicted decreased OS (HR 1.70, 95% CI 1.25-2.32, P = .0007) by multivariate analysis. Appearance of hand-foot skin reaction independently predicted prolonged PFS (HR 0.72, 95% CI 0.56-0.93, P = .0149), whereas decreased appetite G ≥ 2 predicted decreased PFS (HR 1.36, 95% CI 1.04-1.77, P = .0277).
CONCLUSIONS
Our main findings are that the occurrence of arterial hypertension G ≥ 2 is a predictor of longer survival, whereas decreased appetite G ≥ 2 predicts for a poor prognosis. A careful management of AEs under lenvatinib treatment for HCC is required, to improve patients' quality of life, minimize the need for treatment discontinuation and achieve optimal outcome.

Identifiants

pubmed: 34250737
doi: 10.1111/liv.15014
doi:

Substances chimiques

Phenylurea Compounds 0
Quinolines 0
lenvatinib EE083865G2

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

2997-3008

Informations de copyright

© 2021 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.

Références

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Auteurs

Ilario Giovanni Rapposelli (IG)

Department of Medical Oncology, IRCCS Istituto Romagnolo per lo Studio dei Tumori "Dino Amadori"-IRST, Meldola, Italy.

Toshifumi Tada (T)

Department of Internal Medicine, Japanese Red Cross Himeji Hospital, Himeji, Japan.

Shigeo Shimose (S)

Division of Gastroenterology, Department of Medicine, Kurume University School of Medicine, Kurume, Fukuoka, Japan.

Valentina Burgio (V)

Department of Medical Oncology, San Raffaele Scientific Institute IRCCS, Milan, Italy.

Takashi Kumada (T)

Faculty of Nursing, Gifu Kyoritsu University, Ogaki, Japan.

Hideki Iwamoto (H)

Division of Gastroenterology, Department of Medicine, Kurume University School of Medicine, Kurume, Fukuoka, Japan.

Atsushi Hiraoka (A)

Gastroenterology Center, Ehime Prefectural Central Hospital, Matsuyama, Japan.

Takashi Niizeki (T)

Division of Gastroenterology, Department of Medicine, Kurume University School of Medicine, Kurume, Fukuoka, Japan.

Masanori Atsukawa (M)

Division of Gastroenterology and Hepatology, Department of Internal Medicine, Nippon Medical School, Tokyo, Japan.

Hironori Koga (H)

Division of Gastroenterology, Department of Medicine, Kurume University School of Medicine, Kurume, Fukuoka, Japan.

Masashi Hirooka (M)

Department of Gastroenterology and Metabology, Ehime University Graduate School of Medicine, Matsuyama, Japan.

Takuji Torimura (T)

Division of Gastroenterology, Department of Medicine, Kurume University School of Medicine, Kurume, Fukuoka, Japan.

Massimo Iavarone (M)

Division of Gastroenterology and Hepatology, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, Milan, Italy.

Raffaella Tortora (R)

Liver Unit, Cardarelli Hospital, Naples, Italy.

Claudia Campani (C)

Department of Experimental and Clinical Biomedical Sciences "Mario Serio", University of Florence, Florence, Italy.

Sara Lonardi (S)

Early Phase Clinical Trial Unit, Department of Oncology, Veneto Institute of Oncology IOV-IRCCS, Padua, Italy.
Medical Oncology Unit 1, Department of Oncology, Veneto Institute of Oncology IOV-IRCCS, Padua, Italy.

Emiliano Tamburini (E)

Department of Medical Oncology, Card. G. Panico Hospital of Tricase, Tricase, Italy.

Fabio Piscaglia (F)

Division of Internal Medicine, Hepatobiliary and Immunoallergic Diseases, Azienda Ospedaliero Universitaria di Bologna, Italy.

Gianluca Masi (G)

Azienda Ospedaliero-Universitaria Pisana, Pisa, Italy.

Giuseppe Cabibbo (G)

Department of Health Promotion, Mother & Child Care, Internal Medicine & Medical Specialties, PROMISE, Gastroenterology & Hepatology Unit, University of Palermo, Palermo, Italy.

Francesco Giuseppe Foschi (F)

Department of Internal Medicine, Faenza Hospital, AUSL Romagna, Faenza, Italy.

Marianna Silletta (M)

Medical Oncology Unit, University Campus Bio-Medico, Rome, Italy.

Kunihiko Tsuji (K)

Center of Gastroenterology, Teine Keijinkai Hospital, Sapporo, Japan.

Toru Ishikawa (T)

Department of Gastroenterology, Saiseikai Niigata Hospital, Niigata, Japan.

Koichi Takaguchi (K)

Department of Hepatology, Kagawa Prefectural Central Hospital, Takamatsu, Japan.

Kazuya Kariyama (K)

Department of Gastroenterology, Okayama City Hospital, Okayama, Japan.

Ei Itobayashi (E)

Department of Gastroenterology, Asahi General Hospital, Asahi, Japan.

Kazuto Tajiri (K)

Department of Gastroenterology, Toyama University Hospital, Toyama, Japan.

Noritomo Shimada (N)

Division of Gastroenterology and Hepatology, Otakanomori Hospital, Kashiwa, Japan.

Hiroshi Shibata (H)

Department of Gastroenterology, Tokushima Prefectural Central Hospital, Tokushima, Japan.

Hironori Ochi (H)

Hepato-biliary Center, Matsuyama Red Cross Hospital, Matsuyama, Japan.

Satoshi Yasuda (S)

Department of Gastroenterology and Hepatology, Ogaki Municipal Hospital, Ogaki, Japan.

Hidenori Toyoda (H)

Department of Gastroenterology and Hepatology, Ogaki Municipal Hospital, Ogaki, Japan.

Shinya Fukunishi (S)

Second Department of Internal Medicine, Osaka Medical College, Takatsuki, Japan.

Hideko Ohama (H)

Second Department of Internal Medicine, Osaka Medical College, Takatsuki, Japan.

Kazuhito Kawata (K)

Hepatology Division, Department of Internal Medicine, Hamamatsu University School of Medicine, Hamamatsu, Japan.

Joji Tani (J)

Department of Gastroenterology and Neurology, Kagawa University School of Medicine, Kagawa, Japan.

Shinichiro Nakamura (S)

Department of Internal Medicine, Japanese Red Cross Himeji Hospital, Himeji, Japan.

Kazuhiro Nouso (K)

Department of Gastroenterology, Okayama City Hospital, Okayama, Japan.

Akemi Tsutsui (A)

Department of Hepatology, Kagawa Prefectural Central Hospital, Takamatsu, Japan.

Takuya Nagano (T)

Department of Hepatology, Kagawa Prefectural Central Hospital, Takamatsu, Japan.

Takaaki Tanaka (T)

Gastroenterology Center, Ehime Prefectural Central Hospital, Matsuyama, Japan.

Norio Itokawa (N)

Division of Gastroenterology and Hepatology, Department of Internal Medicine, Nippon Medical School, Tokyo, Japan.

Tomomi Okubo (T)

Division of Gastroenterology and Hepatology, Department of Internal Medicine, Nippon Medical School, Tokyo, Japan.

Taeang Arai (T)

Division of Gastroenterology and Hepatology, Department of Internal Medicine, Nippon Medical School, Tokyo, Japan.

Michitaka Imai (M)

Department of Gastroenterology, Saiseikai Niigata Hospital, Niigata, Japan.

Kouji Joko (K)

Hepato-biliary Center, Matsuyama Red Cross Hospital, Matsuyama, Japan.

Yohei Koizumi (Y)

Department of Gastroenterology and Metabology, Ehime University Graduate School of Medicine, Matsuyama, Japan.

Yoichi Hiasa (Y)

Department of Gastroenterology and Metabology, Ehime University Graduate School of Medicine, Matsuyama, Japan.

Margherita Rimini (M)

Division of Oncology, Department of Oncology and Hematology, University Hospital of Modena, Modena, Italy.

Francesca Ratti (F)

Hepatobiliary Surgery Division, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Luca Aldrighetti (L)

Hepatobiliary Surgery Division, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Stefano Cascinu (S)

Department of Medical Oncology, San Raffaele Scientific Institute IRCCS, Milan, Italy.
Vita-Salute San Raffaele University, Milan, Italy.

Andrea Casadei-Gardini (A)

Department of Medical Oncology, San Raffaele Scientific Institute IRCCS, Milan, Italy.
Vita-Salute San Raffaele University, Milan, Italy.

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