Human d-lactate dehydrogenase deficiency by

LDHD ataxia complex IV deficiency developmental delay d‐lactate dehydrogenase neurological

Journal

JIMD reports
ISSN: 2192-8304
Titre abrégé: JIMD Rep
Pays: United States
ID NLM: 101568557

Informations de publication

Date de publication:
Jul 2021
Historique:
received: 15 01 2021
revised: 18 03 2021
accepted: 06 04 2021
entrez: 14 7 2021
pubmed: 15 7 2021
medline: 15 7 2021
Statut: epublish

Résumé

d-lactate, one of the isomers of lactate, exists in a low concentration in healthy individuals and it can be oxidized to pyruvate catalyzed by d-lactate dehydrogenase. Excessive amount of d-lactate causes d-lactate acidosis associated with neurological manifestations. We report here a patient with developmental delay, cerebellar ataxia, and transient hepatomegaly. Enzyme analysis in the patient's skin fibroblast showed decreased mitochondrial complex IV activity. Using whole exome sequencing, we identified compound heterozygous variants in the This is the third report on

Sections du résumé

BACKGROUND BACKGROUND
d-lactate, one of the isomers of lactate, exists in a low concentration in healthy individuals and it can be oxidized to pyruvate catalyzed by d-lactate dehydrogenase. Excessive amount of d-lactate causes d-lactate acidosis associated with neurological manifestations.
METHODS AND RESULTS RESULTS
We report here a patient with developmental delay, cerebellar ataxia, and transient hepatomegaly. Enzyme analysis in the patient's skin fibroblast showed decreased mitochondrial complex IV activity. Using whole exome sequencing, we identified compound heterozygous variants in the
CONCLUSION CONCLUSIONS
This is the third report on

Identifiants

pubmed: 34258137
doi: 10.1002/jmd2.12220
pii: JMD212220
pmc: PMC8260477
doi:

Types de publication

Case Reports

Langues

eng

Pagination

15-22

Informations de copyright

© 2021 The Authors. JIMD Reports published by John Wiley & Sons Ltd on behalf of SSIEM.

Déclaration de conflit d'intérêts

J. S. is the CEO of Khondrion, a pharmaceutical company developing compounds to potentially treat mitochondrial disease. All the other authors declare that they have no conflict of interest.

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Auteurs

Anna Ka-Yee Kwong (AK)

Department of Paediatrics and Adolescent Medicine, Li Ka Shing Faculty of Medicine The University of Hong Kong Hong Kong SAR China.

Sheila Suet-Na Wong (SS)

Department of Paediatrics and Adolescent Medicine, Li Ka Shing Faculty of Medicine The University of Hong Kong Hong Kong SAR China.
Department of Paediatrics and Adolescent Medicine Hong Kong Children's Hospital Hong Kong SAR China.

Richard J T Rodenburg (RJT)

Radboud Centre for Mitochondrial Medicine, Department of Paediatrics Radboud Institute for Molecular Life Sciences, Radboud University Nijmegen Medical Centre Nijmegen The Netherlands.

Jan Smeitink (J)

Radboud Centre for Mitochondrial Medicine, Department of Paediatrics Radboud Institute for Molecular Life Sciences, Radboud University Nijmegen Medical Centre Nijmegen The Netherlands.

Godfrey Chi Fung Chan (GCF)

Department of Paediatrics and Adolescent Medicine, Li Ka Shing Faculty of Medicine The University of Hong Kong Hong Kong SAR China.
Department of Paediatrics and Adolescent Medicine Hong Kong Children's Hospital Hong Kong SAR China.

Cheuk-Wing Fung (CW)

Department of Paediatrics and Adolescent Medicine, Li Ka Shing Faculty of Medicine The University of Hong Kong Hong Kong SAR China.
Department of Paediatrics and Adolescent Medicine Hong Kong Children's Hospital Hong Kong SAR China.

Classifications MeSH