A Novel

DYNC1H1 Exome sequencing SMALED1 Spinal muscular atrophy with lower extremity predominance type 1

Journal

Child neurology open
ISSN: 2329-048X
Titre abrégé: Child Neurol Open
Pays: United States
ID NLM: 101691975

Informations de publication

Date de publication:
Historique:
received: 13 05 2021
accepted: 05 06 2021
entrez: 9 8 2021
pubmed: 10 8 2021
medline: 10 8 2021
Statut: epublish

Résumé

Mutations in

Identifiants

pubmed: 34368388
doi: 10.1177/2329048X211027438
pii: 10.1177_2329048X211027438
pmc: PMC8312150
doi:

Types de publication

Case Reports

Langues

eng

Pagination

2329048X211027438

Informations de copyright

© The Author(s) 2021.

Déclaration de conflit d'intérêts

Declaration of Conflicting Interests: The author(s) declared no potential conflicts of interest with respect to the research, authorship, and/or publication of this article.

Références

Neuromuscul Disord. 2018 Sep;28(9):750-756
pubmed: 30122514
Neuromuscul Disord. 2017 Jul;27(7):607-615
pubmed: 28554554
Genet Med. 2015 May;17(5):405-24
pubmed: 25741868
J Neurol. 2015 Sep;262(9):2124-34
pubmed: 26100331
Sci Rep. 2017 Mar 21;7(1):258
pubmed: 28325891
Eur J Med Genet. 2020 Dec;63(12):104063
pubmed: 32947049
Mol Genet Genomic Med. 2016 May 10;4(5):504-12
pubmed: 27652278
Nat Genet. 2013 Jun;45(6):639-47
pubmed: 23603762
Neurogenetics. 2012 Nov;13(4):327-32
pubmed: 22847149
Proc Natl Acad Sci U S A. 2017 Feb 28;114(9):E1597-E1606
pubmed: 28196890

Auteurs

Alexa Derksen (A)

Child Health and Human Development Program, Research Institute of the McGill University Health Centre, Montréal, Canada.
Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.

Amytice Mirchi (A)

Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.
Department of Pediatrics, McGill University, Montréal, Canada.

Luan T Tran (LT)

Child Health and Human Development Program, Research Institute of the McGill University Health Centre, Montréal, Canada.
Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.

Lei Cao-Lei (L)

Child Health and Human Development Program, Research Institute of the McGill University Health Centre, Montréal, Canada.
Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.

Maryam Oskoui (M)

Child Health and Human Development Program, Research Institute of the McGill University Health Centre, Montréal, Canada.
Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.
Department of Pediatrics, McGill University, Montréal, Canada.

Myriam Srour (M)

Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.
Department of Pediatrics, McGill University, Montréal, Canada.

Chantal Poulin (C)

Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.
Department of Pediatrics, McGill University, Montréal, Canada.

Geneviève Bernard (G)

Child Health and Human Development Program, Research Institute of the McGill University Health Centre, Montréal, Canada.
Department of Neurology and Neurosurgery, McGill University, Montréal, Canada.
Department of Pediatrics, McGill University, Montréal, Canada.
Department of Human Genetics, McGill University, Montréal, Canada.
Division of Medical Genetics, Department of Specialized Medicine, McGill University Health Centre, Montréal, Canada.

Classifications MeSH