Clinical outcome assessments in Duchenne muscular dystrophy and spinal muscular atrophy: past, present and future.
Duchenne muscular dystrophy
clinical outcome assessment
functional outcome
motor development
motor performance
spinal muscular atrophy
Journal
Neuromuscular disorders : NMD
ISSN: 1873-2364
Titre abrégé: Neuromuscul Disord
Pays: England
ID NLM: 9111470
Informations de publication
Date de publication:
10 2021
10 2021
Historique:
received:
30
06
2021
revised:
12
07
2021
accepted:
16
07
2021
pubmed:
21
8
2021
medline:
3
2
2022
entrez:
20
8
2021
Statut:
ppublish
Résumé
Scores and scales used in pediatric motor development for neuromuscular disorders have evolved greatly since the beginning of their development. In this review we provide a brief history of scales used in pediatric patients with neuromuscular disorders and an update regarding the advancement of the scales commonly used in patients with spinal muscular atrophy and Duchenne muscular dystrophy. We focus on the collaborative effort that has led to the development of outcomes and speak to the possible future of Clinical Outcome Assessments.
Identifiants
pubmed: 34412961
pii: S0960-8966(21)00202-9
doi: 10.1016/j.nmd.2021.07.015
pii:
doi:
Types de publication
Journal Article
Review
Langues
eng
Sous-ensembles de citation
IM
Pagination
1028-1037Informations de copyright
Copyright © 2021 Elsevier B.V. All rights reserved.
Déclaration de conflit d'intérêts
Declaration of Competing Interests The authors declare that they have no known competing financial interests or personal relationships that could have appeared to influence the work reported in this paper.