A fresh look to the phenotype in mono-allelic likely pathogenic variants of the leptin and the leptin receptor gene.

Animal Humans LEP LEPR Phenotype

Journal

Molecular and cellular pediatrics
ISSN: 2194-7791
Titre abrégé: Mol Cell Pediatr
Pays: Germany
ID NLM: 101660689

Informations de publication

Date de publication:
26 Aug 2021
Historique:
received: 25 05 2021
accepted: 19 07 2021
entrez: 27 8 2021
pubmed: 28 8 2021
medline: 28 8 2021
Statut: epublish

Résumé

Leptin (LEP) and leptin receptor (LEPR) play a major role in energy homeostasis, metabolism, and reproductive function. While effects of biallelic likely pathogenic variants (-/-) on the phenotype are well characterized, effects of mono-allelic likely pathogenic variants (wt/-) in the LEP and LEPR gene on the phenotype compared to wild-type homozygosity (wt/wt) have not been systematically investigated. We identified in our systematic review 44 animal studies (15 on Lep, 29 on Lepr) and 39 studies in humans reporting on 130 mono-allelic likely pathogenic variant carriers with 20 distinct LEP variants and 108 heterozygous mono-allelic likely pathogenic variant carriers with 35 distinct LEPR variants. We found indications for a higher weight status in carriers of mono-allelic likely pathogenic variant in the leptin and in the leptin receptor gene compared to wt/wt, in both animal and human studies. In addition, animal studies showed higher body fat percentage in Lep and Lepr wt/- vs wt/wt. Animal studies provided indications for lower leptin levels in Lep wt/- vs. wt/wt and indications for higher leptin levels in Lepr wt/- vs wt/wt. Data on leptin levels in human studies was limited. Evidence for an impaired metabolism in mono-allelic likely pathogenic variants of the leptin and in leptin receptor gene was not conclusive (animal and human studies). Mono-allelic likely pathogenic variants in the leptin and in leptin receptor gene have phenotypic effects disposing to increased body weight and fat accumulation.

Identifiants

pubmed: 34448070
doi: 10.1186/s40348-021-00119-7
pii: 10.1186/s40348-021-00119-7
pmc: PMC8390564
doi:

Types de publication

Journal Article Review

Langues

eng

Pagination

10

Subventions

Organisme : German Ministry of Education and Research (BMBF)
ID : FKZ 01GI1120A and 01GI1127
Organisme : Competence Network Obesity
ID : FKZ 01GI1401
Organisme : Hertha-Nathorff-Programm of the Medical Faculty of the University of Ulm
ID : LSSH1000.07
Organisme : Hertha-Nathorff-Programm of the Medical Faculty of the University of Ulm
ID : KSKI, 002.1
Organisme : German Research Association
ID : FI1700/7-1, Heisenberg Professorship

Informations de copyright

© 2021. The Author(s).

Références

Am J Physiol Regul Integr Comp Physiol. 2006 Apr;290(4):R975-81
pubmed: 16339386
Endocrinology. 2015 Jan;156(1):360-6
pubmed: 25353183
Nat Med. 2018 May;24(5):551-555
pubmed: 29736023
Carcinogenesis. 2004 May;25(5):821-5
pubmed: 14729596
Am J Physiol Renal Physiol. 2007 Nov;293(5):F1512-7
pubmed: 17881464
Mol Genet Metab. 2009 Aug;97(4):305-8
pubmed: 19427251
J Nutr. 1996 Oct;126(10):2487-93
pubmed: 8857509
Obes Facts. 2016;9(3):158-73
pubmed: 27241181
Diabetologia. 1981 May;20(5):573-7
pubmed: 7026332
Int J Obes Relat Metab Disord. 1997 Apr;21(4):321-6
pubmed: 9130031
Science. 1979 Feb 16;203(4381):663-5
pubmed: 760211
Endocrine. 2014 Apr;45(3):401-8
pubmed: 23824601
Mol Cell Pediatr. 2014 Dec;1(1):3
pubmed: 26567097
Endocrinology. 2001 Jul;142(7):2888-97
pubmed: 11416008
Pediatr Res. 1989 Feb;25(2):173-9
pubmed: 2919132
Nature. 1995 Oct 12;377(6549):530-2
pubmed: 7566151
Cell. 2019 Apr 18;177(3):597-607.e9
pubmed: 31002796
Hepatology. 2013 Feb;57(2):543-54
pubmed: 22941940
Am J Physiol. 1998 Apr;274(4):R985-90
pubmed: 9575960
Diabetes. 2002 Jun;51(6):1980-5
pubmed: 12031989
Int J Pediatr Obes. 2011 Oct;6(5-6):419-27
pubmed: 21854111
Endocr J. 2009;56(8):997-1008
pubmed: 19706988
Endocrinology. 2008 Jan;149(1):174-84
pubmed: 17932216
Am J Hum Genet. 1962 Dec;14:353-62
pubmed: 13937884
Am J Physiol. 1995 Jan;268(1 Pt 1):E15-20
pubmed: 7840172
Acta Paediatr Suppl. 2006 Apr;450:76-85
pubmed: 16817681
J Appl Physiol (1985). 2008 Jul;105(1):249-59
pubmed: 18467551
Obes Res Clin Pract. 2009 Mar;3(1):1-52
pubmed: 24345539
Biochem Biophys Res Commun. 1997 Nov 17;240(2):492-5
pubmed: 9388507
HPB (Oxford). 2006;8(5):386-92
pubmed: 18333092
Science. 1995 Jul 28;269(5223):543-6
pubmed: 7624777
Hum Mutat. 2016 Jun;37(6):564-9
pubmed: 26931183
Am J Physiol. 1969 Nov;217(5):1298-304
pubmed: 5346292
J Clin Endocrinol Metab. 2001 Jul;86(7):3284-91
pubmed: 11443202
Science. 1966 Sep 2;153(3740):1127-8
pubmed: 5918576
Obes Rev. 2018 Nov;19(11):1525-1543
pubmed: 30261552
EBioMedicine. 2018 Oct;36:390-400
pubmed: 30266296
Cell. 1996 Feb 9;84(3):491-5
pubmed: 8608603
Sci Rep. 2017 Mar 24;7:45130
pubmed: 28338021
Biomed Res Int. 2014;2014:912052
pubmed: 24707501
J Clin Endocrinol Metab. 2010 Jun;95(6):2836-40
pubmed: 20382689
Biol Res. 2016 Apr 13;49:23
pubmed: 27075752
J Med Genet. 1994 Feb;31(2):89-98
pubmed: 8182727
Am J Physiol Endocrinol Metab. 2011 Aug;301(2):E362-9
pubmed: 21558549
Eur J Endocrinol. 2011 Apr;164(4):521-7
pubmed: 21296922
J Clin Res Pediatr Endocrinol. 2017 Dec 08;10(3):274-278
pubmed: 29217499
Eur J Med Genet. 2018 Aug;61(8):465-467
pubmed: 29545012
Biochem Biophys Res Commun. 1968 Dec 30;33(6):883-7
pubmed: 5750852
Nature. 1996 Jul 18;382(6588):250-2
pubmed: 8717038
Lab Anim Res. 2015 Mar;31(1):1-6
pubmed: 25806077
Biochim Biophys Acta. 1982 Mar 12;710(3):290-6
pubmed: 7074117
J Biol Chem. 1975 Jun 25;250(12):4702-7
pubmed: 167002
Cell Metab. 2017 Jul 5;26(1):24-26
pubmed: 28648981
Horm Res Paediatr. 2016;85(6):412-20
pubmed: 26925581
J Exp Med. 1999 Aug 16;190(4):497-507
pubmed: 10449521
J Clin Endocrinol Metab. 1998 Sep;83(9):3239-42
pubmed: 9745435
N Engl J Med. 2003 Mar 20;348(12):1096-103
pubmed: 12646666
Am J Physiol Endocrinol Metab. 2008 May;294(5):E939-51
pubmed: 18349116
Pediatr Res. 2003 Mar;53(3):411-8
pubmed: 12595588
Reprod Sci. 2011 Apr;18(4):342-52
pubmed: 21266665
Diabetologia. 2018 Nov;61(11):2422-2432
pubmed: 30094465
J Endocrinol. 2014 Oct;223(1):T1-8
pubmed: 25121999
Nat Genet. 1998 Mar;18(3):213-5
pubmed: 9500540
J Bone Miner Res. 2003 Sep;18(9):1605-11
pubmed: 12968669
Am J Physiol. 1998 Oct;275(4):R1106-9
pubmed: 9756540
Mol Genet Metab. 2011 Apr;102(4):461-4
pubmed: 21306929
PLoS One. 2008 Aug 29;3(8):e3098
pubmed: 18769731
J Clin Endocrinol Metab. 2015 Sep;100(9):3227-30
pubmed: 26186301
Exp Anim. 2005 Jan;54(1):13-20
pubmed: 15725677
Biol Reprod. 2014 Feb 20;90(2):33
pubmed: 24389871
J Nutr. 1994 Aug;124(8):1230-7
pubmed: 7914918
Clin Genet. 2014 Oct;86(4):391-3
pubmed: 24304187
Cell Mol Life Sci. 2015 Feb;72(3):629-644
pubmed: 25098352
Diabetes. 2012 Feb;61(2):383-90
pubmed: 22210313
Mol Genet Metab. 2012 May;106(1):121-6
pubmed: 22463805
Am J Physiol. 1997 Jan;272(1 Pt 1):E100-6
pubmed: 9038858
Am J Physiol. 1985 Feb;248(2 Pt 1):E188-93
pubmed: 3881986
J Gastrointest Surg. 2004 Dec;8(8):971-81; discussion 981-2
pubmed: 15585384
Horm Metab Res. 2000 Jul;32(7):269-72
pubmed: 10965932
Mol Cell Pediatr. 2017 Nov 3;4(1):10
pubmed: 29101506
Proc Natl Acad Sci U S A. 1991 Sep 1;88(17):7806-9
pubmed: 1881916
Am J Physiol. 1999 May;276(5):E836-42
pubmed: 10329976
Obes Res. 1999 May;7(3):293-8
pubmed: 10348501
Clin Sci (Lond). 2016 Jun 1;130(12):943-86
pubmed: 27154742
J Endocrinol. 2014 Oct;223(1):T9-23
pubmed: 25063754
Nature. 1994 Dec 1;372(6505):425-32
pubmed: 7984236
Anat Rec (Hoboken). 2015 Dec;298(12):2018-29
pubmed: 26370912
J Clin Endocrinol Metab. 1998 May;83(5):1407-13
pubmed: 9589630
J Neurosci. 2001 Dec 15;21(24):RC186
pubmed: 11734601
J Clin Endocrinol Metab. 2015 May;100(5):E757-66
pubmed: 25751111
Nature. 1997 Jun 26;387(6636):903-8
pubmed: 9202122
Diabetes. 2000 Aug;49(8):1347-52
pubmed: 10923636
Eur J Endocrinol. 2017 Mar;176(3):315-322
pubmed: 28007844
Nat Med. 1997 Feb;3(2):238-40
pubmed: 9018247
Am J Physiol. 1984 May;246(5 Pt 1):E391-6
pubmed: 6720944
Endocr Rev. 2016 Aug;37(4):347-71
pubmed: 27187081
Horm Metab Res. 2002 Nov-Dec;34(11-12):686-90
pubmed: 12660883
Neurology. 2014 Jan 14;82(2):139-48
pubmed: 24336230
Clin Genet. 1984 May;25(5):381-415
pubmed: 6373070
Nature. 1996 Feb 15;379(6566):632-5
pubmed: 8628397
J Cell Biochem. 2005 Sep 1;96(1):89-96
pubmed: 16052473
Mol Genet Metab. 2017 May;121(1):51-56
pubmed: 28377240
J Hered. 1950 Dec;41(12):317-8
pubmed: 14824537
J Clin Endocrinol Metab. 1999 Oct;84(10):3686-95
pubmed: 10523015
Diabetologia. 1973 Aug;9(4):294-8
pubmed: 4767369
Nat Genet. 1997 Jul;16(3):218-20
pubmed: 9207782
Diabetes. 2008 Sep;57(9):2511-8
pubmed: 18559663
Nature. 2001 Nov 1;414(6859):34-5
pubmed: 11689931
J Dairy Sci. 2008 Jul;91(7):2893-900
pubmed: 18565947
Obesity (Silver Spring). 2015 Aug;23(8):1687-95
pubmed: 26179253
N Engl J Med. 2007 Jan 18;356(3):237-47
pubmed: 17229951
Obes Res. 2001 Oct;9(10):627-30
pubmed: 11595779
Gut. 2002 Jun;50(6):797-802
pubmed: 12010881
J Endocrinol. 2014 Oct;223(1):T63-70
pubmed: 25232148
J Cell Biochem. 2017 Dec;118(12):4762-4771
pubmed: 28523647
Metabolism. 2021 Mar;116:154438
pubmed: 33221380
Nature. 1998 Mar 26;392(6674):398-401
pubmed: 9537324
Physiol Genomics. 2010 Mar 3;41(1):9-20
pubmed: 19996157
Genes (Basel). 2019 May 07;10(5):
pubmed: 31067764
Obes Rev. 2007 Jul;8(4):293-306
pubmed: 17578380
Endocrinology. 2015 Oct;156(10):3777-90
pubmed: 26196541
Am J Physiol. 1999 Apr;276(4):E762-5
pubmed: 10198314
J Endocr Soc. 2018 Sep 17;3(1):27-41
pubmed: 30560226
BMC Med Genet. 2018 Aug 2;19(1):135
pubmed: 30068297
J Pediatr Hematol Oncol. 2003 Oct;25(10):791-6
pubmed: 14528102
Obesity (Silver Spring). 2014 Apr;22(4):1112-7
pubmed: 24319006
J Gastrointest Surg. 2003 Nov;7(7):857-62; discussion 863
pubmed: 14592658
Science. 1995 Jul 28;269(5223):546-9
pubmed: 7624778
J Clin Res Pediatr Endocrinol. 2019 Apr 17;11(4):341-349
pubmed: 30991789
J Clin Endocrinol Metab. 2018 Jul 1;103(7):2601-2612
pubmed: 29726959

Auteurs

Ingrid Koerber-Rosso (I)

Division of Pediatric Endocrinology and Diabetes, Department of Pediatrics and Adolescent Medicine, University Medical Center Ulm, Ulm, Germany.

Stephanie Brandt (S)

Division of Pediatric Endocrinology and Diabetes, Department of Pediatrics and Adolescent Medicine, University Medical Center Ulm, Ulm, Germany.

Julia von Schnurbein (J)

Division of Pediatric Endocrinology and Diabetes, Department of Pediatrics and Adolescent Medicine, University Medical Center Ulm, Ulm, Germany.

Pamela Fischer-Posovszky (P)

Division of Pediatric Endocrinology and Diabetes, Department of Pediatrics and Adolescent Medicine, University Medical Center Ulm, Ulm, Germany.

Josef Hoegel (J)

Institute of Human Genetics, University of Ulm, University Medical Center Ulm, Ulm, Germany.

Hannah Rabenstein (H)

Institute of Human Genetics, University of Ulm, University Medical Center Ulm, Ulm, Germany.

Reiner Siebert (R)

Institute of Human Genetics, University of Ulm, University Medical Center Ulm, Ulm, Germany.

Martin Wabitsch (M)

Division of Pediatric Endocrinology and Diabetes, Department of Pediatrics and Adolescent Medicine, University Medical Center Ulm, Ulm, Germany. martin.wabitsch@uniklinik-ulm.de.

Classifications MeSH