Common Commentary on Paediatric Oncology Drug Development Published: Another Step in Optimising Global Regulatory Coordination of Paediatric Development Plans.


Journal

Therapeutic innovation & regulatory science
ISSN: 2168-4804
Titre abrégé: Ther Innov Regul Sci
Pays: Switzerland
ID NLM: 101597411

Informations de publication

Date de publication:
11 2021
Historique:
received: 25 07 2021
accepted: 01 09 2021
pubmed: 10 9 2021
medline: 16 10 2021
entrez: 9 9 2021
Statut: ppublish

Résumé

The European Medicines Agency and the US Food and Drug Administration recently published a common commentary document on paediatric oncology drug development, building on the call for simultaneous submissions of paediatric investigation plans and initial pediatric study plans. The objective of this document is to guide deliberations and permit focused discussions at the monthly paediatric cluster calls, allowing early regulatory coordination of global development plans. The differences in regulations related to timeline are not considered posing a barrier in that regard.

Identifiants

pubmed: 34498227
doi: 10.1007/s43441-021-00339-z
pii: 10.1007/s43441-021-00339-z
pmc: PMC9437832
mid: NIHMS1781498
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1109-1110

Subventions

Organisme : Intramural FDA HHS
ID : FD999999
Pays : United States

Informations de copyright

© 2021. The Drug Information Association, Inc.

Références

Clin Pharmacol Ther. 2020 Mar;107(3):507-513
pubmed: 31449664
J Clin Oncol. 2020 Dec 20;38(36):4227-4230
pubmed: 32946356

Auteurs

Dominik Karres (D)

Paediatric Medicines Office, Human Medicines Division, Scientific Evidence Generation Department, European Medicines Agency (EMA), Amsterdam, The Netherlands. Dominik.Karres@ema.europa.eu.

Gregory Reaman (G)

Oncology Center of Excellence, Office of the Commissioner, Office of Oncologic Diseases, Office of New Drugs, Center for Drug Evaluation and Research, U.S. Food and Drug Administration (FDA), Silver Spring, USA.

Franca Ligas (F)

Paediatric Medicines Office, Human Medicines Division, Scientific Evidence Generation Department, European Medicines Agency (EMA), Amsterdam, The Netherlands.

Giovanni Lesa (G)

Paediatric Medicines Office, Human Medicines Division, Scientific Evidence Generation Department, European Medicines Agency (EMA), Amsterdam, The Netherlands.

Susan McCune (S)

Office of Pediatric Therapeutics, Office of the Commissioner, US Food and Drug Administration (FDA), Silver Spring, USA.

Suzanne Malli (S)

Office of Pediatric Therapeutics, Office of the Commissioner, US Food and Drug Administration (FDA), Silver Spring, USA.

Ralph Bax (R)

Paediatric Medicines Office, Human Medicines Division, Scientific Evidence Generation Department, European Medicines Agency (EMA), Amsterdam, The Netherlands.

Jean Temeck (J)

Office of Pediatric Therapeutics, Office of the Commissioner, US Food and Drug Administration (FDA), Silver Spring, USA.

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Classifications MeSH