First Report of Two Egyptian Patients with Desbuquois Dysplasia due to Homozygous

CANT1 Desbuquois dysplasia Genotype-phenotype correlation Hyperphalangism Prominent lesser trochanter

Journal

Molecular syndromology
ISSN: 1661-8769
Titre abrégé: Mol Syndromol
Pays: Switzerland
ID NLM: 101525192

Informations de publication

Date de publication:
Aug 2021
Historique:
received: 09 03 2021
accepted: 17 04 2021
entrez: 4 10 2021
pubmed: 5 10 2021
medline: 5 10 2021
Statut: ppublish

Résumé

Desbuquois dysplasia type 1 (DBQD1) is a very rare skeletal dysplasia characterized by growth retardation, short stature, distinct hand features, and a characteristic radiological monkey wrench appearance at the proximal femur. We report on 2unrelated Egyptian patients having the characteristic features of DBQD1 with different expressivity. Patient 1 presented at the age of 45 days with respiratory distress, short limbs, faltering growth, and distinctive facies while patient 2 presented at 5 years of age with short stature and hypospadias. The 2 patients shared radiological features suggestive of DBQD1. Whole-exome sequencing revealed a homozygous frameshift mutation in the

Identifiants

pubmed: 34602954
doi: 10.1159/000516607
pii: msy-0012-0279
pmc: PMC8436611
doi:

Types de publication

Journal Article

Langues

eng

Pagination

279-288

Informations de copyright

Copyright © 2021 by S. Karger AG, Basel.

Déclaration de conflit d'intérêts

The authors have no conflicts of interest to declare.

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Auteurs

Manal M Thomas (MM)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Engy A Ashaat (EA)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Ghada A Otaify (GA)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Samira Ismail (S)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Mona L Essawi (ML)

Human Genetics and Genome Research Division, Medical Molecular Genetics Department, National Research Centre, Cairo, Egypt.

Mohamed S Abdel-Hamid (MS)

Human Genetics and Genome Research Division, Medical Molecular Genetics Department, National Research Centre, Cairo, Egypt.

Heba A Hassan (HA)

Human Genetics and Genome Research Division, Medical Molecular Genetics Department, National Research Centre, Cairo, Egypt.

Sonia A Alsaiedi (SA)

Pediatric Department, Cairo University, Cairo, Egypt.

Mona Aglan (M)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Mona O El Ruby (MO)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Samia Temtamy (S)

Human Genetics and Genome Research Division, Clinical Genetics Department, National Research Centre, Cairo, Egypt.

Classifications MeSH