X-linked SCID with a rare mutation.

IL2RG gene Immunodeficiency Primary immunodeficiency disorders Severe combined immunodeficiency γc mutation

Journal

Allergy, asthma, and clinical immunology : official journal of the Canadian Society of Allergy and Clinical Immunology
ISSN: 1710-1484
Titre abrégé: Allergy Asthma Clin Immunol
Pays: England
ID NLM: 101244313

Informations de publication

Date de publication:
11 Oct 2021
Historique:
received: 11 05 2021
accepted: 19 09 2021
entrez: 12 10 2021
pubmed: 13 10 2021
medline: 13 10 2021
Statut: epublish

Résumé

Severe combined immunodeficiency (SCID) is a group of relatively rare primary immunodeficiency disorders (PIDs), characterized by disturbed development of T cells and B cells, caused by several genetic mutations that bring on different clinical presentations. SCID may be inherited as an autosomal recessive or an X-linked genetic trait. A 6-year-old male presented with a history of food allergy, productive coughs, and recurrent purulent rhinitis, poor weight gain and hypothyroidism. The total count of CD4+ T lymphocytes, along with their naïve and central memory subpopulations, as well as central memory CD8+ T cells were decreased in flow cytometry. A nucleotide substitution in exon one of interleukin 2 receptor gamma chain (IL-2RG) gene (c.115 G>A, p.D39N, ChrX: 70,331,275) was reported, based on which the diagnosis of X-liked SCID was confirmed. Antiviral and antibiotic prophylaxis, along with monthly IVIG (intravenous immunoglobulin) was started and the patient was subsequently referred for hematopoietic stem cell transplantation. PIDs should be considered as the differential diagnosis in any patient with unexplained and bizarre symptoms associated with recurrent infections, allergic and autoimmune manifestations. Clinicians should also bear X-SCID in mind in case of approach to any patient with poor weight gain, unusual allergic or endocrine manifestations, even in the case of a normal or increased level of serum immunoglobulins or T and B cells numbers.

Sections du résumé

BACKGROUND BACKGROUND
Severe combined immunodeficiency (SCID) is a group of relatively rare primary immunodeficiency disorders (PIDs), characterized by disturbed development of T cells and B cells, caused by several genetic mutations that bring on different clinical presentations. SCID may be inherited as an autosomal recessive or an X-linked genetic trait.
CASE PRESENTATION METHODS
A 6-year-old male presented with a history of food allergy, productive coughs, and recurrent purulent rhinitis, poor weight gain and hypothyroidism. The total count of CD4+ T lymphocytes, along with their naïve and central memory subpopulations, as well as central memory CD8+ T cells were decreased in flow cytometry. A nucleotide substitution in exon one of interleukin 2 receptor gamma chain (IL-2RG) gene (c.115 G>A, p.D39N, ChrX: 70,331,275) was reported, based on which the diagnosis of X-liked SCID was confirmed. Antiviral and antibiotic prophylaxis, along with monthly IVIG (intravenous immunoglobulin) was started and the patient was subsequently referred for hematopoietic stem cell transplantation.
CONCLUSION CONCLUSIONS
PIDs should be considered as the differential diagnosis in any patient with unexplained and bizarre symptoms associated with recurrent infections, allergic and autoimmune manifestations. Clinicians should also bear X-SCID in mind in case of approach to any patient with poor weight gain, unusual allergic or endocrine manifestations, even in the case of a normal or increased level of serum immunoglobulins or T and B cells numbers.

Identifiants

pubmed: 34635152
doi: 10.1186/s13223-021-00605-7
pii: 10.1186/s13223-021-00605-7
pmc: PMC8507167
doi:

Types de publication

Journal Article

Langues

eng

Pagination

107

Informations de copyright

© 2021. The Author(s).

Références

Cell. 1993 Apr 9;73(1):147-57
pubmed: 8462096
Blood. 1995 Jan 1;85(1):38-42
pubmed: 7803808
JAMA. 2009 Dec 9;302(22):2465-70
pubmed: 19996402
J Allergy Clin Immunol. 2020 Aug;146(2):258-261
pubmed: 32561390
J Pediatr Endocrinol Metab. 2008 Nov;21(11):1057-63
pubmed: 19189700
JAMA. 2014 Aug 20;312(7):729-38
pubmed: 25138334
J Allergy Clin Immunol. 2011 Feb;127(2):533-5
pubmed: 21094519
Ann N Y Acad Sci. 2011 Dec;1246:108-17
pubmed: 22236435
Adv Genet. 2001;43:103-88
pubmed: 11037300
J Allergy Clin Immunol. 2009 Sep;124(3):522-7
pubmed: 19482345
J Vis Exp. 2010 Oct 12;(44):
pubmed: 20972413
Pediatr Allergy Immunol. 2008 Jun;19(4):303-6
pubmed: 18093084
Int J Infect Dis. 2009 Nov;13(6):e420-3
pubmed: 19403320
Annu Rev Med. 1996;47:229-39
pubmed: 8712778
Blood. 1997 Oct 15;90(8):3214-21
pubmed: 9376605
Blood. 2008 Sep 1;112(5):1872-5
pubmed: 18559672
Proc Natl Acad Sci U S A. 1994 Sep 27;91(20):9466-70
pubmed: 7937790
J Biol Chem. 1994 Jan 21;269(3):1599-602
pubmed: 8294403
Immunol Rev. 1995 Dec;148:97-114
pubmed: 8825284
Front Pediatr. 2019 Apr 05;7:55
pubmed: 31024866
Am J Reprod Immunol. 2006 Aug;56(2):145-51
pubmed: 16836617
J Pediatr. 1997 Mar;130(3):378-87
pubmed: 9063412
Ann Hum Biol. 2004 Mar-Apr;31(2):263-9
pubmed: 15204368

Auteurs

Fatemeh Sadat Mahdavi (FS)

Student Research Committee, Alborz University of Medical Sciences, Karaj, Iran.

Mohammad Keramatipour (M)

Department of Medical Genetics, School of Medicine, Tehran University of Medical Sciences, Tehran, Iran.

Sarina Ansari (S)

Student Research Committee, Alborz University of Medical Sciences, Karaj, Iran.

Samin Sharafian (S)

Department of Allergy and Clinical Immunology, Mofid Children's Hospital, Shaheed Beheshti University of Medical Sciences, Bushehr, Iran.

Arezou Karamzade (A)

Department of Medical Genetics, School of Medicine, International Campus, Tehran University of Medical Sciences, Tehran, Iran.

Marzieh Tavakol (M)

Non-Communicable Diseases Research Center, Alborz University of Medical Sciences, Karaj, Iran. marziyeh.tavakol@gmail.com.

Classifications MeSH