New Challenges Resulting From the Loss of Function of Na

congenital myasthenic syndrome (CMS) congenital myopathy (CM) loss of function skeletal muscle sodium channel therapeutics

Journal

Frontiers in pharmacology
ISSN: 1663-9812
Titre abrégé: Front Pharmacol
Pays: Switzerland
ID NLM: 101548923

Informations de publication

Date de publication:
2021
Historique:
received: 31 07 2021
accepted: 16 09 2021
entrez: 21 10 2021
pubmed: 22 10 2021
medline: 22 10 2021
Statut: epublish

Résumé

The voltage-gated sodium channel Na

Identifiants

pubmed: 34671263
doi: 10.3389/fphar.2021.751095
pii: 751095
pmc: PMC8521073
doi:

Types de publication

Journal Article Review

Langues

eng

Pagination

751095

Informations de copyright

Copyright © 2021 Nicole and Lory.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

Expert Opin Drug Discov. 2018 Mar;13(3):269-277
pubmed: 29343120
Proc Natl Acad Sci U S A. 2017 Jun 27;114(26):6836-6841
pubmed: 28607094
Int J Mol Sci. 2017 Oct 19;18(10):
pubmed: 29048368
Mol Pharmacol. 2006 Jul;70(1):340-7
pubmed: 16638971
Eur J Neurosci. 2017 Aug;46(3):1887-1896
pubmed: 28635024
Cell Stem Cell. 2020 Sep 3;27(3):498
pubmed: 32888426
Br J Pharmacol. 2020 Oct;177(19):4481-4496
pubmed: 32663327
Prog Biophys Mol Biol. 2008 Oct-Nov;98(2-3):309-18
pubmed: 19351521
Methods Mol Biol. 2018;1787:235-252
pubmed: 29736723
J Cell Biol. 1991 Nov;115(3):765-78
pubmed: 1655812
Pflugers Arch. 1993 Apr;423(1-2):155-7
pubmed: 7683789
Front Physiol. 2021 May 28;12:661413
pubmed: 34122134
J Neurosci. 2000 Dec 1;20(23):8610-7
pubmed: 11102465
Cells. 2021 Jun 16;10(6):
pubmed: 34208776
Nature. 2007 Mar 1;446(7131):76-8
pubmed: 17330043
Neurology. 2010 Aug 17;75(7):641-5
pubmed: 20713951
J Clin Invest. 2008 Apr;118(4):1437-49
pubmed: 18317596
J Neurosci. 1996 Nov 15;16(22):7117-27
pubmed: 8929421
Proc Natl Acad Sci U S A. 2009 Mar 10;106(10):4036-41
pubmed: 19225109
Sci Rep. 2018 Jul 10;8(1):10372
pubmed: 29991727
Neuron. 1998 Oct;21(4):919-31
pubmed: 9808476
Proc Natl Acad Sci U S A. 2018 Aug 21;115(34):E8077-E8085
pubmed: 30076230
Curr Opin Neurol. 2015 Oct;28(5):508-14
pubmed: 26285000
J Biol Chem. 2004 Aug 6;279(32):33323-35
pubmed: 15169781
Lancet Neurol. 2015 Apr;14(4):420-34
pubmed: 25792100
Neurosci Lett. 2020 Jan 1;714:134579
pubmed: 31669315
J Neurocytol. 2003 Jun-Sep;32(5-8):505-22
pubmed: 15034250
Hum Mol Genet. 1994 Aug;3(8):1415-9
pubmed: 7987325
J Muscle Res Cell Motil. 2006;27(5-7):291-6
pubmed: 16874452
J Gen Physiol. 2021 Jan 4;153(1):
pubmed: 33306788
J Gen Physiol. 2011 Oct;138(4):393-419
pubmed: 21948948
Nature. 1985 Mar 14-20;314(6007):164-6
pubmed: 3974720
Neuromuscul Disord. 2018 May;28(5):402-407
pubmed: 29606556
J Biol Chem. 1998 May 1;273(18):11327-34
pubmed: 9556626
Muscle Nerve. 1984 Feb;7(2):110-20
pubmed: 6325904
Proc Natl Acad Sci U S A. 2012 Nov 20;109(47):19250-5
pubmed: 23134726
Neuropharmacology. 2017 Dec;127:87-108
pubmed: 28416444
Comput Biol Chem. 2019 Dec;83:107132
pubmed: 31563636
J Clin Neurol. 2009 Dec;5(4):186-91
pubmed: 20076800
J Neurosci. 2001 Nov 1;21(21):8456-63
pubmed: 11606634
Nat Commun. 2019 Apr 3;10(1):1514
pubmed: 30944319
J Neurosci. 2003 Mar 15;23(6):2102-11
pubmed: 12657669
Sci Rep. 2020 Apr 3;10(1):5852
pubmed: 32246066
Toxins (Basel). 2018 Mar 16;10(3):
pubmed: 29547537
J Mol Cell Cardiol. 2013 Aug;61:133-141
pubmed: 23702286
Nat Commun. 2017 Dec 12;8(1):2077
pubmed: 29233994
Neurosci Lett. 1992 Jan 20;135(1):41-4
pubmed: 1311822
Proc Natl Acad Sci U S A. 2003 Jun 10;100(12):7377-82
pubmed: 12766226
Cells. 2020 Jun 23;9(6):
pubmed: 32585982
Ann Neurol. 2004 Nov;56(5):650-61
pubmed: 15389891
Mol Genet Genomic Med. 2020 Aug;8(8):e1309
pubmed: 32449611
J Membr Biol. 2010 Jun;235(2):109-19
pubmed: 20517693
Neuromuscul Disord. 2006 Jan;16(1):39-45
pubmed: 16368240
Dev Dyn. 2006 Jul;235(7):1962-73
pubmed: 16615064
Sci Transl Med. 2020 Aug 26;12(558):
pubmed: 32848094
Cell. 1994 Jun 17;77(6):863-8
pubmed: 8004673
Handb Exp Pharmacol. 2018;246:309-330
pubmed: 28939973
Neurology. 2016 Jan 12;86(2):161-9
pubmed: 26659129
Dev Neurobiol. 2021 Jul;81(5):427-437
pubmed: 31859465
Neurology. 2013 Apr 16;80(16):1472-5
pubmed: 23516313
Curr Biol. 2021 Sep 13;31(17):3810-3819.e4
pubmed: 34289389
J Mol Biol. 2021 Aug 20;433(17):166967
pubmed: 33794261
J Neurosci. 1998 Jan 1;18(1):128-37
pubmed: 9412493
Physiol Rev. 2021 Oct 1;101(4):1633-1689
pubmed: 33769100
Annu Rev Physiol. 2018 Feb 10;80:159-188
pubmed: 29195055
Am J Med Genet A. 2008 Feb 1;146A(3):380-3
pubmed: 18203179
J Biol Chem. 1999 Mar 19;274(12):8129-36
pubmed: 10075715
Muscle Nerve. 2006 Sep;34(3):292-7
pubmed: 16770776
Nat Commun. 2013;4:2410
pubmed: 24002024
Nat Rev Neurosci. 2021 Mar;22(3):152-166
pubmed: 33531663
JAMA. 2012 Oct 3;308(13):1357-65
pubmed: 23032552
Neuron. 1989 Jul;3(1):33-49
pubmed: 2559760
Ann Neurol. 2015 May;77(5):840-50
pubmed: 25707578
Nature. 2016 Jun 06;534(7608):494-9
pubmed: 27281198
Biochim Biophys Acta. 2007 Nov-Dec;1769(11-12):649-58
pubmed: 17936922
Proc Natl Acad Sci U S A. 2019 May 28;116(22):10763-10772
pubmed: 31072926
Muscle Nerve. 2008 Mar;37(3):326-37
pubmed: 18041053
Brain. 2001 Jun;124(Pt 6):1100-13
pubmed: 11353726
J Physiol. 2011 Feb 1;589(Pt 3):525-46
pubmed: 21135045
J Neuromuscul Dis. 2017;4(4):269-284
pubmed: 29125502
Toxicon. 2007 Dec 15;50(8):1019-26
pubmed: 17976675
Cell. 2001 May 18;105(4):511-9
pubmed: 11371347
J Biol Chem. 2007 Oct 5;282(40):29424-30
pubmed: 17686768
Skelet Muscle. 2012 Aug 30;2(1):17
pubmed: 22935229
J Gen Physiol. 2014 Aug;144(2):137-45
pubmed: 25024265
Acta Physiol Scand. 1996 Mar;156(3):159-68
pubmed: 8729676
Brain. 2014 Apr;137(Pt 4):998-1008
pubmed: 24549961
Neurobiol Dis. 2020 Jul;141:104954
pubmed: 32445790
Handb Clin Neurol. 2018;148:565-589
pubmed: 29478601
Muscle Nerve. 1983 Feb;6(2):113-21
pubmed: 6304507
Muscle Nerve. 1986 Oct;9(8):704-10
pubmed: 3785281
Toxins (Basel). 2016 Oct 18;8(10):
pubmed: 27763551
Exp Brain Res. 2006 Jun;172(2):139-50
pubmed: 16432696
Biol Cell. 2003 Oct;95(7):437-45
pubmed: 14597261
Brain. 2013 Dec;136(Pt 12):3766-74
pubmed: 24142145
Curr Top Membr. 2016;78:315-51
pubmed: 27586289
J Gen Physiol. 2008 Mar;131(3):197-209
pubmed: 18270170
Proc Natl Acad Sci U S A. 2008 Dec 16;105(50):19980-5
pubmed: 19052238
J Neurosci. 1993 Mar;13(3):1326-36
pubmed: 8382738
Front Pharmacol. 2016 Jan 14;6:314
pubmed: 26834636
Sci Rep. 2018 Jun 26;8(1):9714
pubmed: 29946067
Science. 2018 Oct 19;362(6412):
pubmed: 30190309
Science. 1990 Nov 16;250(4983):1000-2
pubmed: 2173143
Lancet. 2018 Apr 14;391(10129):1483-1492
pubmed: 29605429
J Gen Physiol. 2008 Aug;132(2):199-208
pubmed: 18625851
Brain. 2016 Mar;139(Pt 3):674-91
pubmed: 26700687
Proc Natl Acad Sci U S A. 2000 Aug 15;97(17):9549-54
pubmed: 10944223
ACS Chem Biol. 2013;8(6):1215-22
pubmed: 23527544
Expert Opin Biol Ther. 2018 Jun;18(6):681-693
pubmed: 29781327
Stem Cell Rev Rep. 2021 Jul 1;:
pubmed: 34212303
Sci Rep. 2020 Feb 10;10(1):2199
pubmed: 32042141
F1000Res. 2020 Aug 7;9:
pubmed: 32850117
J Clin Invest. 2011 Oct;121(10):4082-94
pubmed: 21881211
PLoS One. 2020 Mar 5;15(3):e0219106
pubmed: 32134913
J Gen Physiol. 2013 Aug;142(2):101-12
pubmed: 23858005
J Clin Med. 2020 Jul 13;9(7):
pubmed: 32668756
Mol Ther. 2020 Jan 8;28(1):235-253
pubmed: 31607539
Brain. 2016 Jun;139(Pt 6):1688-99
pubmed: 27048647
J Clin Invest. 2012 Dec;122(12):4580-91
pubmed: 23187123
Acta Myol. 2017 Sep 01;36(3):125-134
pubmed: 29774303
Neurology. 2013 Mar 19;80(12):1110-6
pubmed: 23427324
Int J Mol Sci. 2021 Mar 09;22(5):
pubmed: 33803193
Sci Rep. 2018 Feb 1;8(1):2041
pubmed: 29391559
Mol Biol Evol. 2016 Apr;33(4):1068-81
pubmed: 26782998
Muscle Nerve. 2018 Apr;57(4):522-530
pubmed: 29125635
Neurol Genet. 2018 Sep 19;4(5):e267
pubmed: 30283817
Brain. 2002 Apr;125(Pt 4):835-43
pubmed: 11912116
Neurology. 2004 Dec 14;63(11):2120-7
pubmed: 15596759
Handb Clin Neurol. 2018;148:549-564
pubmed: 29478600
J Neuromuscul Dis. 2021;8(3):357-381
pubmed: 33325393
Cell. 1991 Nov 29;67(5):1021-7
pubmed: 1659948
Neuron. 1989 Aug;3(2):163-75
pubmed: 2560390
Cell Rep. 2017 Nov 28;21(9):2348-2356
pubmed: 29186674
JAMA. 2018 Dec 11;320(22):2344-2353
pubmed: 30535218
Sci Rep. 2018 Nov 12;8(1):16681
pubmed: 30420713
Neurology. 2017 Jan 24;88(4):414-416
pubmed: 28003497
Ann Neurol. 2001 Sep;50(3):417-20
pubmed: 11558801
Neuron. 1993 Nov;11(5):915-22
pubmed: 8240813
Biochem Biophys Res Commun. 2008 Apr 11;368(3):761-6
pubmed: 18261980
J Neurol Neurosurg Psychiatry. 2020 Aug;91(8):898-900
pubmed: 32487525
Int J Mol Sci. 2020 Nov 04;21(21):
pubmed: 33158049
J Gen Physiol. 2019 Apr 1;151(4):555-566
pubmed: 30733232
Neurology. 2011 May 10;76(19):1635-41
pubmed: 21490317
J Gen Physiol. 2012 Apr;139(4):305-19
pubmed: 22450487
Circ Res. 2010 Apr 30;106(8):1342-50
pubmed: 20339120
Neurology. 2019 Mar 26;92(13):e1405-e1415
pubmed: 30824560
Cell Mol Life Sci. 2021 Jul;78(14):5469-5488
pubmed: 34100980
Biochem Biophys Res Commun. 2006 Sep 22;348(2):653-61
pubmed: 16890191
Brain Commun. 2020 Jul 16;2(2):fcaa103
pubmed: 33005891
Neuromuscul Disord. 2017 Jun;27(6):574-580
pubmed: 28262468
Curr Treat Options Neurol. 2020;22(10):34
pubmed: 32848354
Annu Rev Pharmacol Toxicol. 2020 Jan 6;60:133-154
pubmed: 31537174
Neurosci Lett. 2020 Sep 14;735:135163
pubmed: 32553805
Sci Rep. 2021 Feb 2;11(1):2846
pubmed: 33531589

Auteurs

Sophie Nicole (S)

Institut de Génomique Fonctionnelle (IGF), Université de Montpellier, CNRS, INSERM, Montpellier, France.
LabEx 'Ion Channel Science and Therapeutics (ICST), Montpellier, France.

Philippe Lory (P)

Institut de Génomique Fonctionnelle (IGF), Université de Montpellier, CNRS, INSERM, Montpellier, France.
LabEx 'Ion Channel Science and Therapeutics (ICST), Montpellier, France.

Classifications MeSH