Tunable control of CAR T cell activity through tetracycline mediated disruption of protein-protein interaction.


Journal

Scientific reports
ISSN: 2045-2322
Titre abrégé: Sci Rep
Pays: England
ID NLM: 101563288

Informations de publication

Date de publication:
09 11 2021
Historique:
received: 05 08 2021
accepted: 25 10 2021
entrez: 10 11 2021
pubmed: 11 11 2021
medline: 29 1 2022
Statut: epublish

Résumé

Chimeric antigen receptor (CAR) T cells are a promising form of cancer immunotherapy, although they are often associated with severe toxicities. Here, we present a split-CAR design incorporating separate antigen recognition and intracellular signaling domains. These exploit the binding between the tetracycline repressor protein and a small peptide sequence (TIP) to spontaneously assemble as a functional CAR. Addition of the FDA-approved, small molecule antibiotic minocycline, acts as an "off-switch" by displacing the signaling domain and down-tuning CAR T activity. Here we describe the optimization of this split-CAR approach to generate a CAR in which cytotoxicity, cytokine secretion and proliferation can be inhibited in a dose-dependent and reversible manner. Inhibition is effective during on-going CAR T cell activation and inhibits activation and tumor control in vivo. This work shows how optimization of split-CAR structure affects function and adds a novel design allowing easy CAR inhibition through an FDA-approved small molecule.

Identifiants

pubmed: 34754016
doi: 10.1038/s41598-021-01418-9
pii: 10.1038/s41598-021-01418-9
pmc: PMC8578617
doi:

Substances chimiques

Receptors, Chimeric Antigen 0
Minocycline FYY3R43WGO

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

21902

Subventions

Organisme : Wellcome Trust
Pays : United Kingdom

Informations de copyright

© 2021. The Author(s).

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Auteurs

Alastair Hotblack (A)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Evangelia K Kokalaki (EK)

Autolus Therapeutics, White City, London, UK.

Morgan J Palton (MJ)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Gordon Weng-Kit Cheung (GW)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Iwan P Williams (IP)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Somayya Manzoor (S)

Autolus Therapeutics, White City, London, UK.

Thomas I Grothier (TI)

Autolus Therapeutics, White City, London, UK.

Alice Piapi (A)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Valeria Fiaccadori (V)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Patrycja Wawrzyniecka (P)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Harriet A Roddy (HA)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Giulia Agliardi (G)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Claire Roddie (C)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK.

Shimobi Onuoha (S)

Autolus Therapeutics, White City, London, UK.

Simon Thomas (S)

Autolus Therapeutics, White City, London, UK.

Shaun Cordoba (S)

Autolus Therapeutics, White City, London, UK.

Martin Pule (M)

Department of Haematology, UCL Cancer Institute, University College, 72 Huntley Street, London, WC1E 6DD, UK. m.pule@ucl.ac.uk.
Autolus Therapeutics, White City, London, UK. m.pule@ucl.ac.uk.

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Classifications MeSH