Challenges in Treating Charcot-Marie-Tooth Disease and Related Neuropathies: Current Management and Future Perspectives.
CMT
clinical trials
gene silencing
gene therapy
inherited neuropathy
management
therapy
Journal
Brain sciences
ISSN: 2076-3425
Titre abrégé: Brain Sci
Pays: Switzerland
ID NLM: 101598646
Informations de publication
Date de publication:
29 Oct 2021
29 Oct 2021
Historique:
received:
11
10
2021
revised:
25
10
2021
accepted:
26
10
2021
entrez:
27
11
2021
pubmed:
28
11
2021
medline:
28
11
2021
Statut:
epublish
Résumé
There is still no effective drug treatment available for Charcot-Marie-Tooth neuropathies (CMT). Current management relies on rehabilitation therapy, surgery for skeletal deformities, and symptomatic treatment of pain; fatigue and cramps are frequent complaints that are difficult to treat. The challenge is to find disease-modifying therapies. Several approaches, including gene silencing, to counteract the
Identifiants
pubmed: 34827446
pii: brainsci11111447
doi: 10.3390/brainsci11111447
pmc: PMC8615778
pii:
doi:
Types de publication
Journal Article
Review
Langues
eng
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