Molecular Mechanisms of Cereblon-Interacting Small Molecules in Multiple Myeloma Therapy.

CELMoDs Cereblon IMiDs multiple myeloma thalidomide

Journal

Journal of personalized medicine
ISSN: 2075-4426
Titre abrégé: J Pers Med
Pays: Switzerland
ID NLM: 101602269

Informations de publication

Date de publication:
11 Nov 2021
Historique:
received: 18 10 2021
revised: 08 11 2021
accepted: 08 11 2021
entrez: 27 11 2021
pubmed: 28 11 2021
medline: 28 11 2021
Statut: epublish

Résumé

Thalidomide analogues (or immunomodulatory imide drugs, IMiDs) are cornerstones in the treatment of multiple myeloma (MM). These drugs bind Cereblon (CRBN), a receptor for the Cullin-ring 4 ubiquitin-ligase (CRL4) complex, to modify its substrate specificity. IMiDs mediate CRBN-dependent engagement and proteasomal degradation of 'neosubstrates', Ikaros (IKZF1) and Aiolos (IKZF3), conveying concurrent antimyeloma activity and T-cell costimulation. There is now a greater understanding of physiological CRBN functions, including endogenous substrates and chaperone activity. CRISPR Cas9-based genome-wide screening has further elucidated the complex cellular machinery implicated in IMiD sensitivity, including IKZF1/3-independent mechanisms. New-generation IMiD derivatives with more potent anti-cancer properties-the CELMoDs (Cereblon E3 ligase modulators)-are now being evaluated. Rational drug design also allows 'hijacking' of CRL4

Identifiants

pubmed: 34834536
pii: jpm11111185
doi: 10.3390/jpm11111185
pmc: PMC8623651
pii:
doi:

Types de publication

Journal Article Review

Langues

eng

Subventions

Organisme : Australian Medical Research Future Fund
ID : GNT1160133
Organisme : Family of My Laurence Bode
ID : NA

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Auteurs

Matteo Costacurta (M)

Blood Cancer Therapeutics Laboratory, Department of Medicine, School of Clinical Sciences at Monash Health, Monash University, Clayton, VIC 3168, Australia.
Monash Haematology, Monash Health, Clayton, VIC 3168, Australia.

Jackson He (J)

Blood Cancer Therapeutics Laboratory, Department of Medicine, School of Clinical Sciences at Monash Health, Monash University, Clayton, VIC 3168, Australia.
Monash Haematology, Monash Health, Clayton, VIC 3168, Australia.
Medicinal Chemistry, Monash Institute of Pharmaceutical Sciences, Monash University, 381 Royal Parade, Parkville, VIC 3052, Australia.

Philip E Thompson (PE)

Medicinal Chemistry, Monash Institute of Pharmaceutical Sciences, Monash University, 381 Royal Parade, Parkville, VIC 3052, Australia.

Jake Shortt (J)

Blood Cancer Therapeutics Laboratory, Department of Medicine, School of Clinical Sciences at Monash Health, Monash University, Clayton, VIC 3168, Australia.
Monash Haematology, Monash Health, Clayton, VIC 3168, Australia.

Classifications MeSH