Common Genetic Variants Contribute to Risk of Transposition of the Great Arteries.


Journal

Circulation research
ISSN: 1524-4571
Titre abrégé: Circ Res
Pays: United States
ID NLM: 0047103

Informations de publication

Date de publication:
21 01 2022
Historique:
pubmed: 11 12 2021
medline: 25 2 2022
entrez: 10 12 2021
Statut: ppublish

Résumé

Dextro-transposition of the great arteries (D-TGA) is a severe congenital heart defect which affects approximately 1 in 4,000 live births. While there are several reports of D-TGA patients with rare variants in individual genes, the majority of D-TGA cases remain genetically elusive. Familial recurrence patterns and the observation that most cases with D-TGA are sporadic suggest a polygenic inheritance for the disorder, yet this remains unexplored. We sought to study the role of common single nucleotide polymorphisms (SNPs) in risk for D-TGA. We conducted a genome-wide association study in an international set of 1,237 patients with D-TGA and identified a genome-wide significant susceptibility locus on chromosome 3p14.3, which was subsequently replicated in an independent case-control set (rs56219800, meta-analysis P=8.6x10 This work provides support for a polygenic architecture in D-TGA and identifies a susceptibility locus on chromosome 3p14.3 near

Identifiants

pubmed: 34886679
doi: 10.1161/CIRCRESAHA.120.317107
pmc: PMC8768504
doi:

Substances chimiques

T-Box Domain Proteins 0
TBX20 protein, human 0
WNT5A protein, human 0
Wnt-5a Protein 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

166-180

Subventions

Organisme : NHLBI NIH HHS
ID : U01 HL098123
Pays : United States
Organisme : Medical Research Council
ID : MC_PC_17115
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : U01 HL098163
Pays : United States
Organisme : Medical Research Council
ID : G1100695
Pays : United Kingdom
Organisme : Medical Research Council
ID : MC_G1000733
Pays : United Kingdom
Organisme : Motor Neurone Disease Association
ID : SHAW/NOV14/985-797
Pays : United Kingdom
Organisme : British Heart Foundation
ID : RG/F/21/110050
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : U01 HL131003
Pays : United States
Organisme : Medical Research Council
ID : MR/L021803/1
Pays : United Kingdom
Organisme : NHGRI NIH HHS
ID : U54 HG006504
Pays : United States
Organisme : NHLBI NIH HHS
ID : U01 HL098162
Pays : United States
Organisme : Medical Research Council
ID : G0900635
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 076113
Pays : United Kingdom
Organisme : NICHD NIH HHS
ID : P01 HD070454
Pays : United States
Organisme : NHLBI NIH HHS
ID : U01 HL098147
Pays : United States
Organisme : NHLBI NIH HHS
ID : UM1 HL098147
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR000003
Pays : United States
Organisme : NCRR NIH HHS
ID : M01 RR000240
Pays : United States
Organisme : Wellcome Trust
ID : 090355
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/R024804/1
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : UM1 HL128761
Pays : United States
Organisme : NHLBI NIH HHS
ID : UM1 HL128711
Pays : United States
Organisme : British Heart Foundation
ID : RG/15/12/31616
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : UM1 HL098162
Pays : United States
Organisme : British Heart Foundation
ID : CH/13/2/30154
Pays : United Kingdom
Organisme : Motor Neurone Disease Association
ID : ALCHALABI-DOBSON/APR14/829-791
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 085475
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : UM1 HL098123
Pays : United States
Organisme : Medical Research Council
ID : G0500289
Pays : United Kingdom
Organisme : Motor Neurone Disease Association
ID : SHAW/APR15/970-797
Pays : United Kingdom
Organisme : Medical Research Council
ID : G0900688
Pays : United Kingdom
Organisme : NHLBI NIH HHS
ID : U01 HL098153
Pays : United States
Organisme : NHLBI NIH HHS
ID : P50 HL074731
Pays : United States
Organisme : NHLBI NIH HHS
ID : U01 HL098188
Pays : United States

Commentaires et corrections

Type : CommentIn

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Auteurs

Doris Škorić-Milosavljević (D)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).
Department of Human Genetics, Amsterdam University Medical Centers, The Netherlands (D.S.-M., E.M.L., A.V.P.).

Rafik Tadros (R)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).
Department of Medicine, Cardiovascular Genetics Center, Montreal Heart Institute and Faculty of Medicine, Université de Montréal, Montreal, Québec, Canada (R.T., M.-A.C.).

Fernanda M Bosada (FM)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Federico Tessadori (F)

Hubrecht Institute-KNAW and University Medical Center Utrecht, the Netherlands (F.T., J.B., C.J.B.).

Jan Hendrik van Weerd (JH)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Odilia I Woudstra (OI)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).
Department of Cardiology, University Medical Center Utrecht, The Netherlands (O.I.W., G.T.S., F.M.).

Fleur V Y Tjong (FVY)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

Najim Lahrouchi (N)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

Fanny Bajolle (F)

German Heart Center Berlin, Department of Congenital Heart Disease, Pediatric Cardiology, DZHK (German Centre for Cardiovascular Research), Partner Site Berlin, Germany (F.B., S.S.).

Heather J Cordell (HJ)

Population Health Sciences Institute, Newcastle University, Newcastle, United Kingdom (H.J.C.).

A J Agopian (AJ)

Human Genetics Center, Department of Epidemiology, Human Genetics, and Environmental Sciences, UTHealth School of Public Health, Houston, TX (A.J.A.).

Gillian M Blue (GM)

Heart Centre for Children, The Children's Hospital at Westmead and Sydney Medical School, Faculty of Medicine and Health, University of Sydney, Australia (G.M.B., D.S.W.).

Daniela Q C M Barge-Schaapveld (DQCM)

Department of Clinical Genetics, Leiden University Medical Center, The Netherlands (D.Q.C.M.B.-S.).

Marc Gewillig (M)

University of Leuven, Belgium (M.G.).

Christoph Preuss (C)

Cardiovascular Genetics, Department of Pediatrics, CHU Sainte-Justine, Université de Montréal, Québec, Canada (C.P., G.A.).
The Jackson Laboratory, Bar Harbor, ME (C.P.).

Elisabeth M Lodder (EM)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).
Department of Human Genetics, Amsterdam University Medical Centers, The Netherlands (D.S.-M., E.M.L., A.V.P.).

Phil Barnett (P)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Aho Ilgun (A)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Leander Beekman (L)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

Karel van Duijvenboden (K)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Regina Bokenkamp (R)

Division of Pediatric Cardiology, Department of Pediatrics (R.B., R.L.F.v.d.P.), Leiden University Medical Center, The Netherlands.

Martina Müller-Nurasyid (M)

Institute of Genetic Epidemiology, Helmholtz Zentrum München - German Research Center for Environmental Health, Neuherberg, Germany (M.M.-N.).
IBE, Faculty of Medicine, LMU Munich, Germany (M.M.-N.).
Institute of Medical Biostatistics, Epidemiology and Informatics (IMBEI), University Medical Center, Johannes Gutenberg University, Mainz, Germany (M.M.-N.).

Hubert W Vliegen (HW)

Department of Cardiology (H.W.V.), Leiden University Medical Center, The Netherlands.

Thelma C Konings (TC)

Department of Cardiology, Amsterdam University Medical Centers, VU Amsterdam, The Netherlands (T.C.K.).

Joost P van Melle (JP)

Department of Cardiology, University Medical Center Groningen, University of Groningen, The Netherlands (J.P.v.M.).

Arie P J van Dijk (APJ)

Department of Cardiology, Radboud University Medical Center, Nijmegen, The Netherlands (A.P.J.v.D., R.R.J.v.K.).

Roland R J van Kimmenade (RRJ)

Department of Cardiology, Radboud University Medical Center, Nijmegen, The Netherlands (A.P.J.v.D., R.R.J.v.K.).
Department of Cardiology, Maastricht University Medical Center, The Netherlands (R.R.J.v.K.).

Jolien W Roos-Hesselink (JW)

Department of Cardiology, Erasmus Medical Center, Erasmus University, Rotterdam, The Netherlands (J.W.R.-H.).

Gertjan T Sieswerda (GT)

Department of Cardiology, University Medical Center Utrecht, The Netherlands (O.I.W., G.T.S., F.M.).

Folkert Meijboom (F)

Department of Cardiology, University Medical Center Utrecht, The Netherlands (O.I.W., G.T.S., F.M.).

Hashim Abdul-Khaliq (H)

Saarland University Medical Center, Department of Pediatric Cardiology, Homburg, Germany (H.A.-K.).

Felix Berger (F)

Unité Médico-Chirurgicale de Cardiologie Congénitale et Pédiatrique, Centre de référence Malformations Cardiaques Congénitales Complexes - M3C, Hôpital Necker Enfants Malades, APHP and Université Paris Descartes, Sorbonne Paris Cité, Paris, France (F.B., D.B.).
Charité, Universitätsmedizin Berlin, Department for Paediatric Cardiology, Germany (F.B.).

Sven Dittrich (S)

Department of Pediatric Cardiology, Friedrich-Alexander-University of Erlangen-Nuernberg (FAU), Germany (S.D., J.M.).

Marc-Phillip Hitz (MP)

Department of Congenital Heart Disease and Pediatric Cardiology, University Hospital Schleswig-Holstein/Campus Kiel, DZHK (German Centre for Cardiovascular Research), partner site Hamburg/Kiel/Lübeck, Germany (M.-P.H.).
Department of Human Genetics, University Medical Center Schleswig-Holstein, Kiel, Germany (M.-P.H.).

Julia Moosmann (J)

Department of Pediatric Cardiology, Friedrich-Alexander-University of Erlangen-Nuernberg (FAU), Germany (S.D., J.M.).

Frank-Thomas Riede (FT)

Leipzig Heart Center, Department of Pediatric Cardiology, University of Leipzig, Germany (F.-T.R.).

Stephan Schubert (S)

German Heart Center Berlin, Department of Congenital Heart Disease, Pediatric Cardiology, DZHK (German Centre for Cardiovascular Research), Partner Site Berlin, Germany (F.B., S.S.).
Heart and Diabetes Center NRW, Center of Congenital Heart Disease, Ruhr-University of Bochum, Bad Oeynhausen, Germany (S.S.).

Pilar Galan (P)

Sorbonne Paris Nord (Paris 13) University, Inserm U1153, Inrae U1125, Cnam, Nutritional Epidemiology Research Team (EREN), Epidemiology and Statistics Research Center - University of Paris (CRESS), Bobigny, France (P.G.).

Mark Lathrop (M)

McGill Genome Centre and Department of Human Genetics, McGill University, Montreal, Québec, Canada (M.L., H.M.M.).

Hans M Munter (HM)

McGill Genome Centre and Department of Human Genetics, McGill University, Montreal, Québec, Canada (M.L., H.M.M.).

Ammar Al-Chalabi (A)

Maurice Wohl Clinical Neuroscience Institute, Department of Basic and Clinical Neuroscience, King's College London, United Kingdom (A.A.-C.).

Christopher E Shaw (CE)

United Kingdom Dementia Research Institute Centre, Maurice Wohl Clinical Neuroscience Institute, Institute of Psychiatry, Psychology and Neuroscience, King's College London, United Kingdom (C.E.S.).
Centre for Brain Research, University of Auckland, New Zealand (C.E.S.).

Pamela J Shaw (PJ)

Sheffield Institute for Translational Neuroscience (SITraN), University of Sheffield and NIHR Sheffield Biomedical Research Centre for Translational Neuroscience, United Kingdom (P.J.S.).

Karen E Morrison (KE)

Faculty of Medicine Health & Life Sciences, Queens University Belfast, United Kingdom (K.E.M.).

Jan H Veldink (JH)

Department of Neurology, UMC Utrecht Brain Center, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands (J.H.V., L.H.v.d.B.).

Leonard H van den Berg (LH)

Department of Neurology, UMC Utrecht Brain Center, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands (J.H.V., L.H.v.d.B.).

Sylvia Evans (S)

Skaggs School of Pharmacy and Pharmaceutical Sciences, University of California, San Diego (S.E.).

Marcelo A Nobrega (MA)

Department of Human Genetics, University of Chicago, IL (M.A.N., I.A.).

Ivy Aneas (I)

Department of Human Genetics, University of Chicago, IL (M.A.N., I.A.).

Milena Radivojkov-Blagojević (M)

Helmholtz Zentrum Munich, Institut of Human Genetics, Neuherberg, Germany (M.R.-B., T.M.).

Thomas Meitinger (T)

Helmholtz Zentrum Munich, Institut of Human Genetics, Neuherberg, Germany (M.R.-B., T.M.).
Division of Cardiology, Department of Pediatrics, McMaster University, Hamilton, Ontario, Canada (T.M.).

Erwin Oechslin (E)

Peter Munk Cardiac Center, Toronto Congenital Cardiac Centre for Adults and University of Toronto, Canada (E.O.).

Tapas Mondal (T)

DZHK (German Centre for Cardiovascular Research), partner site Munich Heart Alliance, Germany (T.M.).

Lynn Bergin (L)

Division of Cardiology, Department of Medicine, London Health Sciences Centre, ON, Canada (L.B.).

John F Smythe (JF)

Division of Cardiology, Department of Pediatrics, Kingston General Hospital, ON, Canada (J.F.S.).

Luis Altamirano-Diaz (L)

Western University, Ontario, Canada (L.A.-D.).

Jane Lougheed (J)

Division of Cardiology, Department of Pediatrics, Children's Hospital of Eastern Ontario, Ottawa, Canada (J.L.).

Berto J Bouma (BJ)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

Marie-A Chaix (MA)

Department of Medicine, Cardiovascular Genetics Center, Montreal Heart Institute and Faculty of Medicine, Université de Montréal, Montreal, Québec, Canada (R.T., M.-A.C.).

Jennie Kline (J)

Department of Epidemiology, Mailman School of Public Health, Columbia University, NY (J.K.).

Anne S Bassett (AS)

Clinical Genetics Research Program, Centre for Addiction and Mental Health (A.S.B.).
Department of Psychiatry, University of Toronto, Toronto General Hospital, University Health Network, Ontario, Canada (A.S.B.).

Gregor Andelfinger (G)

Cardiovascular Genetics, Department of Pediatrics, CHU Sainte-Justine, Université de Montréal, Québec, Canada (C.P., G.A.).

Roel L F van der Palen (RLF)

Division of Pediatric Cardiology, Department of Pediatrics (R.B., R.L.F.v.d.P.), Leiden University Medical Center, The Netherlands.

Patrice Bouvagnet (P)

CPDPN, Hôpital MFME, CHU Martinique, Fort de France, Martinique, France (P.B.).

Sally-Ann B Clur (SB)

Department of Pediatric Cardiology, Emma Children's Hospital Amsterdam University Medical Centers (AMC), The Netherlands (S.-A.B.C.).
Centre for Congenital Heart Disease Amsterdam-Leiden (CAHAL) (S.-A.B.C.).

Jeroen Breckpot (J)

Hubrecht Institute-KNAW and University Medical Center Utrecht, the Netherlands (F.T., J.B., C.J.B.).
Center for Human Genetics University Hospitals KU Leuven, Belgium (J.B.).

Wilhelmina S Kerstjens-Frederikse (WS)

Department of Clinical Genetics, University Medical Center Groningen, University of Groningen, The Netherlands (W.S.K.-F.).

David S Winlaw (DS)

Heart Centre for Children, The Children's Hospital at Westmead and Sydney Medical School, Faculty of Medicine and Health, University of Sydney, Australia (G.M.B., D.S.W.).

Ulrike M M Bauer (UMM)

National Register for Congenital Heart Defects, DZHK (German Centre for Cardiovascular Research), Berlin, Germany (U.M.M.B.).

Seema Mital (S)

Hospital for Sick Children, University of Toronto, Ontario, Canada (S.M.).

Elizabeth Goldmuntz (E)

Division of Cardiology, Children's Hospital of Philadelphia and Department of Pediatrics, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA (E.G.).

Bernard Keavney (B)

Division of Cardiovascular Sciences, School of Medical Sciences, Faculty of Biology, Medicine and Health, The University of Manchester and Manchester University NHS Foundation Trust, Manchester Academic Health Science Centre, United Kingdom (B.K.).

Damien Bonnet (D)

Unité Médico-Chirurgicale de Cardiologie Congénitale et Pédiatrique, Centre de référence Malformations Cardiaques Congénitales Complexes - M3C, Hôpital Necker Enfants Malades, APHP and Université Paris Descartes, Sorbonne Paris Cité, Paris, France (F.B., D.B.).

Barbara J Mulder (BJ)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

Michael W T Tanck (MWT)

Department of Clinical Epidemiology, Biostatistics and Bioinformatics, Amsterdam Public Health (APH), Amsterdam University Medical Centers, University of Amsterdam, The Netherlands (M.W.T.T.).

Jeroen Bakkers (J)

Division of Heart and Lungs, Department of Medical Physiology, University Medical Center Utrecht, the Netherlands (J.B.).

Vincent M Christoffels (VM)

Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Cornelis J Boogerd (CJ)

Hubrecht Institute-KNAW and University Medical Center Utrecht, the Netherlands (F.T., J.B., C.J.B.).

Alex V Postma (AV)

Department of Human Genetics, Amsterdam University Medical Centers, The Netherlands (D.S.-M., E.M.L., A.V.P.).
Department of Medical Biology, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Cardiovascular Sciences, the Netherlands (F.M.B., J.H.v.W., P.B., A.I., K.v.D., V.M.C., A.V.P.).

Connie R Bezzina (CR)

Department of Clinical and Experimental Cardiology, Amsterdam University Medical Centers, University of Amsterdam, Heart Center, Amsterdam Cardiovascular Sciences, The Netherlands (D.S.-M., R.T., O.I.W., F.V.Y.T., N.L., E.M.L., L.B., B.J.B., B.J.M., C.R.B.).

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