Heterogeneity of beta-cell function in subjects with multiple islet autoantibodies in the TEDDY family prevention study - TEFA.

Continuous glucose monitoring Glucose metabolism Islet autoantibodies beta-cell function

Journal

Clinical diabetes and endocrinology
ISSN: 2055-8260
Titre abrégé: Clin Diabetes Endocrinol
Pays: England
ID NLM: 101669619

Informations de publication

Date de publication:
05 Jan 2022
Historique:
received: 26 07 2021
accepted: 29 11 2021
entrez: 5 1 2022
pubmed: 6 1 2022
medline: 6 1 2022
Statut: epublish

Résumé

Individuals with multiple islet autoantibodies are at increased risk for clinical type 1 diabetes and may proceed gradually from stage to stage complicating the recruitment to secondary prevention studies. We evaluated multiple islet autoantibody positive subjects before randomisation for a clinical trial 1 month apart for beta-cell function, glucose metabolism and continuous glucose monitoring (CGM). We hypothesized that the number and type of islet autoantibodies in combination with different measures of glucose metabolism including fasting glucose, HbA1c, oral glucose tolerance test (OGTT), intra venous glucose tolerance test (IvGTT) and CGM allows for more precise staging of autoimmune type 1 diabetes than the number of islet autoantibodies alone. Subjects (n = 57) at 2-50 years of age, positive for two or more islet autoantibodies were assessed by fasting plasma insulin, glucose, HbA1c as well as First Phase Insulin Response (FPIR) in IvGTT, followed 1 month later by OGTT, and 1 week of CGM (n = 24). Autoantibodies against GAD65 (GADA; n = 52), ZnT8 (ZnT8A; n = 40), IA-2 (IA-2A; n = 38) and insulin (IAA; n = 28) were present in 9 different combinations of 2-4 autoantibodies. Fasting glucose and HbA1c did not differ between the two visits. The estimate of the linear relationship between log2-transformed FPIR as the outcome and log2-transformed area under the OGTT glucose curve (AUC) as the predictor, adjusting for age and sex was - 1.88 (- 2.71, - 1.05) p = 3.49 × 10-5. The direction of the estimates for all glucose metabolism measures was positive except for FPIR, which was negative. FPIR was associated with higher blood glucose. Both the median and the spread of the CGM glucose data were significantly associated with higher glucose values based on OGTT, higher HbA1c, and lower FPIR. There was no association between glucose metabolism, autoantibody number and type except that there was an indication that the presence of at least one of ZnT8(Q/R/W) A was associated with a lower log2-transformed FPIR (- 0.80 (- 1.58, - 0.02), p = 0.046). The sole use of two or more islet autoantibodies as inclusion criterion for Stage 1 diabetes in prevention trials is unsatisfactory. Staging type 1 diabetes needs to take the heterogeneity in beta-cell function and glucose metabolism into account. ClinicalTrials.gov identifier: NCT02605148 , November 16, 2015.

Sections du résumé

BACKGROUND BACKGROUND
Individuals with multiple islet autoantibodies are at increased risk for clinical type 1 diabetes and may proceed gradually from stage to stage complicating the recruitment to secondary prevention studies. We evaluated multiple islet autoantibody positive subjects before randomisation for a clinical trial 1 month apart for beta-cell function, glucose metabolism and continuous glucose monitoring (CGM). We hypothesized that the number and type of islet autoantibodies in combination with different measures of glucose metabolism including fasting glucose, HbA1c, oral glucose tolerance test (OGTT), intra venous glucose tolerance test (IvGTT) and CGM allows for more precise staging of autoimmune type 1 diabetes than the number of islet autoantibodies alone.
METHODS METHODS
Subjects (n = 57) at 2-50 years of age, positive for two or more islet autoantibodies were assessed by fasting plasma insulin, glucose, HbA1c as well as First Phase Insulin Response (FPIR) in IvGTT, followed 1 month later by OGTT, and 1 week of CGM (n = 24).
RESULTS RESULTS
Autoantibodies against GAD65 (GADA; n = 52), ZnT8 (ZnT8A; n = 40), IA-2 (IA-2A; n = 38) and insulin (IAA; n = 28) were present in 9 different combinations of 2-4 autoantibodies. Fasting glucose and HbA1c did not differ between the two visits. The estimate of the linear relationship between log2-transformed FPIR as the outcome and log2-transformed area under the OGTT glucose curve (AUC) as the predictor, adjusting for age and sex was - 1.88 (- 2.71, - 1.05) p = 3.49 × 10-5. The direction of the estimates for all glucose metabolism measures was positive except for FPIR, which was negative. FPIR was associated with higher blood glucose. Both the median and the spread of the CGM glucose data were significantly associated with higher glucose values based on OGTT, higher HbA1c, and lower FPIR. There was no association between glucose metabolism, autoantibody number and type except that there was an indication that the presence of at least one of ZnT8(Q/R/W) A was associated with a lower log2-transformed FPIR (- 0.80 (- 1.58, - 0.02), p = 0.046).
CONCLUSIONS CONCLUSIONS
The sole use of two or more islet autoantibodies as inclusion criterion for Stage 1 diabetes in prevention trials is unsatisfactory. Staging type 1 diabetes needs to take the heterogeneity in beta-cell function and glucose metabolism into account.
TRIAL REGISTRATION BACKGROUND
ClinicalTrials.gov identifier: NCT02605148 , November 16, 2015.

Identifiants

pubmed: 34983671
doi: 10.1186/s40842-021-00135-6
pii: 10.1186/s40842-021-00135-6
pmc: PMC8728995
doi:

Banques de données

ClinicalTrials.gov
['NCT02605148']

Types de publication

Journal Article

Langues

eng

Pagination

23

Subventions

Organisme : juvenile diabetes research foundation united states of america
ID : 2-SRA-2014-309-M-R
Organisme : foundation for the national institutes of health
ID : 1UO1 DK063861
Organisme : vetenskapsrådet
ID : Dnr 2020-01537
Organisme : stiftelsen för strategisk forskning
ID : Dnr IRC15-0067

Investigateurs

Anita Ramelius (A)
Ida Jönsson (I)
Rasmus Bennet (R)
Birgitta Sjöberg (B)
Åsa Wimar (Å)
Jessica Melin (J)
Maria Ask (M)
Anne Wallin (A)
Monika Hansen (M)
Susanne Hyberg (S)
Karin Ottosson (K)
Jenny Bremer (J)
Ulla-Marie Carlsson (UM)
Ulrika Ulvenhag (U)
Anette Sjöberg (A)
Marielle Lindström (M)
Lina Fransson (L)
Fredrik Johansen (F)
Kobra Rahmati (K)
Zeliha Mestan (Z)
Evelyn Tekum-Amboh (E)
Silvija Jovic (S)
Joanna Gerardsson (J)
Emelie Ericson-Hallström (E)
Sofie Åberg (S)
Sara Sibthorpe (S)
Elina Mäntymäki (E)
Sini Vainionpää (S)
Minna Romo (M)
Zhian Othmani (Z)
Eeva Varjonen (E)
Sanna Jokipuu (S)
Satu Ruohonen (S)
Laura Leppänen (L)
Petra Rajala (P)
Eija Riski (E)
Miia Kähönen (M)
Minna-Liisa Koivikko (ML)
Tea Joensuu (T)
Heidi Alanen (H)
Teija Mykkänen (T)
Tiina Latva-Aho (T)
Minna-Liisa Koivikko (ML)
Aino Stenius (A)
Paula Ollikainen (P)
Marika Korpela (M)
Katja Multasuo (K)
Päivi Salmijärvi (P)
Pieta Kemppainen (P)
Merja Runtti (M)
Riitta Päkkilä (R)
Irene Viinikangas (I)
Sinikka Pietikäinen (S)
Tuula Arkkola (T)

Informations de copyright

© 2022. The Author(s).

Références

Pediatr Diabetes. 2013 Aug;14(5):341-9
pubmed: 23469940
Diabetologia. 2018 May;61(5):1193-1202
pubmed: 29404673
J Clin Invest. 2001 Nov;108(9):1247-52
pubmed: 11696564
Diabetes Care. 2013 Sep;36(9):2615-20
pubmed: 23818528
Clin Exp Immunol. 2013 Jan;171(1):82-90
pubmed: 23199327
Diabetes Metab Res Rev. 2013 Oct;29(7):557-67
pubmed: 23674484
Diabetologia. 2015 May;58(5):980-7
pubmed: 25660258
Diabetes Care. 1998 Dec;21(12):2191-2
pubmed: 9839117
J Clin Endocrinol Metab. 2012 Feb;97(2):632-7
pubmed: 22162482
N Engl J Med. 2019 Aug 15;381(7):603-613
pubmed: 31180194
Clin Diabetes. 2021 Jan;39(1):14-43
pubmed: 33551551
Pediatr Diabetes. 2018 Mar;19(2):284-292
pubmed: 28597949
JAMA. 2013 Jun 19;309(23):2473-9
pubmed: 23780460
Pediatr Diabetes. 2011 Dec;12(8):733-43
pubmed: 21564455
Acta Diabetol. 2015 Jun;52(3):473-81
pubmed: 25381193
Autoimmunity. 2011 Aug;44(5):394-405
pubmed: 21244337
Diabetes. 2012 Oct;61(10):2556-64
pubmed: 22787139
Diabetes. 2013 Oct;62(10):3636-40
pubmed: 23835325
Clin Chem. 2019 Sep;65(9):1141-1152
pubmed: 31409598
Endocrinol Diabetes Metab. 2020 Nov 05;4(2):e00198
pubmed: 33855205
Nat Med. 2019 Dec;25(12):1865-1872
pubmed: 31792456
Pediatr Diabetes. 2016 Jul;17 Suppl 22:25-30
pubmed: 27411433
Eur J Endocrinol. 2013 Sep 14;169(4):479-85
pubmed: 23904276
Diabetes Metab Res Rev. 2013 Nov;29(8):646-54
pubmed: 23861236
Diabetes. 2020 Jan;69(1):12-19
pubmed: 31591105
Eur J Endocrinol. 2016 Mar;174(3):251-9
pubmed: 26620391
Autoimmunity. 2011 Dec;44(8):616-23
pubmed: 21604969
Diabetes Care. 2019 Jun;42(6):1051-1060
pubmed: 30967432
Autoimmunity. 2011 Mar;44(2):107-14
pubmed: 20836749
Diabetologia. 2007 Jun;50(6):1161-9
pubmed: 17406854
Diabetes Care. 2004 Jun;27(6):1487-95
pubmed: 15161807
J Clin Endocrinol Metab. 2018 Aug 1;103(8):2870-2878
pubmed: 29300921
Diabetes Care. 2020 Sep;43(9):2066-2073
pubmed: 32641373
Proc Natl Acad Sci U S A. 2007 Oct 23;104(43):17040-5
pubmed: 17942684
J Clin Endocrinol Metab. 2017 Dec 1;102(12):4428-4434
pubmed: 29040630
Diabetes Care. 2015 Oct;38(10):1975-85
pubmed: 26404927

Auteurs

Maria Månsson Martinez (MM)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden. maria.mansson_martinez@med.lu.se.

Lampros Spiliopoulos (L)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Falastin Salami (F)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Daniel Agardh (D)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Jorma Toppari (J)

Department of Pediatrics, Turku University Hospital, Turku, Finland.
Research Centre for Integrative Physiology and Pharmacology, Institute of Biomedicine, and Centre for Population Health Research, University of Turku, Turku, Finland.

Åke Lernmark (Å)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Jukka Kero (J)

Department of Pediatrics, Turku University Hospital, Turku, Finland.
Research Centre for Integrative Physiology and Pharmacology, Institute of Biomedicine, and Centre for Population Health Research, University of Turku, Turku, Finland.

Riitta Veijola (R)

Department of Pediatrics, PEDEGO Research Unit, MRC Oulu, University of Oulu, Oulu, Finland.
Department of Children and Adolescents, Oulu University Hospital, Oulu, Finland.

Päivi Tossavainen (P)

Department of Pediatrics, PEDEGO Research Unit, MRC Oulu, University of Oulu, Oulu, Finland.
Department of Children and Adolescents, Oulu University Hospital, Oulu, Finland.

Sauli Palmu (S)

Department of Pediatrics, Tampere Center for Child, Adolescent and Maternal Health Research, Tampere University Hospital, Tampere, Finland.

Markus Lundgren (M)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Henrik Borg (H)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Anastasia Katsarou (A)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Helena Elding Larsson (HE)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Mikael Knip (M)

Research Program for Clinical and Molecular Metabolism, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Marlena Maziarz (M)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Carina Törn (C)

Department of Clinical Sciences, Lund University CRC, Skåne University Hospital, Jan Waldenströms gata 35, Box 503 32, SE-214 28, Malmö, Sweden.

Classifications MeSH