A population study of clinical trial accrual for women and minorities in neuro-oncology following the NIH Revitalization Act.


Journal

Neuro-oncology
ISSN: 1523-5866
Titre abrégé: Neuro Oncol
Pays: England
ID NLM: 100887420

Informations de publication

Date de publication:
01 08 2022
Historique:
pubmed: 10 1 2022
medline: 3 8 2022
entrez: 9 1 2022
Statut: ppublish

Résumé

The NIH Revitalization Act, implemented 29 years ago, set to improve the representation of women and minorities in clinical trials. In this study, we investigate progress made in all phase therapeutic clinical trials for neuroepithelial CNS tumors stratified by demographic-specific age-adjusted disease incidence and mortality. Additionally, we identify workforce characteristics associated with clinical trials meeting established accrual benchmarks. Registry study of published clinical trials for World Health Organization defined neuroepithelial CNS tumors between January 2000 and December 2019. Study participants were obtained from PubMed and ClinicalTrials.gov. Population-based data originated from the CBTRUS for incidence analyses. SEER-18 Incidence-Based Mortality data was used for mortality analysis. Descriptive statistics, Fisher exact, and χ 2 tests were used for data analysis. Among 662 published clinical trials representing 49 907 participants, 62.5% of participants were men and 37.5% women (P < .0001) representing a mortality specific over-accrual for men (P = .001). Whites, Asians, Blacks, and Hispanics represented 91.7%, 1.5%, 2.6%, and 1.7% of trial participants. Compared with mortality, Blacks (47% of expected mortality, P = .008), Hispanics (17% of expected mortality, P < .001) and Asians (33% of expected mortality, P < .001) were underrepresented compared with Whites (114% of expected mortality, P < .001). Clinical trials meeting accrual benchmarks for race included minority authorship. Following the Revitalization Act, minorities and women remain underrepresented in therapeutic clinical trials for neuroepithelial tumors, relative to disease incidence and mortality. Study accrual has improved with time. This study provides a framework for clinical trial accrual efforts and offers guidance regarding workforce considerations associated with enrollment of underserved patients.

Sections du résumé

BACKGROUND
The NIH Revitalization Act, implemented 29 years ago, set to improve the representation of women and minorities in clinical trials. In this study, we investigate progress made in all phase therapeutic clinical trials for neuroepithelial CNS tumors stratified by demographic-specific age-adjusted disease incidence and mortality. Additionally, we identify workforce characteristics associated with clinical trials meeting established accrual benchmarks.
METHODS
Registry study of published clinical trials for World Health Organization defined neuroepithelial CNS tumors between January 2000 and December 2019. Study participants were obtained from PubMed and ClinicalTrials.gov. Population-based data originated from the CBTRUS for incidence analyses. SEER-18 Incidence-Based Mortality data was used for mortality analysis. Descriptive statistics, Fisher exact, and χ 2 tests were used for data analysis.
RESULTS
Among 662 published clinical trials representing 49 907 participants, 62.5% of participants were men and 37.5% women (P < .0001) representing a mortality specific over-accrual for men (P = .001). Whites, Asians, Blacks, and Hispanics represented 91.7%, 1.5%, 2.6%, and 1.7% of trial participants. Compared with mortality, Blacks (47% of expected mortality, P = .008), Hispanics (17% of expected mortality, P < .001) and Asians (33% of expected mortality, P < .001) were underrepresented compared with Whites (114% of expected mortality, P < .001). Clinical trials meeting accrual benchmarks for race included minority authorship.
CONCLUSIONS
Following the Revitalization Act, minorities and women remain underrepresented in therapeutic clinical trials for neuroepithelial tumors, relative to disease incidence and mortality. Study accrual has improved with time. This study provides a framework for clinical trial accrual efforts and offers guidance regarding workforce considerations associated with enrollment of underserved patients.

Identifiants

pubmed: 34999844
pii: 6499288
doi: 10.1093/neuonc/noac011
pmc: PMC9340618
doi:

Types de publication

Journal Article Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, P.H.S. Research Support, N.I.H., Extramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

1341-1349

Subventions

Organisme : NINDS NIH HHS
ID : K08 NS110919
Pays : United States
Organisme : CDC HHS
ID : 75D30119C06056
Pays : United States
Organisme : NCATS NIH HHS
ID : TL1 TR001871
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

© The Author(s) 2022. Published by Oxford University Press on behalf of the Society for Neuro-Oncology. All rights reserved. For permissions, please e-mail: journals.permissions@oup.com.

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Auteurs

Sheantel J Reihl (SJ)

University of California, San Francisco, Department of Neurosurgery, San Francisco, California,USA.

Nirav Patil (N)

Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.
University Health System, Research and Education Institute, Cleveland, Ohio, USA.
University Hospitals Health System, Research Health Analytics and Informatics, Cleveland, Ohio, USA.

Ramin A Morshed (RA)

University of California, San Francisco, Department of Neurosurgery, San Francisco, California,USA.

Mulki Mehari (M)

University of California, San Francisco, Department of Neurosurgery, San Francisco, California,USA.

Alexander Aabedi (A)

University of California, San Francisco, Department of Neurosurgery, San Francisco, California,USA.

Ugonma N Chukwueke (UN)

Center for Neuro-Oncology, Dana-Farber Cancer Institute, Department of Neurology, Harvard Medical School, Boston, Massachusetts, USA.

Alyx B Porter (AB)

Mayo Clinic, Division of Neuro-Oncology, Department of Neurology, Phoenix, Arizona, USA.

Valy Fontil (V)

University of California San Francisco, Division of General Internal Medicine, San Francisco, California, USA.
University of California San Francisco, Center for Vulnerable Populations, Zuckerberg San Francisco General Hospital, San Francisco, California, USA.

Gino Cioffi (G)

Division of Cancer Epidemiology and Genetics, Trans-Divisional Research Program, National Cancer Institute, Bethesda, Maryland,USA.
Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.

Kristin Waite (K)

Division of Cancer Epidemiology and Genetics, Trans-Divisional Research Program, National Cancer Institute, Bethesda, Maryland,USA.
Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.

Carol Kruchko (C)

Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.

Quinn Ostrom (Q)

Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.
Department of Neurosurgery, Duke University School of Medicine, Durham, North Carolina, USA.
The Preston Robert Tisch Brain Tumor Center, Duke University School of Medicine, Durham, North Carolina, USA.
Duke Cancer Institute, Duke University Medical Center, Durham, North Carolina, USA.

Jill Barnholtz-Sloan (J)

Central Brain Tumor Registry of the United States (CBTRUS), Hinsdale, Illinois, USA.
Center for Biomedical Informatics and Information Technology, National Cancer Institute, Bethesda, Maryland,USA.

Shawn L Hervey-Jumper (SL)

University of California, San Francisco, Department of Neurosurgery, San Francisco, California,USA.

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Classifications MeSH