Baseline fat fraction is a strong predictor of disease progression in Becker muscular dystrophy.
Dixon, mixed-effects model, MRI, MRS, muscle degeneration/disease progression
Journal
NMR in biomedicine
ISSN: 1099-1492
Titre abrégé: NMR Biomed
Pays: England
ID NLM: 8915233
Informations de publication
Date de publication:
07 2022
07 2022
Historique:
revised:
24
12
2021
received:
24
08
2021
accepted:
10
01
2022
pubmed:
16
1
2022
medline:
18
6
2022
entrez:
15
1
2022
Statut:
ppublish
Résumé
In Becker muscular dystrophy (BMD), muscle weakness progresses relatively slowly, with a highly variable rate among patients. This complicates clinical trials, as clinically relevant changes are difficult to capture within the typical duration of a trial. Therefore, predictors for disease progression are needed. We assessed if temporal increase of fat fraction (FF) in BMD follows a sigmoidal trajectory and whether fat fraction at baseline (FFbase) could therefore predict FF increase after 2 years (ΔFF). Thereafter, for two different MR-based parameters, we tested the additional predictive value to FFbase. We used 3-T Dixon data from the upper and lower leg, and multiecho spin-echo MRI and 7-T
Identifiants
pubmed: 35032073
doi: 10.1002/nbm.4691
pmc: PMC9286612
doi:
Substances chimiques
Adenosine Triphosphate
8L70Q75FXE
Types de publication
Journal Article
Research Support, Non-U.S. Gov't
Langues
eng
Sous-ensembles de citation
IM
Pagination
e4691Informations de copyright
© 2022 The Authors. NMR in Biomedicine published by John Wiley & Sons Ltd.
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