Three-year outcome of local injection of autologous stromal vascular fraction cells and microfat in refractory perianal fistulas of Crohn's disease.


Journal

Stem cell research & therapy
ISSN: 1757-6512
Titre abrégé: Stem Cell Res Ther
Pays: England
ID NLM: 101527581

Informations de publication

Date de publication:
09 02 2022
Historique:
received: 10 05 2021
accepted: 20 01 2022
entrez: 10 2 2022
pubmed: 11 2 2022
medline: 25 3 2022
Statut: epublish

Résumé

Perianal fistulas in Crohn's disease are frequent and disabling, with a major impact on patients' quality of life. Cell-based therapy using mesenchymal stem cells represents new hope for these patients, but long-term efficacy remains challenging. In a pilot study, including patients with refractory complex perianal fistulas, autologous adipose-derived stromal vascular fraction (ADSVF) combined with microfat achieved combined remission in 60% of cases, with a good safety profile at 1 year. The purpose of this study is to assess whether these results were maintained at longer term. The safety and efficacy data of the ten patients were evaluated retrospectively 3 years after injection on the basis of clinical and radiological data. MRI were analysed according to the MAGNIFI-CD score. No adverse event was attributed to the experimental stem-cell treatment. Combined remission was achieved in 7 patients (70%) and associated with a significant improvement in the MAGNIFI-CD MRI score. In conclusion, the safety and efficacy of ADSVF and microfat injection in Crohn's disease fistulas were maintained at 3 years, demonstrating that this innovative strategy is effective in producing a long-lasting healing effect. The ongoing multicentre randomized placebo-controlled trial (NCT04010526) will be helpful to define the place for this approach in the current therapeutic arsenal.

Identifiants

pubmed: 35139888
doi: 10.1186/s13287-022-02738-x
pii: 10.1186/s13287-022-02738-x
pmc: PMC8827195
doi:

Banques de données

ClinicalTrials.gov
['NCT04010526']

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

67

Informations de copyright

© 2022. The Author(s).

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Auteurs

Lucas Guillo (L)

Gastroenterology Department, Assistance Publique Hôpitaux de Marseille, University Hospital of Marseille Nord (AP-HM), Chemin des Bourrely, 13015, Marseille, France. lucas.guillo690@gmail.com.
Cell Therapy Department, INSERM CBT-1409, Assistance Publique Hôpitaux de Marseille, Aix-Marseille University, Marseille, France. lucas.guillo690@gmail.com.

Fanny Grimaud (F)

Cell Therapy Department, INSERM CBT-1409, Assistance Publique Hôpitaux de Marseille, Aix-Marseille University, Marseille, France.

Fanny Houser (F)

Gastroenterology Department, Assistance Publique Hôpitaux de Marseille, University Hospital of Marseille Nord (AP-HM), Chemin des Bourrely, 13015, Marseille, France.

Caroline Prost (C)

Department of Radiology, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Elisabeth Jouve (E)

Statistical Department, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Cécile Philandrianos (C)

Plastic Surgery Department, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Maxime Abellan (M)

Plastic Surgery Department, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Julie Veran (J)

Cell Therapy Department, INSERM CBT-1409, Assistance Publique Hôpitaux de Marseille, Aix-Marseille University, Marseille, France.

Carine Visee (C)

Digestive Surgery Department, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Laura Beyer-Berjot (L)

Digestive Surgery Department, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Ariadne Desjeux (A)

Gastroenterology Department, Assistance Publique Hôpitaux de Marseille, University Hospital of Marseille Nord (AP-HM), Chemin des Bourrely, 13015, Marseille, France.

Françoise Dignat-George (F)

C2VN, INSERM UMR 1263, Faculté de Pharmacie de Marseille, Aix Marseille University, Marseille, France.

Marc Leone (M)

Department of Anaesthesia and Intensive Care, Assistance Publique Hôpitaux de Marseille, Marseille, France.

Jean-Charles Grimaud (JC)

Gastroenterology Department, Assistance Publique Hôpitaux de Marseille, University Hospital of Marseille Nord (AP-HM), Chemin des Bourrely, 13015, Marseille, France.
Centre d'Investigation Clinique 1409, Assistance Publique Hôpitaux de Marseille, Aix Marseille University, Marseille, France.

Florence Sabatier (F)

Cell Therapy Department, INSERM CBT-1409, Assistance Publique Hôpitaux de Marseille, Aix-Marseille University, Marseille, France.
C2VN, INSERM UMR 1263, Faculté de Pharmacie de Marseille, Aix Marseille University, Marseille, France.

Mélanie Serrero (M)

Gastroenterology Department, Assistance Publique Hôpitaux de Marseille, University Hospital of Marseille Nord (AP-HM), Chemin des Bourrely, 13015, Marseille, France.

Jérémy Magalon (J)

Cell Therapy Department, INSERM CBT-1409, Assistance Publique Hôpitaux de Marseille, Aix-Marseille University, Marseille, France.
C2VN, INSERM UMR 1263, Faculté de Pharmacie de Marseille, Aix Marseille University, Marseille, France.

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